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ClinicalTrials.gov 95 recruiting now early-phase tilt #43 of 28,707 conditions

Sickle Cell Disease: early-phase trial registry

95 of 214 indexed Sickle Cell Disease trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #43 of 28,707 conditions by registered trial count.

214 US clinical trials · 95 currently recruiting · #43 of 28,707 conditions by registered trial count

Sickle Cell Disease: 214 US clinical trials tracked, 95 recruiting.

Sickle Cell Disease is the subject of 214 registered US clinical trials on ClinicalTrials.gov, 95 of them currently open to new participants. 14 are in Phase 3-4 (later-stage) and 87 in Phase 1-2 (earlier-stage). The most active sponsor is St. Jude Children's Research Hospital, running 17 of these trials.

Enrollment posture brief

Registry condition sickle-cell-disease

OPEN 95 | RECR 44% | LATE 14 | EARLY 87 | RANK #43 | SPON 17

Nearest open-share peer: Acute Ischemic Stroke (44% recruiting · 27 trials)

Mild Cognitive Impairment48.5%Sickle Cell Disease (this)44%Atrial Fibrillation29.4%Coronary Artery Disease25.9%Diabetes Mellitus23.3%
Open-enrollment share among volume-matched conditions near Sickle Cell Disease

Sickle Cell Disease lists 95 open slots (44% of 214 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Sickle Cell Disease on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Sickle Cell Disease is recruiting above its size-band peers.

    95 of 214 indexed trials (44.4%) are open to enrollment, against a 37.1% average across 139 conditions with 100+ trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. Sponsorship of Sickle Cell Disease trials is spread across many organizations.

    St. Jude Children's Research Hospital accounts for 17 of 214 trials (7.9%). 101 distinct sponsors appear on at least one study for this condition label.

  3. Most Sickle Cell Disease trials plan to enrol fewer than 100 people.

    Median target enrolment is 50 among the 214 trials that report a genuine target (sentinel values excluded). 150 of those (70.1%) plan for fewer than 100 participants.

  4. Sickle Cell Disease research is mostly interventional.

    160 interventional and 54 observational studies make up this index (74.8% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 139Phase 248Phase 311Phase 43

Open and recent trials

214 total, page 1 of 5

RECRUITING 30,000 participants

Study of the Role of Genetic Modifiers in Hemoglobinopathies

Cyprus Institute of Neurology and Genetics

NCT05799118

RECRUITING 10,000 participants

Sickle Cell Clinical Research and Intervention Program

St. Jude Children's Research Hospital

NCT02098863

RECRUITING 1,716 participants

Investigation of the Genetics of Hematologic Diseases

St. Jude Children's Research Hospital

NCT02720679

RECRUITING 750 participants

Cooperative Assessment of Late Effects for SCD Curative Therapies

Vanderbilt University Medical Center

NCT05153967

RECRUITING 500 participants

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

RTI International

NCT06385886

RECRUITING Phase 3 480 participants

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

Novo Nordisk A/S

NCT06609226

RECRUITING NA 470 participants

Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain

University of Pittsburgh

NCT06374238

RECRUITING Phase 3 408 participants

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

Novo Nordisk A/S

NCT06612268

RECRUITING Phase 2 389 participants

A Phase 2/3 Study in Adult and Adolescent Participants With SCD

Pfizer

NCT05431088

RECRUITING 352 participants

Sickle Cell Disease and the Genomic and Gene Therapy Needs of Stakeholders

St. Jude Children's Research Hospital

NCT04416178

RECRUITING NA 350 participants

Cerebral Oxygen Metabolism in Children

Washington University School of Medicine

NCT04157179

RECRUITING Phase 3 315 participants

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

Novartis Pharmaceuticals

NCT06439082

RECRUITING 300 participants

Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants

National Institute of Allergy and Infectious Diseases (NIAID)

NCT03937817

RECRUITING NA 287 participants

Delivering Patient-Facing Evidence-Based Guidelines Through mHealth to Adults With Sickle Cell Disease

Ohio State University

NCT06919224

RECRUITING NA 272 participants

SMYLS Multi-site Trial

Medical University of South Carolina

NCT06035939

RECRUITING 250 participants

Blood Sampling for Research Related to Sickle Cell Disease

National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

NCT00542230

RECRUITING NA 240 participants

Exercise in Child Health

University of California, Irvine

NCT05359991

RECRUITING NA 240 participants

Acupressure in Patients With Sickle Cell Disease

Indiana University

NCT06511453

RECRUITING 200 participants

Hydroxyurea Exposure Limiting Pregnancy and Follow-Up Lactation

Children's Hospital Medical Center, Cincinnati

NCT04093986

RECRUITING Phase 2 200 participants

Tocilizumab for Acute Chest Syndrome

University of Chicago

NCT05640271

RECRUITING Phase 3 192 participants

The Efficacy and Safety of Rilzabrutinib in Patients Aged 10 to 65 Years With Sickle-cell Disease

Sanofi

NCT06975865

RECRUITING NA 185 participants

A Stress and Pain Self-management m-Health App for Adult Outpatients With Sickle Cell Disease

University of Florida

NCT04484272

RECRUITING Phase 1 161 participants

A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease

Novartis Pharmaceuticals

NCT06546670

RECRUITING NA 155 participants

Integrative Training Program for Pediatric Sickle Cell Pain

Emory University

NCT06691867

RECRUITING Phase 4 130 participants

Rollover Study for Patients With Sickle Cell Disease Who Have Completed a Prior Novartis-Sponsored Crizanlizumab Study

Novartis Pharmaceuticals

NCT04657822

RECRUITING 130 participants

Verifying Antibodies After Live Immunization Delivery (VALID): A Study of Measles Vaccine Immunogenicity in Children With Sickle Cell Disease

Children's Hospital Medical Center, Cincinnati

NCT07356050

RECRUITING Phase 2 120 participants

Sub-dissociative Dose Ketamine in Treatment of Vaso-occlusive Pain Event in Children and Young Adults

Mohsen Saidinejad

NCT07369024

RECRUITING NA 120 participants

Integrative Medicine in Pain Management in Sickle Cell Disease, 2.0

Indiana University

NCT06725550

RECRUITING Phase 2 120 participants

Cognitive Remediation Intervention to Prepare for Transition of Care

University of Alabama at Birmingham

NCT05336201

RECRUITING NA 120 participants

Metabolic and Hemodynamic Reserve in Pediatric SCA

Washington University School of Medicine

NCT04406818

RECRUITING Phase 2 100 participants

Minimizing Toxicity in HLA-identical Sibling Donor Transplantation for Children With Sickle Cell Disease

Robert Nickel

NCT03587272

RECRUITING Phase 2 100 participants

Early Screening and Treatment of Heart Complication in Sickle Cell Disease

Inova Health Care Services

NCT07023666

RECRUITING Early Phase 1 100 participants

Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling

National Heart, Lung, and Blood Institute (NHLBI)

NCT06313398

RECRUITING Phase 3 100 participants

Study of a Single Dose of a 21-valent Pneumococcal Conjugate Vaccine in Children and Adolescents With Sickle Cell Disease

Sanofi

NCT07247188

RECRUITING 100 participants

Sickle Cell Disease Biofluid Chip Technology (SCD BioChip)

University Hospitals Cleveland Medical Center

NCT02824471

RECRUITING Phase 2 99 participants

Intravenous L-Citrulline for Vaso-occlusive Pain Episode in Sickle Cell Disease

Suvankar Majumdar

NCT06635902

RECRUITING NA 90 participants

MULTIsite Feasibility of MUSIc Therapy to Address Quality Of Life in Sickle Cell Disease

University of California, Irvine

NCT06853158

RECRUITING 80 participants

Dietary Intake and Dietary Behaviors in Adults With Sickle Cell Disease

National Institutes of Health Clinical Center (CC)

NCT05170412

RECRUITING NA 76 participants

Effect of Virtual Reality Technology for Pain Management of Vaso-Occlusive Crisis in Patients With Sickle Cell Disease

St. Jude Children's Research Hospital

NCT03353584

RECRUITING Phase 1 72 participants

Methylphenidate to Address Attention and Executive Deficits Among Children With Sickle Cell Disease

St. Jude Children's Research Hospital

NCT07226219

RECRUITING NA 70 participants

Predictors of Pain in Sickle Cell Disease

Duke University

NCT06139510

RECRUITING 70 participants

Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)

St. Jude Children's Research Hospital

NCT05810181

RECRUITING NA 68 participants

Empowering Adolescents and Young Adults With Sickle Cell Disease as Partners in Treatment Decision Making (EMPOWER-AYA)

Nemours Children's Clinic

NCT05383911

RECRUITING 65 participants

Peripheral Arterial Tonometry and Neurocognition in Sickle Cell Disease

St. Jude Children's Research Hospital

NCT06477289

RECRUITING Phase 2 63 participants

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

CSL Behring

NCT07224360

RECRUITING Phase 2 62 participants

Allo HSCT for High Risk Hemoglobinopathies

Masonic Cancer Center, University of Minnesota

NCT06872333

RECRUITING NA 60 participants

Let's Get REAL: Family Health Communication Tool in Pediatric Stem Cell Transplant and Cellular Therapy

Washington University School of Medicine

NCT06689800

RECRUITING NA 60 participants

Applying Directly Observed Therapy to Hydroxyurea to Realize Effectiveness

Nationwide Children's Hospital

NCT06264700

RECRUITING Phase 2 60 participants

Cannabinoids for the Reduction of Inflammation and Sickle Cell Related Pain

Icahn School of Medicine at Mount Sinai

NCT05519111

RECRUITING Phase 2 56 participants

A Dose-Finding Study of Tebapivat to Assess Efficacy, and Safety in Participants With Sickle Cell Disease (SCD)

Agios Pharmaceuticals

NCT06924970

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Phase Distribution

PhaseTrial count
Phase 1 39
Phase 2 48
Phase 3 11
Phase 4 3

Named interventions

Most-linked intervention names on Sickle Cell Disease records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Placebo Drug
15 trials
Alemtuzumab Drug
10 trials
Fludarabine Drug
7 trials
Sirolimus Drug
5 trials
Cyclophosphamide Drug
5 trials
Hydroxyurea Drug
4 trials
Pentostatin Drug
3 trials
Total Body Irradiation Radiation
3 trials

US sites by state

Facility locations filed on Sickle Cell Disease trials. A trial with sites in several states counts in each.

California 41 trials
Illinois 39 trials
Georgia 39 trials
New York 37 trials
Tennessee 36 trials
Maryland 35 trials
North Carolina 34 trials
Ohio 27 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Sickle Cell Disease page

214 registered trials, 95 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Sickle Cell Disease condition card totals 214 registered trials; most-linked intervention Placebo; top US site state California. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.