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ClinicalTrials.gov 4 recruiting now early-phase tilt

Myelodysplasia: early-phase trial registry

4 of 20 indexed Myelodysplasia trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #848 of 28,707 conditions by registered trial count.

20 US clinical trials · 4 currently recruiting · #848 of 28,707 conditions by registered trial count

Myelodysplasia: 20 US clinical trials tracked, 4 recruiting.

Myelodysplasia is the subject of 20 registered US clinical trials on ClinicalTrials.gov, 4 of them currently open to new participants. 1 are in Phase 3-4 (later-stage) and 15 in Phase 1-2 (earlier-stage). The most active sponsor is David Rizzieri, MD, running 3 of these trials.

Enrollment posture brief

Registry condition myelodysplasia

OPEN 4 | RECR 20% | LATE 1 | EARLY 15 | RANK #848 | SPON 3

Nearest open-share peer: Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive (20% recruiting · 10 trials)

Advanced or Metastatic Solid55%ALS50%Abdominal Pain25%Acute Myocardial Infarction25%Myelodysplasia (this)20%
Open-enrollment share among volume-matched conditions near Myelodysplasia

Myelodysplasia lists 4 open slots (20% of 20 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Myelodysplasia on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Myelodysplasia is recruiting below its size-band peers.

    4 of 20 indexed trials (20%) are open to enrollment, against a 39.7% average across 762 conditions with 20-99 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Myelodysplasia research.

    David Rizzieri, MD accounts for 3 of 20 trials (15%). 15 distinct sponsors appear on at least one study for this condition label.

  3. Most Myelodysplasia trials plan to enrol fewer than 100 people.

    Median target enrolment is 48 among the 20 trials that report a genuine target (sentinel values excluded). 12 of those (60%) plan for fewer than 100 participants.

  4. Myelodysplasia research is mostly interventional.

    18 interventional and 2 observational studies make up this index (90% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 15Phase 210Phase 31

Open and recent trials

20 total, page 1 of 1

RECRUITING Phase 2 300 participants

Myeloablative Allo HSCT With Related or Unrelated Donor for Heme Disorders

Masonic Cancer Center, University of Minnesota

NCT03314974

RECRUITING NA 200 participants

Umbilical Cord Blood Transplantation Using a Myeloablative Preparative Regimen for Hematological Diseases

Masonic Cancer Center, University of Minnesota

NCT01962636

RECRUITING Phase 2 124 participants

Dose-Expansion Study of Low Dose Post-Transplant Cyclophosphamide/Tacrolimus/Ruxolitinib for Graft-versus-Host Disease (GVHD) Prophylaxis in Myeloablative Allogeneic Peripheral Blood Stem Cell Transplantation

Hannah Choe, MD

NCT07249346

RECRUITING NA 40 participants

MCW Alpha/Beta T-Cell and B-Cell Depletion With Targeted ATG Dosing

Medical College of Wisconsin

NCT05794880

ACTIVE NOT RECRUITING 1,500 participants

Collecting and Storing Blood, Bone Marrow, and Other Samples From Patients With Acute Leukemia, Chronic Leukemia, or Myelodysplastic Syndromes

Alliance for Clinical Trials in Oncology

NCT00899223

ACTIVE NOT RECRUITING Phase 2 140 participants

Allogeneic Stem Cell Transplant With Alpha/Beta T AND B Cell Depletion for Hematologic Malignancies

Children's Hospital of Philadelphia

NCT02323867

ACTIVE NOT RECRUITING Phase 2 22 participants

Trial Evaluating MGTA-456 in Patients With High-Risk Malignancy

Masonic Cancer Center, University of Minnesota

NCT03674411

ACTIVE NOT RECRUITING Phase 3 21 participants

Haploidentical Allogeneic Peripheral Blood Transplantation: Examining Checkpoint Immune Regulators' Expression

Dartmouth-Hitchcock Medical Center

NCT03480360

ACTIVE NOT RECRUITING Phase 1 20 participants

Haploidentical Hematopoietic Cell Transplantation for Children With Hematologic Malignancies and Myelodysplasia

Nationwide Children's Hospital

NCT03431090

COMPLETED Phase 2 279 participants

Novel Approaches for Graft-versus-Host Disease Prevention Compared to Contemporary Controls (BMT CTN 1203)

National Heart, Lung, and Blood Institute (NHLBI)

NCT02208037

COMPLETED Phase 2 264 participants

Efficacy Study of T Cell Depleted Allogeneic Non-myeloablative Stem Cell Transplant

David Rizzieri, MD

NCT00597714

COMPLETED Phase 2 176 participants

Allo Non-Myeloablative SCT Utilizing Mis-Matched Family Member Stem Cells Purged Using Campath

David Rizzieri, MD

NCT00580034

COMPLETED Phase 1 52 participants

ABT-348 as Monotherapy and in Combination With Azacitidine to Treat Advanced Hematologic Malignancies

AbbVie (prior sponsor, Abbott)

NCT01110473

COMPLETED Phase 2 48 participants

Allo Non-myeloablative SCT Utilizing Matched Family Member Stem Cells Purged Using Campath

David Rizzieri, MD

NCT00578942

COMPLETED 48 participants

Registry Study of T Cell Depleted Allo Non-Myeloablative Stem Cell Transplant

Duke University

NCT01904175

COMPLETED Phase 1 45 participants

Safety Study of Human Myeloid Progenitor Cells (CLT-008) After Chemotherapy for Leukemia

Cellerant Therapeutics

NCT01297543

COMPLETED Phase 1 40 participants

Total Body Irradiation With Fludarabine Followed by Combined Umbilical Cord Blood (UCB) Transplants

Duke University

NCT00606437

COMPLETED Phase 2 40 participants

HLA-Nonidentical Stem Cell and Natural Killer Cell Transplantation for Children Less the Two Years of Age With Hematologic Malignancies

St. Jude Children's Research Hospital

NCT00145626

COMPLETED Phase 2 36 participants

Phase II Study Evaluating Busulfan and Fludarabine as Preparative Therapy in Adults With Hematopoietic Disorders Undergoing MUD SCT

University of California, San Francisco

NCT00516152

COMPLETED Phase 1 30 participants

Study of Vaccination With Autologous Acute Myeloblastic Leukemia Cells in Patients With Advanced Myelodysplasia or Acute Myelogenous Leukemia

Dana-Farber Cancer Institute

NCT00136422

Phase Distribution

PhaseTrial count
Phase 1 5
Phase 2 10
Phase 3 1

Named interventions

Most-linked intervention names on Myelodysplasia records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Cyclophosphamide Drug
3 trials
Campath Purged Non-myeloablative ASCT Drug
2 trials
Total Body Irradiation Radiation
2 trials
Tacrolimus Drug
2 trials
Fludarabine Drug
2 trials
human myeloid progenitor cells Biological
1 trials
ABT-348 and azacitidine Drug
1 trials
ABT-348 Drug
1 trials

US sites by state

Facility locations filed on Myelodysplasia trials. A trial with sites in several states counts in each.

North Carolina 6 trials
Minnesota 5 trials
California 4 trials
Ohio 3 trials
Massachusetts 3 trials
Illinois 3 trials
Texas 2 trials
Pennsylvania 2 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Myelodysplasia page

20 registered trials, 4 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Myelodysplasia condition card totals 20 registered trials; most-linked intervention Cyclophosphamide; top US site state North Carolina. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.