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ClinicalTrials.gov 47 recruiting now early-phase tilt #130 of 28,707 conditions

Amyotrophic Lateral Sclerosis: early-phase trial registry

47 of 103 indexed Amyotrophic Lateral Sclerosis trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #130 of 28,707 conditions by registered trial count.

103 US clinical trials · 47 currently recruiting · #130 of 28,707 conditions by registered trial count

Amyotrophic Lateral Sclerosis: 103 US clinical trials tracked, 47 recruiting.

Amyotrophic Lateral Sclerosis is the subject of 103 registered US clinical trials on ClinicalTrials.gov, 47 of them currently open to new participants. 6 are in Phase 3-4 (later-stage) and 40 in Phase 1-2 (earlier-stage). The most active sponsor is University of Miami, running 7 of these trials.

Enrollment posture brief

Registry condition amyotrophic-lateral-sclerosis

OPEN 47 | RECR 46% | LATE 6 | EARLY 40 | RANK #130 | SPON 7

Nearest open-share peer: Endothelial Dysfunction (46% recruiting · 46 trials)

Amyotrophic Lateral Scle (th…46%Mantle Cell Lymphoma44.7%Chronic Kidney Disease31.1%Attention Deficit Hyperactiv28.2%Metabolic Syndrome26.9%
Open-enrollment share among volume-matched conditions near Amyotrophic Lateral Sclerosis

Amyotrophic Lateral Sclerosis lists 47 open slots (46% of 103 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Amyotrophic Lateral Sclerosis on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Amyotrophic Lateral Sclerosis is recruiting above its size-band peers.

    47 of 103 indexed trials (45.6%) are open to enrollment, against a 37.1% average across 139 conditions with 100+ trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. Sponsorship of Amyotrophic Lateral Sclerosis trials is spread across many organizations.

    University of Miami accounts for 7 of 103 trials (6.8%). 69 distinct sponsors appear on at least one study for this condition label.

  3. Most Amyotrophic Lateral Sclerosis trials plan to enrol fewer than 100 people.

    Median target enrolment is 66 among the 103 trials that report a genuine target (sentinel values excluded). 62 of those (60.2%) plan for fewer than 100 participants.

  4. Amyotrophic Lateral Sclerosis splits between interventional and observational designs.

    68 interventional and 35 observational studies make up this index (66% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 119Phase 221Phase 36

Open and recent trials

103 total, page 2 of 3

ACTIVE NOT RECRUITING 217 participants

Phenotype, Genotype and Biomarkers 2

University of Miami

NCT04875416

ACTIVE NOT RECRUITING 170 participants

Remote Speech and Swallowing Assessment in ALS

Milton S. Hershey Medical Center

NCT04889898

ACTIVE NOT RECRUITING 100 participants

PRE-Symptomatic Studies in Amyotrophic Lateral Sclerosis

University of Miami

NCT01508962

ACTIVE NOT RECRUITING Phase 3 89 participants

FUSION: A Study to Evaluate the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of ION363 in Amyotrophic Lateral Sclerosis Participants With Fused in Sarcoma Mutations (FUS-ALS)

Ionis Pharmaceuticals

NCT04768972

ACTIVE NOT RECRUITING Phase 2 75 participants

Intrathecal Autologous Adipose-derived Mesenchymal Stromal Cells for Amyotrophic Lateral Sclerosis (ALS)

Mayo Clinic

NCT03268603

ACTIVE NOT RECRUITING Phase 1 66 participants

Regulatory T Cells for Amyotrophic Lateral Sclerosis

Cellenkos

NCT05695521

ACTIVE NOT RECRUITING Phase 2 40 participants

Rho Kinase Inhibitor in Amyotrophic Lateral Sclerosis (REAL)

Woolsey Pharmaceuticals

NCT05218668

ACTIVE NOT RECRUITING Phase 1 30 participants

Acamprosate in C9orf72 Hexanucleotide Repeat Expansion Amyotrophic Lateral Sclerosis (ACALS)

National Institute of Neurological Disorders and Stroke (NINDS)

NCT07204977

ACTIVE NOT RECRUITING Phase 1 20 participants

Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)

UniQure Biopharma B.V.

NCT06100276

ACTIVE NOT RECRUITING Phase 1 16 participants

CNS10-NPC-GDNF Delivered to the Motor Cortex for ALS

Cedars-Sinai Medical Center

NCT05306457

ACTIVE NOT RECRUITING NA 6 participants

COMMAND Early Feasibility Study: Implantable BCI to Control a Digital Device for People With Paralysis

Synchron Medical

NCT05035823

ACTIVE NOT RECRUITING Phase 1 5 participants

Study in ALS With Abatacept & IL-2

The Methodist Hospital Research Institute

NCT06307301

ACTIVE NOT RECRUITING Phase 1 1 participants

Personalized Antisense Oligonucleotide Therapy for A Single Participant With CHCHD10 ALS

n-Lorem Foundation

NCT06392126

ACTIVE NOT RECRUITING Phase 1 1 participants

Personalized Antisense Oligonucleotide for a Single Participant With CHCHD10 ALS

n-Lorem Foundation

NCT06977451

ACTIVE NOT RECRUITING Phase 1 1 participants

Personalized Antisense Oligonucleotide Therapy for A Single Participant With TARDBP ALS

n-Lorem Foundation

NCT07095712

COMPLETED 15,000 participants

Amyotrophic Lateral Sclerosis Web Based Patient Care Database: ALSConnection.Org

Forbes Norris MDA/ALS Research Center

NCT00302198

COMPLETED Phase 2 711 participants

Study of Safety, Tolerability & Efficacy of CK-2017357 in Amyotrophic Lateral Sclerosis (ALS)

Cytokinetics

NCT01709149

COMPLETED Phase 2 551 participants

Study Evaluating TCH346 and Placebo Administered Once Daily in Patients With Amyotrophic Lateral Sclerosis (ALS)

Novartis Pharmaceuticals

NCT00072709

COMPLETED NA 431 participants

Trial of Ascertaining Individual Preferences for Loved One's Role in End-of-Life

Johns Hopkins University

NCT01160367

COMPLETED 230 participants

Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases

Nemours Children's Clinic

NCT02532244

COMPLETED Phase 3 176 participants

An Efficacy, Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of BIIB067 (Tofersen) in Adults With Inherited Amyotrophic Lateral Sclerosis (ALS)

Biogen

NCT02623699

COMPLETED NA 153 participants

Early Treatment of Amyotrophic Lateral Sclerosis (ALS) With Nutrition and Non-Invasive Positive Pressure Ventilation

Edward Kasaraskis

NCT00116558

COMPLETED Phase 2 138 participants

Safety and Efficacy Study of NP001 in Patients With Amyotrophic Lateral Sclerosis (ALS) and Systemic Inflammation

Neuraltus Pharmaceuticals

NCT02794857

COMPLETED Phase 2 136 participants

A Study of NP001 in Subjects With Amyotrophic Lateral Sclerosis (ALS)

Neuraltus Pharmaceuticals

NCT01281631

COMPLETED Phase 2 109 participants

A Multi-Center Controlled Screening Trial of Safety and Efficacy of Lithium Carbonate in Subjects With Amyotrophic Lateral Sclerosis (ALS)

Forbes Norris MDA/ALS Research Center

NCT00790582

COMPLETED Phase 3 100 participants

Safety/Efficacy of AVP-923 in the Treatment of Emotional Lability (Uncontrolled Crying & Laughing) in Patients With ALS

Avanir Pharmaceuticals

NCT00021697

COMPLETED Phase 2 90 participants

Open Label Extension Study of AMX0035 in Patients With ALS

Amylyx Pharmaceuticals

NCT03488524

COMPLETED 87 participants

The E-health Application To Modify ORal Energy Intake and Measure Outcomes REmotely in ALS Clinical Trial (EAT MORE2)

Massachusetts General Hospital

NCT04051333

COMPLETED Phase 2 74 participants

Open-Label, Safety and Tolerability Extension Study of KNS-760704 in Amyotrophic Lateral Sclerosis (ALS) (CL211)

Knopp Biosciences

NCT00931944

COMPLETED Phase 2 73 participants

A Study to Evaluate, Safety, Tolerability, Pharmacodynamic (PD) Markers and Pharmacokinetics (PK) of AP-101 in Participants With Amyotrophic Lateral Sclerosis (ALS)

AL-S Pharma

NCT05039099

COMPLETED Phase 2 54 participants

Multiple Doses of AT-1501-A201 in Adults With ALS

Anelixis Therapeutics

NCT04322149

COMPLETED NA 39 participants

Virtual Seating Coach on Power Wheelchairs of Persons With Amyotrophic Lateral Sclerosis (ALS)

Wake Forest University Health Sciences

NCT05742828

COMPLETED Phase 2 38 participants

Phase II/III Randomized, Placebo-controlled Trial of Arimoclomol in SOD1 Positive Familial Amyotrophic Lateral Sclerosis

University of Miami

NCT00706147

COMPLETED 35 participants

Assessment of Postural Orientation and Equilibrium In Early Amyotrophic Lateral Sclerosis (ALS)

Wake Forest University Health Sciences

NCT00956501

COMPLETED NA 28 participants

ALS and Airway Clearance (ALSAC) Therapy

The University of Texas Health Science Center at San Antonio

NCT04947436

COMPLETED Phase 2 28 participants

A Compassionate Use Protocol of AMX0035 for Treatment of Patients With Amyotrophic Lateral Sclerosis (ALS)

Amylyx Pharmaceuticals

NCT04516096

COMPLETED Phase 1 28 participants

Impact of Nuedexta on Bulbar Physiology and Function in ALS

University of Florida

NCT03883581

COMPLETED 25 participants

Comparing The Cyberlink Control System to the Manual Letter Board for Communication Purposes in the ALS Patient Population

Drexel University College of Medicine

NCT00718497

COMPLETED Phase 2 25 participants

Clenbuterol on Motor Function in Individuals With Amyotrophic Lateral Sclerosis

Dwight Koeberl, M.D., Ph.D.

NCT04245709

COMPLETED 25 participants

Efficacy of Noninvasive Ventilation in Amyotrophic Lateral Sclerosis (ALS)

Columbia University

NCT00537641

COMPLETED Early Phase 1 22 participants

Perampanel Single Ascending Dose Transcranial Magnetic Stimulation Biomarker Study in Amyotrophic Lateral Sclerosis

Mayo Clinic

NCT03793868

COMPLETED 21 participants

Confirmation of Self-Reported Incident ALS Cases in the AARP-Diet and Health (AARP-DH) Cohort

National Institute of Environmental Health Sciences (NIEHS)

NCT00377351

COMPLETED Phase 2 20 participants

Levetiracetam for Cramps, Spasticity and Neuroprotection in Motor Neuron Disease

Duke University

NCT00324454

COMPLETED NA 19 participants

Cervical Electrical Stimulation for ALS

VA Office of Research and Development

NCT03411863

COMPLETED Phase 1 18 participants

CNS10-NPC-GDNF for the Treatment of ALS

Cedars-Sinai Medical Center

NCT02943850

COMPLETED Phase 2 18 participants

Safety of Engensis in Participants With Amyotrophic Lateral Sclerosis

Helixmith Co.

NCT04632225

COMPLETED Phase 1 17 participants

Neurodegenerative Alzheimer's Disease and Amyotrophic Lateral Sclerosis (NADALS) Basket Trial

Massachusetts General Hospital

NCT05189106

COMPLETED NA 13 participants

Yogic Breathing Exercise for People With Amyotrophic Lateral Sclerosis

University of Alabama at Birmingham

NCT05979688

COMPLETED Phase 1 12 participants

Open Label Study: Treatment of ALS Fatigue With PolyMVA

University of Missouri-Columbia

NCT04557410

COMPLETED 11 participants

Cerebrospinal Fluid Repository

Drexel University College of Medicine

NCT00714636

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Phase Distribution

PhaseTrial count
Phase 1 19
Phase 2 21
Phase 3 6

Named interventions

Most-linked intervention names on Amyotrophic Lateral Sclerosis records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Placebo Drug
9 trials
Placebo Other
5 trials
AMX0035 Drug
3 trials
NP001 Drug
2 trials
nL-CHCHD-001 Drug
2 trials
Pridopidine Drug
2 trials
R1 Robot Device
2 trials
N1 Implant Device
2 trials

US sites by state

Facility locations filed on Amyotrophic Lateral Sclerosis trials. A trial with sites in several states counts in each.

Florida 38 trials
California 35 trials
Massachusetts 29 trials
New York 25 trials
Pennsylvania 20 trials
Maryland 20 trials
Texas 19 trials
Arizona 19 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Amyotrophic Lateral Sclerosis page

103 registered trials, 47 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 47 Amyotrophic Lateral Sclerosis trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • University of Miami sponsors the most Amyotrophic Lateral Sclerosis trials on record, review their full trial history before evaluating a specific study. See University of Miami's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Amyotrophic Lateral Sclerosis condition card totals 103 registered trials; most-linked intervention Placebo; top US site state Florida. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.