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ClinicalTrials.gov 95 recruiting now early-phase tilt #43 of 28,707 conditions

Sickle Cell Disease: early-phase trial registry

95 of 214 indexed Sickle Cell Disease trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #43 of 28,707 conditions by registered trial count.

214 US clinical trials · 95 currently recruiting · #43 of 28,707 conditions by registered trial count

Sickle Cell Disease: 214 US clinical trials tracked, 95 recruiting.

Sickle Cell Disease is the subject of 214 registered US clinical trials on ClinicalTrials.gov, 95 of them currently open to new participants. 14 are in Phase 3-4 (later-stage) and 87 in Phase 1-2 (earlier-stage). The most active sponsor is St. Jude Children's Research Hospital, running 17 of these trials.

Enrollment posture brief

Registry condition sickle-cell-disease

OPEN 95 | RECR 44% | LATE 14 | EARLY 87 | RANK #43 | SPON 17

Nearest open-share peer: Acute Ischemic Stroke (44% recruiting · 27 trials)

Mild Cognitive Impairment48.5%Sickle Cell Disease (this)44%Atrial Fibrillation29.4%Coronary Artery Disease25.9%Diabetes Mellitus23.3%
Open-enrollment share among volume-matched conditions near Sickle Cell Disease

Sickle Cell Disease lists 95 open slots (44% of 214 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Sickle Cell Disease on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Sickle Cell Disease is recruiting above its size-band peers.

    95 of 214 indexed trials (44.4%) are open to enrollment, against a 37.1% average across 139 conditions with 100+ trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. Sponsorship of Sickle Cell Disease trials is spread across many organizations.

    St. Jude Children's Research Hospital accounts for 17 of 214 trials (7.9%). 101 distinct sponsors appear on at least one study for this condition label.

  3. Most Sickle Cell Disease trials plan to enrol fewer than 100 people.

    Median target enrolment is 50 among the 214 trials that report a genuine target (sentinel values excluded). 150 of those (70.1%) plan for fewer than 100 participants.

  4. Sickle Cell Disease research is mostly interventional.

    160 interventional and 54 observational studies make up this index (74.8% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 139Phase 248Phase 311Phase 43

Open and recent trials

214 total, page 4 of 5

COMPLETED 186 participants

Living With Sickle Cell Disease in the COVID-19 Pandemic

National Human Genome Research Institute (NHGRI)

NCT04417673

COMPLETED 165 participants

Cerebrovascular Reserve and White Matter Disease in Patients with Chronic Anemia

Children's Hospital Los Angeles

NCT03715972

COMPLETED 157 participants

Red Blood Cell - IMProving trAnsfusions for Chronically Transfused Recipients

Westat

NCT05255445

COMPLETED NA 134 participants

Decision Aid for Therapeutic Options In Sickle Cell Disease

Emory University

NCT02326597

COMPLETED 131 participants

Validation of the Sickle Cell Disease Pain Burden Interview

Connecticut Children's Medical Center

NCT00804362

COMPLETED Phase 1 129 participants

A Study to Evaluate GBT021601 in Single and Multiple Doses in Healthy Participants

Pfizer

NCT05036512

COMPLETED 120 participants

The Link Between Anemia and Deficits in Memory and Attention in Individuals With Sickle Cell Disease

National Heart, Lung, and Blood Institute (NHLBI)

NCT00451919

COMPLETED NA 112 participants

Sickle Cell Anemia WE CARE

Boston Medical Center

NCT03716726

COMPLETED 109 participants

Examining the Knowledge, Attitudes, and Beliefs of Sickle Cell Disease Patients, Parents of Patients With Sickle Cell Disease, and Providers Towards the Integration of CRISPR in Clinical Care

National Human Genome Research Institute (NHGRI)

NCT03167450

COMPLETED Phase 2 108 participants

Arginine Therapy for Sickle Cell Disease Pain

Emory University

NCT02536170

COMPLETED 99 participants

Pathophysiology of Acute Pain in Patients With Sickle Cell Disease

National Heart, Lung, and Blood Institute (NHLBI)

NCT03049475

COMPLETED 99 participants

Molecular Phenotyping of Asthma in Sickle Cell Disease

Nemours Children's Clinic

NCT01879592

COMPLETED 98 participants

A Study to Learn About Sickle Cell Disease In Adult Patients

Pfizer

NCT05407805

COMPLETED Phase 2 95 participants

Haploidentical Bone Marrow Transplantation in Sickle Cell Patients (BMTCTN1507)

Medical College of Wisconsin

NCT03263559

COMPLETED NA 91 participants

Microvascular Blood Flow in Sickle Cell Anemia

Versiti Blood Health

NCT01566890

COMPLETED Phase 2 90 participants

A Study of the Efficacy and Safety of ICA-17043 (With or Without Hydroxyurea) in Patients With Sickle Cell Anemia.

Icagen

NCT00040677

COMPLETED 88 participants

Parent Willingness to Participate in Tobacco Trials in the Pediatric Clinical Setting

St. Jude Children's Research Hospital

NCT01673243

COMPLETED Phase 2 87 participants

A Study to Assess the Effect of Ticagrelor in Reducing the Number of Days With Pain in Patients With Sickle Cell Disease

AstraZeneca

NCT02482298

COMPLETED 78 participants

Sickle Cell Uric Acid (SCUA) - Cohort Repository

Virginia Commonwealth University

NCT04190888

COMPLETED NA 78 participants

Patient-Provider Tools to Improve the Transition to Adult Care in Sickle Cell Disease

Children's Hospital Medical Center, Cincinnati

NCT02200510

COMPLETED 77 participants

The Feasibility of Text Messaging to Assess Secondhand Smoke Exposure Among Youngsters With Cancer or Sickle Cell Disease

St. Jude Children's Research Hospital

NCT01591187

COMPLETED NA 74 participants

Computerized Cognitive Behavioral Therapy Assisted Life Management for Pain in Sickle Cell Disease

University of Pittsburgh

NCT03029468

COMPLETED Phase 2 70 participants

Vitamin D for Sickle-cell Respiratory Complications

Gary M Brittenham, MD

NCT01443728

COMPLETED 57 participants

Functional Neuroimaging of Pain Using EEG and fMRI

University of Minnesota

NCT02212691

COMPLETED Phase 2 54 participants

Inhaled Mometasone to Reduce Painful Episodes in Patients With Sickle Cell Disease

Jeffrey Glassberg

NCT02061202

COMPLETED Phase 2 53 participants

A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease

Forma Therapeutics

NCT04987489

COMPLETED NA 50 participants

BEATS 2: Music Therapy in Sickle Cell

University Hospitals Cleveland Medical Center

NCT03233269

COMPLETED 50 participants

Genes Influencing Iron Overload State

St. Jude Children's Research Hospital

NCT01158794

COMPLETED NA 46 participants

The Feasibility of the PAINReportIt Guided Relaxation Intervention-INPATIENT

University of Florida

NCT02729350

COMPLETED NA 45 participants

SMART Mobile Application Technology Utilization in the Treatment of Sickle Cell Disease Post Day Hospital Discharge

Duke University

NCT02475993

COMPLETED Phase 1 44 participants

Atorvastatin Therapy to Improve Endothelial Function in Sickle Cell Disease

National Institutes of Health Clinical Center (CC)

NCT00072826

COMPLETED 42 participants

Evaluation of Sickle Cell Liver Disease

National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

NCT01950429

COMPLETED Phase 1 42 participants

Simvastatin (Zocor) Therapy in Sickle Cell Disease

UCSF Benioff Children's Hospital Oakland

NCT00508027

COMPLETED NA 40 participants

Home-based Assessment of PRO Measures in SCD Using A Smartphone App Platform: A Feasibility Study

Ann & Robert H Lurie Children's Hospital of Chicago

NCT04678037

COMPLETED Phase 1 39 participants

Adenosine 2A Agonist Lexiscan in Children and Adults With Sickle Cell Disease

Dana-Farber Cancer Institute

NCT01085201

COMPLETED Phase 1 36 participants

Inhaled Corticosteroid Use to Prevent Acute Chest Syndrome Recurrence in Children Between 1 and 4 With Sickle Cell Disease: a Feasibility Trial

Vanderbilt University

NCT02187445

COMPLETED Phase 2 34 participants

Treatment of Sickle Cell Patients Hospitalized in Pain Crisis With Prophylactic Dose Low-molecular-weight Heparin (LMWH) Versus Placebo

Duke University

NCT01419977

COMPLETED NA 33 participants

COVID-19 Vaccination Hesitancy in Adults With Sickle Cell Disease

Duke University

NCT05998824

COMPLETED Phase 2 31 participants

Study of Propranolol as Anti-Adhesive Therapy in Sickle Cell Disease (SCD)

Laura M. De Castro, MD

NCT01077921

COMPLETED NA 30 participants

Cognitive Behavioral Therapy and Real-time Self-management Intervention for SCD Via Mobile Applications

University of Pittsburgh

NCT02384590

COMPLETED Phase 1 28 participants

Safety of Single Doses of CSL889 in Adult Patients With Sickle Cell Disease

CSL Behring

NCT04285827

COMPLETED 27 participants

Motivations, Expectations, and Decision-making of Sickle Cell Patients in Clinical Research

National Institutes of Health Clinical Center (CC)

NCT03709303

COMPLETED Phase 2 25 participants

Study to Assess Efficacy and Safety of VIT-2763 (Vamifeport) in Subjects With Sickle Cell Disease

Vifor (International)

NCT04817670

COMPLETED 25 participants

Assessing Function in Pediatric Patients With Sickle Cell Disease

Connecticut Children's Medical Center

NCT00590148

COMPLETED 25 participants

Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients

University of California, San Francisco

NCT03609827

COMPLETED NA 24 participants

MUSic Therapy to Improve Quality Of Life in Sickle Cell Disease (MUSIQOLS)

University Hospitals Cleveland Medical Center

NCT03556657

COMPLETED Phase 1 24 participants

Abatacept for GVHD Prophylaxis After Hematopoietic Stem Cell Transplantation for Pediatric Sickle Cell Disease

Monica Bhatia

NCT02867800

COMPLETED Phase 1 22 participants

Red Blood Cell Survival in Sickle Cell Disease

Marianne Yee

NCT04426591

COMPLETED Phase 2 22 participants

Stem Cell Transplant for Hemoglobinopathy

Masonic Cancer Center, University of Minnesota

NCT00176852

COMPLETED 21 participants

Use of a Mobile-based App for SCD Patients

Duke University

NCT01833702

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Phase Distribution

PhaseTrial count
Phase 1 39
Phase 2 48
Phase 3 11
Phase 4 3

Named interventions

Most-linked intervention names on Sickle Cell Disease records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Placebo Drug
15 trials
Alemtuzumab Drug
10 trials
Fludarabine Drug
7 trials
Sirolimus Drug
5 trials
Cyclophosphamide Drug
5 trials
Hydroxyurea Drug
4 trials
Pentostatin Drug
3 trials
Total Body Irradiation Radiation
3 trials

US sites by state

Facility locations filed on Sickle Cell Disease trials. A trial with sites in several states counts in each.

California 41 trials
Illinois 39 trials
Georgia 39 trials
New York 37 trials
Tennessee 36 trials
Maryland 35 trials
North Carolina 34 trials
Ohio 27 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Sickle Cell Disease page

214 registered trials, 95 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Sickle Cell Disease condition card totals 214 registered trials; most-linked intervention Placebo; top US site state California. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.