Agios Pharmaceuticals

Open enrollment with an early-phase pipeline tilt

According to ClinicalTrials.gov-derived indexes, Agios Pharmaceuticals sits in the top decile of US sponsors by registered trial count (#407 of 15,742 sponsors by registered trial count).

44 total trials 3 currently recruiting 31 completed early-phase tilt top decile by trial count

Agios Pharmaceuticals: 44 sponsored US clinical trials, 3 recruiting.

Agios Pharmaceuticals sponsors 44 registered US clinical trials on ClinicalTrials.gov, 3 of them currently recruiting, and 31 completed. 7 of these trials are in Phase 3-4 (later-stage) and 33 in Phase 1-2 (earlier-stage). The most-studied condition in this pipeline is Healthy Volunteers, with 3 trials.

Top-decile sponsor footprint

Agios Pharmaceuticals ranks in the top decile of sponsors by registered trial count (#407 of 15,742 sponsors by registered trial count). Volume at this scale usually reflects a long institutional pipeline, read phase tilt and therapeutic areas below before treating it as current-year activity.

Trial completion reliability score

C 75/100

31 of 33 decided trials (Completed vs. Terminated on ClinicalTrials.gov) reached their planned completion (93.9%), vs. national p10 68.4% / p90 100% among 1,234 sponsors with at least 10 decided trials. Still-open trials (Recruiting, Active-not-recruiting, Not-yet-recruiting) are excluded since they have not reached an outcome yet.

Open and recent trials

44 total, page 1 of 1

RECRUITING Phase 1

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

NCT07241234

RECRUITING Phase 1

A Study to Determine the Safety and Tolerability of AG-236 and How it is Absorbed, Broken Down, and Eliminated From the Body in Healthy Participants

NCT07075640

RECRUITING Phase 2

A Dose-Finding Study of Tebapivat to Assess Efficacy, and Safety in Participants With Sickle Cell Disease (SCD)

NCT06924970

ACTIVE NOT RECRUITING Phase 2

A Study of Tebapivat (AG-946) in Participants With Anemia Due to Lower-Risk Myelodysplastic Syndromes (LR-MDS)

NCT05490446

ACTIVE NOT RECRUITING Phase 3

A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Regularly Transfused, Followed by a 5-Year Extension Period

NCT05144256

ACTIVE NOT RECRUITING Phase 3

A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Not Regularly Transfused, Followed by a 5-Year Extension Period

NCT05175105

ACTIVE NOT RECRUITING Phase 2

A Study Evaluating the Efficacy and Safety of Mitapivat (AG-348) in Participants With Sickle Cell Disease (RISE UP)

NCT05031780

ACTIVE NOT RECRUITING Phase 3

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)

NCT04770753

ACTIVE NOT RECRUITING Phase 3

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)

NCT04770779

ACTIVE NOT RECRUITING Phase 2

A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia

NCT03692052

ACTIVE NOT RECRUITING

Pyruvate Kinase Deficiency Global Longitudinal Registry

NCT03481738

COMPLETED Phase 1

A Study to Determine How Tebapivat is Absorbed, Broken Down, and Removed From the Body and the Extent to Which Tebapivat is Made Available in the Body in Healthy Participants

NCT06745271

COMPLETED Phase 1

Study of How Mitapivat Affects Midazolam Blood Levels in Healthy Participants

NCT06648824

COMPLETED Phase 1

Single and Multiple Ascending Dose Study and Food Effect Study for AG181

NCT06286033

COMPLETED Phase 1

A Pharmacokinetic Study of Mitapivat in Participants With Moderate Hepatic Impairment Compared to Matched Healthy Control Participants With Normal Hepatic Function

NCT05610657

COMPLETED

Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008

NCT04995315

TERMINATED

Pyruvate Kinase (PK) Deficiency Global Longitudinal Registry: Patient-Reported Outcomes (PRO)

NCT04964323

COMPLETED Phase 1

A Study to Compare the Pharmacokinetics and Safety of Mitapivat 100 mg Tablet Formulation With Mitapivat 2 × 50 mg Tablet Formulation in Healthy Adult Participants

NCT04696393

COMPLETED Phase 1

A Study to Assess the Relative Bioavailability and Effect of Food on the Coated Granule Formulation of Mitapivat in Healthy Participants

NCT04565678

COMPLETED Phase 1

A Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-946 in Healthy Volunteers and in Participants With Sickle Cell Disease

NCT04536792

COMPLETED Phase 1

A Study to Evaluate the Pharmacokinetics, Safety, and Tolerability of Mitapivat (AG-348) in Healthy Adult Participants

NCT04472832

COMPLETED Phase 1

A Study to Evaluate AG-881 in Healthy Japanese and Non-Asian Participants

NCT04145128

COMPLETED Phase 1

A Study to Compare the Relative Bioavailability of Two AG-881 Formulations and Evaluate the Effect of Food and Omeprazole on the Pharmacokinetics of AG-881

NCT04128787

COMPLETED Phase 1

A Study to Evaluate the Effect of AG-881 on the Pharmacokinetics of a Single Dose of Lamotrigine in Healthy Adults

NCT04015687

COMPLETED Phase 1

Study to Evaluate the Effect of Multiple Doses of Itraconazole and Rifampin on the Single-Dose Pharmacokinetics of Mitapivat Sulfate (AG-348) in Healthy Adult Participants

NCT03991312

TERMINATED Phase 1

A Study of AG-636 in the Treatment of Subjects With Advanced Lymphoma

NCT03834584

COMPLETED Phase 1

A Safety and Pharmacokinetic Study of AG-881 in Healthy Male Participants Following Administration of a Single Oral Dose of [14C] AG-881 and Concomitant Intravenous Microdose of [13C315N3] AG-881

NCT03960502

COMPLETED Phase 3

Extension Study of AG-348 in Adult Participants With Pyruvate Kinase Deficiency Previously Enrolled in AG-348-006 or AG348-C-007

NCT03853798

COMPLETED Phase 3

A Study to Evaluate Efficacy and Safety of AG-348 in Not Regularly Transfused Adult Participants With Pyruvate Kinase Deficiency (PKD)

NCT03548220

COMPLETED Phase 3

A Study Evaluating the Efficacy and Safety of AG-348 in Regularly Transfused Adult Participants With Pyruvate Kinase Deficiency (PKD)

NCT03559699

COMPLETED Phase 1

A Study to Evaluate the Absorption, Distribution, Metabolism, Excretion and Absolute Bioavailability of AG-348 in Healthy Male Participants Following Administration of a Single Oral Dose of [14C]AG-348 and Concomitant Single Intravenous Microdose of [13C6]AG-348

NCT03703505

COMPLETED

Pre-Screening Study to Identify MTAP Loss in Advanced Solid Tumors or Lymphoma

NCT03361358

COMPLETED Phase 1

Study to Evaluate the Relative Bioavailability and Safety of the AG-348 Tablet and Capsule Formulations in Healthy Adults

NCT03397329

COMPLETED Phase 1

A Study of AG-120 (Ivosidenib) in Subjects With Mild or Moderate Hepatic Impairment or Normal Hepatic Function

NCT03282513

COMPLETED Phase 1

Study to Evaluate the Pharmacokinetics, Safety, and QTc Effect of AG-348 in Healthy Subjects of Japanese Origin and Non-Asian Origin

NCT03250598

COMPLETED Phase 1

Japanese Bridging Study of Ivosidenib (AG-120) in Healthy Subjects

NCT03071770

COMPLETED Phase 1

Drug-Drug Interaction Study of AG120 in Healthy Subjects

NCT02831972

COMPLETED Phase 1

Food Effect Study of AG120 in Healthy Subjects

NCT02579707

COMPLETED Phase 1

Study of Orally Administered AG-881 in Patients With Advanced Hematologic Malignancies With an IDH1 and/or IDH2 Mutation

NCT02492737

COMPLETED Phase 2

A Study of AG-348 in Adult Participants With Pyruvate Kinase (PK) Deficiency

NCT02476916

COMPLETED Phase 1

Study to Investigate the Absorption, Metabolism, and Excretion of [14C]-AG-120

NCT02489513

COMPLETED Phase 1

Food Effect Study of AG-221 in Healthy Male Subjects

NCT02218346

COMPLETED Phase 1

A Phase I Study of AG-348 in Healthy Volunteers

NCT02149966

COMPLETED Phase 1

A Phase I Study of AG-348 in Healthy Volunteers

NCT02108106

What is open in the Agios Pharmaceuticals pipeline

3 recruiting of 44 indexed (7% open); 31 completed (70%).

Phase mix: 7 late (III/IV) vs 33 early (I/II) (early-phase heavy).

Top condition: Healthy Volunteers (3 trials), 9 others listed.

How open-pipeline share is computed

Recruiting share is recruiting_count divided by trial_count for this sponsor in the public registry export. Status can change between pulls; treat the figure as a research-attention snapshot, not product availability.

Agios Pharmaceuticals: open-pipeline peers nationwide

Peers matched on 44 registered trials and 7% open enrollment, not the therapeutic-area sidebar.

Agios Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot). 2×2 strategic matrix plotting 9 entities by Total trials (X) and Recruiting share (Y), with a crosshair dividing the plot into four quadrants. Higher volume & more openFocused & more openHigher volume, mostly closedSmaller & mostly closed 0100200300400 0%2%4%6%8%10% Total trials Recruiting share Agios PharmaceuticalsBeth Israel Medical CenterInnovative MedicalKowa Research InstituteMedtronic CardiovascularClinical Nutrition Research Center, Illinois Institute of TechnologyBioCryst PharmaceuticalsGenentechH. Lundbeck A/S
Agios Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot).

Agios Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together.

Sponsors near 44 trials (± recruiting share)

Sponsors near 7% open enrollment (± trial volume)

What to do with this Agios Pharmaceuticals page

44 registered trials is a research-attention snapshot, not an endorsement of Agios Pharmaceuticals or any single study.

  • 3 of Agios Pharmaceuticals's trials are currently recruiting, check each one's own eligibility criteria before contacting a site. Browse recruiting trials
  • Healthy Volunteers is the condition Agios Pharmaceuticals studies most, compare against other sponsors active in the same condition before evaluating a specific study. See Healthy Volunteers trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Agios Pharmaceuticals pipeline card: 44 registered trials from official public datasets.Report a data error.