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ClinicalTrials.gov 13 recruiting now early-phase tilt

Medulloblastoma: early-phase trial registry

13 of 30 indexed Medulloblastoma trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #519 of 28,707 conditions by registered trial count.

30 US clinical trials · 13 currently recruiting · #519 of 28,707 conditions by registered trial count

Medulloblastoma: 30 US clinical trials tracked, 13 recruiting.

Medulloblastoma is the subject of 30 registered US clinical trials on ClinicalTrials.gov, 13 of them currently open to new participants. 4 are in Phase 3-4 (later-stage) and 23 in Phase 1-2 (earlier-stage). The most active sponsor is St. Jude Children's Research Hospital, running 6 of these trials.

Enrollment posture brief

Registry condition medulloblastoma

OPEN 13 | RECR 43% | LATE 4 | EARLY 23 | RANK #519 | SPON 6

Nearest open-share peer: Bronchopulmonary Dysplasia (43% recruiting · 30 trials)

AML60%Medulloblastoma (this)43%Acute Myeloid Leukemia40%Anatomic Stage IA Breast Can26.7%Adult Acute Myeloid Leukemia0%
Open-enrollment share among volume-matched conditions near Medulloblastoma

Medulloblastoma lists 13 open slots (43% of 30 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Medulloblastoma on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Medulloblastoma is recruiting above its size-band peers.

    13 of 30 indexed trials (43.3%) are open to enrollment, against a 39.7% average across 762 conditions with 20-99 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Medulloblastoma research.

    St. Jude Children's Research Hospital accounts for 6 of 30 trials (20%). 20 distinct sponsors appear on at least one study for this condition label.

  3. Typical Medulloblastoma enrolment sits around 74 participants.

    Median target enrolment is 74 among the 30 trials that report a genuine target (sentinel values excluded). 17 of those (56.7%) plan for fewer than 100 participants.

  4. Medulloblastoma research is mostly interventional.

    29 interventional and 1 observational studies make up this index (96.7% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 112Phase 211Phase 32Phase 42

Open and recent trials

30 total, page 1 of 1

RECRUITING Phase 4 200 participants

68-Ga DOTATATE PET/MRI in the Diagnosis and Management of Somatostatin Receptor Positive CNS Tumors.

Weill Medical College of Cornell University

NCT04081701

RECRUITING 184 participants

CSIMEMPHIS: Long-term Follow-up of Medulloblastoma Survivors That Received Craniospinal Irradiation

St. Jude Children's Research Hospital

NCT07085325

RECRUITING Phase 1 146 participants

PLX038 in Primary Central Nervous System Tumors Containing MYC or MYCN Amplifications

National Cancer Institute (NCI)

NCT06161519

RECRUITING Phase 2 130 participants

Molecular and Clinical Risk-Directed Therapy for Infants and Young Children With Newly Diagnosed Medulloblastoma

St. Jude Children's Research Hospital

NCT05535166

RECRUITING Phase 2 118 participants

DFMO as Maintenance Therapy for Molecular High/Very High Risk and Relapsed Medulloblastoma

Giselle Sholler

NCT04696029

RECRUITING NA 74 participants

Individualized Treatment Plan in Children and Young Adults With Relapsed Medulloblastoma and Ependymoma

University of California, San Francisco

NCT05057702

RECRUITING Phase 1 65 participants

Lutathera for Treatment of Recurrent or Progressive High-Grade CNS Tumors

Nationwide Children's Hospital

NCT05278208

RECRUITING Phase 1 48 participants

Loc3CAR: Locoregional Delivery of B7-H3-CAR T Cells for Pediatric Patients With Primary CNS Tumors

St. Jude Children's Research Hospital

NCT05835687

RECRUITING Phase 1 37 participants

Chemo-immunotherapy Using Ibrutinib Plus Indoximod for Patients With Pediatric Brain Cancer

Theodore S. Johnson

NCT05106296

RECRUITING Phase 2 23 participants

Digoxin Medulloblastoma Study

H. Lee Moffitt Cancer Center and Research Institute

NCT06701812

RECRUITING Phase 1 20 participants

Flavored, Oral Irinotecan VAL-413 (Orotecan®) Given With Temozolomide for Treatment of Recurrent Pediatric Solid Tumors

Valent Technologies

NCT04337177

RECRUITING Phase 1 18 participants

Atovaquone Combined With Radiation in Children With Malignant Brain Tumors

Emory University

NCT06624371

RECRUITING Phase 1 18 participants

GPC2-CAR T Cell Therapy for Relapsed or Refractory Medulloblastoma in Children and Young Adults

Stanford University

NCT07087002

ACTIVE NOT RECRUITING Phase 2 660 participants

A Clinical and Molecular Risk-Directed Therapy for Newly Diagnosed Medulloblastoma

St. Jude Children's Research Hospital

NCT01878617

ACTIVE NOT RECRUITING Phase 2 503 participants

Methionine PET/CT Studies In Patients With Cancer

St. Jude Children's Research Hospital

NCT00840047

ACTIVE NOT RECRUITING Phase 3 379 participants

Chemotherapy and Radiation Therapy in Treating Young Patients With Newly Diagnosed, Previously Untreated, High-Risk Medulloblastoma/PNET

Children's Oncology Group

NCT00392327

ACTIVE NOT RECRUITING Phase 4 250 participants

HeadStart4: Newly Diagnosed Children (<10 y/o) With Medulloblastoma and Other CNS Embryonal Tumors

Parth Patel

NCT02875314

ACTIVE NOT RECRUITING Phase 2 130 participants

Pediatric Trial of Indoximod With Chemotherapy and Radiation for Relapsed Brain Tumors or Newly Diagnosed DIPG

Theodore S. Johnson

NCT04049669

ACTIVE NOT RECRUITING Phase 2 128 participants

Study Of Palbociclib Combined With Chemotherapy In Pediatric Patients With Recurrent/Refractory Solid Tumors

Pfizer

NCT03709680

ACTIVE NOT RECRUITING Phase 2 45 participants

Reduced Craniospinal Radiation Therapy and Chemotherapy in Treating Younger Patients With Newly Diagnosed WNT-Driven Medulloblastoma

Children's Oncology Group

NCT02724579

ACTIVE NOT RECRUITING Phase 1 35 participants

A Pilot Study of SurVaxM in Children Progressive or Relapsed Medulloblastoma, High Grade Glioma, Ependymoma and Newly Diagnosed Diffuse Intrinsic Pontine Glioma

Children's Oncology Group

NCT04978727

ACTIVE NOT RECRUITING Phase 1 32 participants

Phase I Study of APX005M in Pediatric Central Nervous System Tumors

Pediatric Brain Tumor Consortium

NCT03389802

ACTIVE NOT RECRUITING Phase 2 22 participants

Quantitative Assessment of Radiation-induced Neuroinflammation - A Proof of Principle Study

St. Jude Children's Research Hospital

NCT05128903

ACTIVE NOT RECRUITING Phase 1 10 participants

HER2-specific CAR T Cell Locoregional Immunotherapy for HER2-positive Recurrent/Refractory Pediatric CNS Tumors

Seattle Children's Hospital

NCT03500991

ACTIVE NOT RECRUITING Phase 1 10 participants

Brain Tumor-Specific Immune Cells (IL13Ralpha2-CAR T Cells) for the Treatment of Leptomeningeal Glioblastoma, Ependymoma, or Medulloblastoma

City of Hope Medical Center

NCT04661384

COMPLETED Phase 3 549 participants

Comparison of Radiation Therapy Regimens in Combination With Chemotherapy in Treating Young Patients With Newly Diagnosed Standard-Risk Medulloblastoma

Children's Oncology Group

NCT00085735

COMPLETED Phase 2 122 participants

Impact of Ga-68 DOTATOC PET-CT Imaging in Management of Neuroendocrine Tumors

Sue O'Dorisio

NCT02441062

COMPLETED NA 90 participants

Proton Beam Radiotherapy for Medulloblastoma and Pineoblastoma

Massachusetts General Hospital

NCT01063114

COMPLETED Phase 2 22 participants

A Phase II Study of Oral LDE225 in Patients With Hedge-Hog (Hh)-Pathway Activated Relapsed Medulloblastoma (MB)

Novartis Pharmaceuticals

NCT01708174

COMPLETED Phase 1 18 participants

Aflac ST0901 CHOANOME - Sirolimus in Solid Tumors

Emory University

NCT01331135

Phase Distribution

PhaseTrial count
Phase 1 12
Phase 2 11
Phase 3 2
Phase 4 2

Named interventions

Most-linked intervention names on Medulloblastoma records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Cyclophosphamide Drug
8 trials
Cisplatin Drug
5 trials
Temozolomide Drug
3 trials
Indoximod Drug
2 trials
Vincristine Drug
2 trials
Laboratory Biomarker Analysis Other
2 trials
68Ga-DOTATOC PET/CT Drug
1 trials
proton beam radiation Radiation
1 trials

US sites by state

Facility locations filed on Medulloblastoma trials. A trial with sites in several states counts in each.

California 14 trials
Tennessee 9 trials
Texas 8 trials
Georgia 8 trials
Pennsylvania 7 trials
Florida 7 trials
Ohio 6 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Medulloblastoma page

30 registered trials, 13 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Medulloblastoma condition card totals 30 registered trials; most-linked intervention Cyclophosphamide; top US site state California. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.