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ClinicalTrials.gov 8 recruiting now early-phase tilt small index

Retinal Degeneration: early-phase trial registry

8 of 18 indexed Retinal Degeneration trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #953 of 28,707 conditions by registered trial count.

18 US clinical trials · 8 currently recruiting · #953 of 28,707 conditions by registered trial count

Retinal Degeneration: 18 US clinical trials tracked, 8 recruiting.

Retinal Degeneration is the subject of 18 registered US clinical trials on ClinicalTrials.gov, 8 of them currently open to new participants. 1 are in Phase 3-4 (later-stage) and 7 in Phase 1-2 (earlier-stage). The most active sponsor is National Eye Institute (NEI), running 5 of these trials.

Enrollment posture brief

Registry condition retinal-degeneration

OPEN 8 | RECR 44% | LATE 1 | EARLY 7 | RANK #953 | SPON 5

Nearest open-share peer: Acute Ischemic Stroke (44% recruiting · 27 trials)

Retinal Degeneration (this)44%Arrhythmias, Cardiac27.8%Androgenetic Alopecia16.7%Anemia, Sickle Cell16.7%Acquired Immunodeficiency Sy5.6%
Open-enrollment share among volume-matched conditions near Retinal Degeneration

Retinal Degeneration lists 8 open slots (44% of 18 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Retinal Degeneration on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Retinal Degeneration is recruiting below its size-band peers.

    8 of 18 indexed trials (44.4%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Retinal Degeneration research.

    National Eye Institute (NEI) accounts for 5 of 18 trials (27.8%). 12 distinct sponsors appear on at least one study for this condition label.

  3. Most Retinal Degeneration trials plan to enrol fewer than 100 people.

    Median target enrolment is 54 among the 18 trials that report a genuine target (sentinel values excluded). 13 of those (72.2%) plan for fewer than 100 participants.

  4. Retinal Degeneration splits between interventional and observational designs.

    9 interventional and 9 observational studies make up this index (50% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 15Phase 22Phase 31

Open and recent trials

18 total, page 1 of 1

RECRUITING 930 participants

Cell Collection to Study Eye Diseases

National Eye Institute (NEI)

NCT01432847

RECRUITING 500 participants

Rod and Cone Mediated Function in Retinal Disease

National Eye Institute (NEI)

NCT02617966

RECRUITING 100 participants

Adaptive Optics Imaging of Outer Retinal Diseases

Food and Drug Administration (FDA)

NCT05355415

RECRUITING Phase 2 70 participants

SGLT2 Inhibitors in Geographic Atrophy

Washington University School of Medicine

NCT07174687

RECRUITING Phase 1 56 participants

Oral Metformin for Treatment of ABCA4 Retinopathy

National Eye Institute (NEI)

NCT04545736

RECRUITING Phase 1 54 participants

A Study to Investigate the Safety of OpCT-001 in Adults Who Have Primary Photoreceptor Disease (CLARICO)

BlueRock Therapeutics

NCT06789445

RECRUITING Phase 1 16 participants

A Repeat-Dose, Open-Label, Two Arm Safety and Efficacy Study of Two Doses of VP-001 Administered Intravitreally in Participants With Confirmed PRPF31 Mutation-Associated Retinal Dystrophy, Including Participants Previously Treated With VP001

PYC Therapeutics

NCT06852963

RECRUITING Phase 1 12 participants

MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby)

PYC Therapeutics

NCT06455826

ACTIVE NOT RECRUITING 250 participants

Investigating Geographic Atrophy Insights (i-GAIN) Natural History Study

Complement Therapeutics

NCT05797896

ACTIVE NOT RECRUITING 68 participants

Natural History of Eye Diseases Related to ABCA4 Mutations

National Eye Institute (NEI)

NCT01736293

ACTIVE NOT RECRUITING 44 participants

Rate of Progression of PCDH15-Related Retinal Degeneration in Usher Syndrome 1F

Jaeb Center for Health Research

NCT04765345

ACTIVE NOT RECRUITING 18 participants

Non-Interventional Long Term Follow-up Study of Participants Previously Enrolled in the RESTORE Study

Nanoscope Therapeutics

NCT06162585

COMPLETED 3,549 participants

Molecular Genetics of Retinal Degenerations

National Eye Institute (NEI)

NCT00231010

COMPLETED NA 36 participants

A Multi-Center Study of Reading Rehabilitation in Macular Disease

US Department of Veterans Affairs

NCT00746668

COMPLETED Phase 2 27 participants

Efficacy and Safety of MCO-010 Optogenetic Therapy in Adults With Retinitis Pigmentosa [RESTORE]

Nanoscope Therapeutics

NCT04945772

COMPLETED 26 participants

Natural History Study of CEP290-Related Retinal Degeneration

Editas Medicine

NCT03396042

COMPLETED Phase 1 24 participants

Safety And Tolerability Study Of RN6G In Subjects With Advanced Dry, Age-Related Macular Degeneration Including Geographic Atrophy

Pfizer

NCT01003691

COMPLETED Phase 3 14 participants

Study to Collect Safety and ECG Data on Brolucizumab 6 mg Intravitreal Treatment in Patients With Wet AMD

Novartis Pharmaceuticals

NCT03954626

Phase Distribution

PhaseTrial count
Phase 1 5
Phase 2 2
Phase 3 1

Named interventions

Most-linked intervention names on Retinal Degeneration records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

VP-001 Drug
2 trials
Module 3: Reading Practice with RSVP Behavioral
1 trials
Module 2: Control of Reading Eye Movements Behavioral
1 trials
Module 1: Visual Awareness and Eccentric Viewing Behavioral
1 trials
Sham Injection Procedure
1 trials
brolucuzumab 6 mg IVT Biological
1 trials
RN6G Biological
1 trials
Gene Therapy Product-MCO-010 Biological
1 trials

US sites by state

Facility locations filed on Retinal Degeneration trials. A trial with sites in several states counts in each.

Texas 8 trials
Maryland 8 trials
Florida 7 trials
California 5 trials
Oregon 4 trials
Michigan 4 trials
North Dakota 2 trials
Massachusetts 2 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Retinal Degeneration page

18 registered trials, 8 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Retinal Degeneration condition card totals 18 registered trials; most-linked intervention VP-001; top US site state Texas. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.