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ClinicalTrials.gov 21 recruiting now early-phase tilt

Down Syndrome: early-phase trial registry

21 of 55 indexed Down Syndrome trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #254 of 28,707 conditions by registered trial count.

55 US clinical trials · 21 currently recruiting · #254 of 28,707 conditions by registered trial count

Down Syndrome: 55 US clinical trials tracked, 21 recruiting.

Down Syndrome is the subject of 55 registered US clinical trials on ClinicalTrials.gov, 21 of them currently open to new participants. 5 are in Phase 3-4 (later-stage) and 10 in Phase 1-2 (earlier-stage). The most active sponsor is Sequenom, running 3 of these trials.

Enrollment posture brief

Registry condition down-syndrome

OPEN 21 | RECR 38% | LATE 5 | EARLY 10 | RANK #254 | SPON 3

Nearest open-share peer: Liver Diseases (38% recruiting · 34 trials)

Colorectal Neoplasms41.8%Down Syndrome (this)38%Menopause32.7%Constipation27.3%Brain and Central Nervous Sy1.8%
Open-enrollment share among volume-matched conditions near Down Syndrome

Down Syndrome lists 21 open slots (38% of 55 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Down Syndrome on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Down Syndrome recruits in line with its size-band peers.

    21 of 55 indexed trials (38.2%) are open to enrollment, against a 39.7% average across 762 conditions with 20-99 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. Sponsorship of Down Syndrome trials is spread across many organizations.

    Sequenom accounts for 3 of 55 trials (5.5%). 41 distinct sponsors appear on at least one study for this condition label.

  3. Typical Down Syndrome enrolment sits around 81 participants.

    Median target enrolment is 81 among the 55 trials that report a genuine target (sentinel values excluded). 31 of those (56.4%) plan for fewer than 100 participants.

  4. Down Syndrome research is mostly interventional.

    39 interventional and 16 observational studies make up this index (70.9% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 12Phase 28Phase 34Phase 41

Phase Distribution

PhaseTrial count
Phase 1 2
Phase 2 8
Phase 3 4
Phase 4 1

Named interventions

Most-linked intervention names on Down Syndrome records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Cytarabine Drug
3 trials
Placebo Drug
3 trials
Asparaginase Erwinia chrysanthemi Drug
2 trials
Blinatumomab Biological
2 trials
Dexamethasone Drug
2 trials
Biospecimen Collection Procedure
2 trials
Cyclophosphamide Drug
2 trials
Blood sampling for Laboratory Developed Test (LDT) analysis Other
1 trials

US sites by state

Facility locations filed on Down Syndrome trials. A trial with sites in several states counts in each.

Arizona 17 trials
California 15 trials
Ohio 11 trials
Massachusetts 10 trials
Pennsylvania 9 trials
Michigan 9 trials
Alabama 9 trials
Colorado 7 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Down Syndrome page

55 registered trials, 21 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 21 Down Syndrome trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • Sequenom sponsors the most Down Syndrome trials on record, review their full trial history before evaluating a specific study. See Sequenom's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Down Syndrome condition card totals 55 registered trials; most-linked intervention Cytarabine; top US site state Arizona. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.