Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.

ClinicalTrials.gov 6 recruiting now early-phase tilt small index

Diamond-Blackfan Anemia: early-phase trial registry

6 of 12 indexed Diamond-Blackfan Anemia trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #1,429 of 28,707 conditions by registered trial count.

12 US clinical trials · 6 currently recruiting · #1,429 of 28,707 conditions by registered trial count

Diamond-Blackfan Anemia: 12 US clinical trials tracked, 6 recruiting.

Diamond-Blackfan Anemia is the subject of 12 registered US clinical trials on ClinicalTrials.gov, 6 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 5 in Phase 1-2 (earlier-stage). The most active sponsor is St. Jude Children's Research Hospital, running 3 of these trials.

Enrollment posture brief

Registry condition diamond-blackfan-anemia

OPEN 6 | RECR 50% | LATE 0 | EARLY 5 | RANK #1429 | SPON 3

Nearest open-share peer: Abdominal Aortic Aneurysms (50% recruiting · 6 trials)

Diamond-Blackfan Anemia (thi…50%Acute Myeloid Leukemia in Re41.7%Adenocarcinoma of the Rectum41.7%Adherence, Patient16.7%Accelerated Phase Chronic My0%
Open-enrollment share among volume-matched conditions near Diamond-Blackfan Anemia

Diamond-Blackfan Anemia lists 6 open slots (50% of 12 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Diamond-Blackfan Anemia on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Diamond-Blackfan Anemia is recruiting above its size-band peers.

    6 of 12 indexed trials (50%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Diamond-Blackfan Anemia research.

    St. Jude Children's Research Hospital accounts for 3 of 12 trials (25%). 9 distinct sponsors appear on at least one study for this condition label.

  3. Most Diamond-Blackfan Anemia trials plan to enrol fewer than 100 people.

    Median target enrolment is 37 among the 12 trials that report a genuine target (sentinel values excluded). 8 of those (66.7%) plan for fewer than 100 participants.

  4. Diamond-Blackfan Anemia splits between interventional and observational designs.

    6 interventional and 6 observational studies make up this index (50% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 13Phase 22

Open and recent trials

12 total, page 1 of 1

RECRUITING 4,000 participants

Cancer in Inherited Bone Marrow Failure Syndromes

National Cancer Institute (NCI)

NCT00027274

RECRUITING 1,716 participants

Investigation of the Genetics of Hematologic Diseases

St. Jude Children's Research Hospital

NCT02720679

RECRUITING 1,500 participants

Familial Investigations of Childhood Cancer Predisposition

St. Jude Children's Research Hospital

NCT03050268

RECRUITING Phase 2 20 participants

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

Mitchell Cairo

NCT04099966

RECRUITING 10 participants

Mobilization of CD34+ Peripheral Blood Stem Cells in Patients With Diamond Blackfan Anemia Syndrome (DBAS)

Northwell Health

NCT07186179

RECRUITING Phase 1 5 participants

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Paul Szabolcs

NCT03653338

ACTIVE NOT RECRUITING Phase 1 37 participants

CD34+ (Non-Malignant) Stem Cell Selection for Patients Receiving Allogeneic Stem Cell Transplantation

Diane George

NCT01966367

COMPLETED 423 participants

Multi-Center Study of Iron Overload: Survey Study (MCSIO)

UCSF Benioff Children's Hospital Oakland

NCT01913548

COMPLETED Phase 1 40 participants

Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First Remission

University of California, San Francisco

NCT00305708

COMPLETED Phase 2 22 participants

Stem Cell Transplant for Hemoglobinopathy

Masonic Cancer Center, University of Minnesota

NCT00176852

COMPLETED 20 participants

Multi-Center Study of Iron Overload: Pilot Study

UCSF Benioff Children's Hospital Oakland

NCT01114776

COMPLETED NA 4 participants

Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias

St. Jude Children's Research Hospital

NCT00244010

Phase Distribution

PhaseTrial count
Phase 1 3
Phase 2 2

Named interventions

Most-linked intervention names on Diamond-Blackfan Anemia records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Campath, Fludarabine, Cyclophosphamide Drug
1 trials
Busulfan, Cyclophosphamide, ATG, GCSF Drug
1 trials
Busulfan, Fludarabine, ATG, TLI Drug
1 trials
Allogeneic stem cell transplant Device
1 trials
anti-thymocyte globulin Biological
1 trials
allogeneic bone marrow transplantation Procedure
1 trials
busulfan Drug
1 trials
CD34 Stem Cell Selection Therapy Biological
1 trials

US sites by state

Facility locations filed on Diamond-Blackfan Anemia trials. A trial with sites in several states counts in each.

Tennessee 4 trials
New York 3 trials
California 3 trials
Pennsylvania 2 trials
North Carolina 1 trials
Minnesota 1 trials
Maryland 1 trials
Illinois 1 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Diamond-Blackfan Anemia page

12 registered trials, 6 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Diamond-Blackfan Anemia condition card totals 12 registered trials; most-linked intervention Campath, Fludarabine, Cyclophosphamide; top US site state Tennessee. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.