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ClinicalTrials.gov 6 recruiting now official registry

Diamond-Blackfan Anemia clinical trials

6 of 12 indexed Diamond-Blackfan Anemia trials are currently recruiting.

12 US clinical trials · 6 currently recruiting

Diamond-Blackfan Anemia is the subject of 12 registered US clinical trials on ClinicalTrials.gov, 6 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 5 in Phase 1-2 (earlier-stage). The most active sponsor is St. Jude Children's Research Hospital, running 3 of these trials.

The research picture

Diamond-Blackfan Anemia has 12 registered US clinical trials, 6 of them open to new participants right now, about 50% of the total.

6
recruiting participants now
50%
of trials open to enrollment
0
in Phase 3–4 (later-stage)
3
top sponsor: St. Jude Children's Research Hospital
Phase 13Phase 22

Active & Recent Trials

12 total, page 1 of 1

RECRUITING 4,000 participants

Cancer in Inherited Bone Marrow Failure Syndromes

National Cancer Institute (NCI)

NCT00027274

RECRUITING 1,716 participants

Investigation of the Genetics of Hematologic Diseases

St. Jude Children's Research Hospital

NCT02720679

RECRUITING 1,500 participants

Familial Investigations of Childhood Cancer Predisposition

St. Jude Children's Research Hospital

NCT03050268

RECRUITING Phase 2 20 participants

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

Mitchell Cairo

NCT04099966

RECRUITING 10 participants

Mobilization of CD34+ Peripheral Blood Stem Cells in Patients With Diamond Blackfan Anemia Syndrome (DBAS)

Northwell Health

NCT07186179

RECRUITING Phase 1 5 participants

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Paul Szabolcs

NCT03653338

ACTIVE NOT RECRUITING Phase 1 37 participants

CD34+ (Non-Malignant) Stem Cell Selection for Patients Receiving Allogeneic Stem Cell Transplantation

Diane George

NCT01966367

COMPLETED 423 participants

Multi-Center Study of Iron Overload: Survey Study (MCSIO)

UCSF Benioff Children's Hospital Oakland

NCT01913548

COMPLETED Phase 1 40 participants

Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First Remission

University of California, San Francisco

NCT00305708

COMPLETED Phase 2 22 participants

Stem Cell Transplant for Hemoglobinopathy

Masonic Cancer Center, University of Minnesota

NCT00176852

COMPLETED 20 participants

Multi-Center Study of Iron Overload: Pilot Study

UCSF Benioff Children's Hospital Oakland

NCT01114776

COMPLETED NA 4 participants

Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias

St. Jude Children's Research Hospital

NCT00244010

Phase Distribution

PhaseTrial count
Phase 1 3
Phase 2 2

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

Reading the Diamond-Blackfan Anemia Trial Landscape

12 indexed Diamond-Blackfan Anemia studies · 6 recruiting (50%).

Phase mix: 0 late (III/IV) vs 5 early (I/II).

Top sponsor: St. Jude Children's Research Hospital (3 trials), 8 others listed. 12 shown below, recruiting first.

How to read this condition's trial landscape

That ratio is a useful proxy for activity level: a high share of recruiting studies often signals that research interest is current and that new enrollment opportunities are appearing, while a low share typically means the field is dominated by completed or follow-up work where most participant spots have already been filled. These counts reflect the public registry only and include studies at every stage of design, so they should be read as an index of research attention rather than as a measure of treatment availability.

Phase 1 and Phase 2 studies focus on early safety signals, dosing, and preliminary effect, while Phase 3 studies are typically the larger efficacy and safety trials submitted toward regulatory review, and Phase 4 studies follow approved interventions in real-world use. A condition weighted toward later phases often reflects a mature research pipeline with several interventions already close to or past approval, whereas a heavier early-phase tilt suggests the field is still exploring new mechanisms and candidate approaches.

All figures are derived from the public ClinicalTrials.gov dataset maintained by the National Library of Medicine and are reproduced here for reference. Inclusion of a trial, sponsor, or intervention on this page is neither an endorsement nor a recommendation, eligibility, protocol changes, and site-level status can shift frequently, so always verify current details on ClinicalTrials.gov and consult a qualified healthcare provider before acting on anything you see here.

Frequently Asked Questions

How many clinical trials are there for Diamond-Blackfan Anemia?

PlainTrial tracks 12 US clinical trials for Diamond-Blackfan Anemia, of which 6 are currently recruiting participants. Data sourced from ClinicalTrials.gov.

How do I find a recruiting trial for Diamond-Blackfan Anemia?

Use the trial list above filtered by "Recruiting" status, or visit our trial finder at /recruiting to search by condition and state. Always discuss trial participation with your healthcare provider before enrolling.

Is this data current?

Data is sourced from ClinicalTrials.gov and reflects our most recent data pull. Trial status may have changed since then. Always verify current information at ClinicalTrials.gov before making decisions about participation.

Disclaimer: This information is provided for informational purposes only and does not constitute professional advice. Data is sourced from ClinicalTrials.gov (National Library of Medicine). Consult a qualified professional before making decisions based on this data.

Source: ClinicalTrials.gov (NIH/NLM) ClinicalTrials.gov AACT registry · 2026 Trial counts and statuses sourced from ClinicalTrials.gov. Sponsor counts include both industry and federal/academic sponsors.

Verify with NIH →

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page aggregates every registered trial for this condition, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.