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2026 data Public-data reference. official source

Muscular Dystrophy

Open-data reference.

12 US clinical trials · 10 currently recruiting

Active & Recent Trials

RECRUITING 3,500 participants

Study of Inherited Neurological Disorders

National Institute of Neurological Disorders and Stroke (NINDS)

NCT00004568

RECRUITING 3,000 participants

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

University of Rochester

NCT00082108

RECRUITING 2,000 participants

Genetics of Cardiovascular and Neuromuscular Disease

University of Chicago

NCT00138931

RECRUITING 190 participants

Clinical Trial Readiness for the Dystroglycanopathies

Katherine Mathews

NCT00313677

RECRUITING 150 participants

Investigational Use of Neuromuscular Ultrasound

National Institute of Neurological Disorders and Stroke (NINDS)

NCT05237973

RECRUITING Phase 2 50 participants

Vasodilator and Exercise Study for DMD (VASO-REx)

University of Florida

NCT06290713

RECRUITING NA 44 participants

Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement Disorders

National Institutes of Health Clinical Center (CC)

NCT05726591

RECRUITING NA 36 participants

Nomad P-KAFO Study

Shirley Ryan AbilityLab

NCT05644522

RECRUITING NA 27 participants

BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With Tetraplegia

Leigh R. Hochberg, MD, PhD.

NCT00912041

RECRUITING Phase 1 10 participants

A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)

AskBio

NCT05230459

COMPLETED 448 participants

Arrhythmias in Myotonic Muscular Dystrophy

Indiana University School of Medicine

NCT00622453

COMPLETED 230 participants

Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases

Nemours Children's Clinic

NCT02532244

Phase Distribution

PhaseTrial count
Early Phase 1 1
Phase 2 1

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

Reading the Muscular Dystrophy Trial Landscape

ClinicalTrials.gov lists 12 US studies indexed under Muscular Dystrophy, and 10 of those are currently open to recruitment — roughly 83% of the total volume on the registry. That ratio is a useful proxy for activity level: a high share of recruiting studies often signals that research interest is current and that new enrollment opportunities are appearing, while a low share typically means the field is dominated by completed or follow-up work where most participant spots have already been filled. These counts reflect the public registry only and include studies at every stage of design, so they should be read as an index of research attention rather than as a measure of treatment availability.

The phase distribution for Muscular Dystrophy shows 0 late-stage studies (Phase 3 and Phase 4 combined) alongside 2 earlier-phase entries (Phase 1 through Phase 2). Phase 1 and Phase 2 studies focus on early safety signals, dosing, and preliminary effect, while Phase 3 studies are typically the larger efficacy and safety trials submitted toward regulatory review, and Phase 4 studies follow approved interventions in real-world use. A condition weighted toward later phases often reflects a mature research pipeline with several interventions already close to or past approval, whereas a heavier early-phase tilt suggests the field is still exploring new mechanisms and candidate approaches.

Top sponsor activity for Muscular Dystrophy is led by National Institute of Neurological Disorders and Stroke (NINDS) with 2 indexed trials, alongside 9 other organizations in the top contributor list. The list on this page surfaces up to 12 of the most relevant recent and active entries, ordered with recruiting studies first so practical options are visible. All figures are derived from the public ClinicalTrials.gov dataset maintained by the National Library of Medicine and are reproduced here for reference. Inclusion of a trial, sponsor, or intervention on this page is neither an endorsement nor a recommendation — eligibility, protocol changes, and site-level status can shift frequently, so always verify current details on ClinicalTrials.gov and consult a qualified healthcare provider before acting on anything you see here.

Frequently Asked Questions

How many clinical trials are there for Muscular Dystrophy?

PlainTrial tracks 12 US clinical trials for Muscular Dystrophy, of which 10 are currently recruiting participants. Data sourced from ClinicalTrials.gov.

How do I find a recruiting trial for Muscular Dystrophy?

Use the trial list above filtered by "Recruiting" status, or visit our trial finder at /recruiting to search by condition and state. Always discuss trial participation with your healthcare provider before enrolling.

Is this data current?

Data is sourced from ClinicalTrials.gov and reflects our most recent data pull. Trial status may have changed since then. Always verify current information at ClinicalTrials.gov before making decisions about participation.

Related

Data sourced from official U.S. government datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Disclaimer: This information is provided for informational purposes only and does not constitute professional advice. Data is sourced from ClinicalTrials.gov (National Library of Medicine). Consult a qualified professional before making decisions based on this data.

Source: ClinicalTrials.gov (NIH/NLM) ClinicalTrials.gov AACT registry · 2024 Trial counts and statuses sourced from ClinicalTrials.gov. Sponsor counts include both industry and federal/academic sponsors.

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