Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.
Fanconi Anemia: early-phase trial registry
8 of 16 indexed Fanconi Anemia trials are currently recruiting, with more weight in Phase 1-2.
Corpus placement: #1,060 of 28,707 conditions by registered trial count.
16 US clinical trials · 8 currently recruiting · #1,060 of 28,707 conditions by registered trial count
Fanconi Anemia: 16 US clinical trials tracked, 8 recruiting.
Fanconi Anemia is the subject of 16 registered US clinical trials on ClinicalTrials.gov, 8 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 9 in Phase 1-2 (earlier-stage). The most active sponsor is Masonic Cancer Center, University of Minnesota, running 3 of these trials.
Enrollment posture brief
Registry condition fanconi-anemia
OPEN 8 | RECR 50% | LATE 0 | EARLY 9 | RANK #1060 | SPON 3
Volume-matched condition peers
Nearest open-share peer: Abdominal Aortic Aneurysms (50% recruiting · 6 trials)
Fanconi Anemia lists 8 open slots (50% of 16 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Fanconi Anemia on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Fanconi Anemia is recruiting above its size-band peers.
8 of 16 indexed trials (50%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
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One sponsor concentrates Fanconi Anemia research.
Masonic Cancer Center, University of Minnesota accounts for 3 of 16 trials (18.8%). 10 distinct sponsors appear on at least one study for this condition label.
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Most Fanconi Anemia trials plan to enrol fewer than 100 people.
Median target enrolment is 40 among the 16 trials that report a genuine target (sentinel values excluded). 12 of those (75%) plan for fewer than 100 participants.
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Fanconi Anemia research is mostly interventional.
13 interventional and 3 observational studies make up this index (81.3% interventional). Study type is sponsor-reported on ClinicalTrials.gov.
Open and recent trials
16 total, page 1 of 1
Cancer in Inherited Bone Marrow Failure Syndromes
National Cancer Institute (NCI)
NCT00027274
Defining the Natural History of Squamous Cell Carcinoma in Fanconi Anemia
National Cancer Institute (NCI)
NCT05687149
Role of Acetaldehyde in the Development of Oral Cancer
Masonic Cancer Center, University of Minnesota
NCT05973656
HSCT for Patients With Fanconi Anemia Using Risk-Adjusted Chemotherapy
Children's Hospital Medical Center, Cincinnati
NCT02143830
Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders
Masonic Cancer Center, University of Minnesota
NCT03579875
Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
NCT04232085
Experience and Management of Cancer Screening-Related Anxiety in Fanconi Anemia
National Cancer Institute (NCI)
NCT06744283
Depleted Donor Stem Cell Transplant in Children and Adults With Fanconi Anemia After Being Conditioned With a Regimen Containing Briquilimab
Porteus, Matthew, MD
NCT04784052
Widefield Fluorescence and Reflectance Imaging Systems and Oral Tissue Samples in Monitoring Participants at Risk for Developing Oral Cancer
M.D. Anderson Cancer Center
NCT00542373
Quercetin Chemoprevention for Squamous Cell Carcinoma in Patients With Fanconi Anemia
Children's Hospital Medical Center, Cincinnati
NCT03476330
Eltrombopag for People With Fanconi Anemia
National Heart, Lung, and Blood Institute (NHLBI)
NCT03206086
Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First Remission
University of California, San Francisco
NCT00305708
Hematopoietic Stem Cell Transplantation for Treatment of Patients With Fanconi Anemia Lacking a Genotypically Identical Donor, Using Total Body Irradiation, Cyclophosphamide and Fludarabine
Memorial Sloan Kettering Cancer Center
NCT00595127
Hematopoietic Stem Cell Transplantation in High Risk Patients With Fanconi Anemia
Masonic Cancer Center, University of Minnesota
NCT00258427
Time-restricted Feeding to Reduce Inflammation in Fanconi Anemia
Children's Hospital Medical Center, Cincinnati
NCT05598515
Hematopoietic Stem Cell Transplant for Fanconi Anemia
Medical College of Wisconsin
NCT01071239
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 1 | 2 |
| Phase 2 | 7 |
Top Sponsors
Named interventions
Most-linked intervention names on Fanconi Anemia records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Fanconi Anemia trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Fanconi Anemia page
16 registered trials, 8 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 8 Fanconi Anemia trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- Masonic Cancer Center, University of Minnesota sponsors the most Fanconi Anemia trials on record, review their full trial history before evaluating a specific study. See Masonic Cancer Center, University of Minnesota's trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Fanconi Anemia condition card totals 16 registered trials; most-linked intervention Cyclophosphamide; top US site state Maryland. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.