Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.
Tuberous Sclerosis clinical trials
5 of 7 indexed Tuberous Sclerosis trials are currently recruiting.
Corpus placement: #2,497 of 28,707 conditions by registered trial count.
7 US clinical trials · 5 currently recruiting · #2,497 of 28,707 conditions by registered trial count
Tuberous Sclerosis: 7 US clinical trials tracked, 5 recruiting.
Tuberous Sclerosis is the subject of 7 registered US clinical trials on ClinicalTrials.gov, 5 of them currently open to new participants. The most active sponsor is National Heart, Lung, and Blood Institute (NHLBI), running 4 of these trials.
Enrollment posture brief
Registry condition tuberous-sclerosis
OPEN 5 | RECR 71% | LATE 0 | EARLY 0 | RANK #2497 | SPON 4
Volume-matched condition peers
Nearest open-share peer: Advanced Endometrial Carcinoma (71% recruiting · 7 trials)
Tuberous Sclerosis lists 5 open slots (71% of 7 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Tuberous Sclerosis on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Tuberous Sclerosis is recruiting above its size-band peers.
5 of 7 indexed trials (71.4%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
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One sponsor concentrates Tuberous Sclerosis research.
National Heart, Lung, and Blood Institute (NHLBI) accounts for 4 of 7 trials (57.1%). 4 distinct sponsors appear on at least one study for this condition label.
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Typical Tuberous Sclerosis enrolment sits around 400 participants.
Median target enrolment is 400 among the 7 trials that report a genuine target (sentinel values excluded). 2 of those (28.6%) plan for fewer than 100 participants.
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Tuberous Sclerosis research leans observational.
1 interventional and 6 observational studies make up this index (14.3% interventional). Study type is sponsor-reported on ClinicalTrials.gov.
Open and recent trials
7 total, page 1 of 1
TSC Biosample Repository and Natural History Database
National Tuberous Sclerosis Association
NCT05676099
Role of Genetic Factors in the Development of Lung Disease
National Heart, Lung, and Blood Institute (NHLBI)
NCT00001532
Study of the Disease Process of Lymphangioleiomyomatosis
National Heart, Lung, and Blood Institute (NHLBI)
NCT00001465
Study of Skin Tumors in Tuberous Sclerosis
National Heart, Lung, and Blood Institute (NHLBI)
NCT00001975
Web Intervention for Parents of Youth With Genetic Syndromes (WINGS)
Rush University Medical Center
NCT06139172
Autism Spectrum Disorder (ASD) and Intellectual Disability (ID) Determinants in Tuberous Sclerosis Complex (TSC)
Boston Children's Hospital
NCT02461459
Effect of Fasting on the Size of Abdominal Lymphatic Tumors in Women
National Heart, Lung, and Blood Institute (NHLBI)
NCT00552955
Phase Distribution
Phase data not available
Top Sponsors
Named interventions
Most-linked intervention names on Tuberous Sclerosis records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Tuberous Sclerosis trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Tuberous Sclerosis page
7 registered trials, 5 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 5 Tuberous Sclerosis trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- National Heart, Lung, and Blood Institute (NHLBI) sponsors the most Tuberous Sclerosis trials on record, review their full trial history before evaluating a specific study. See National Heart, Lung, and Blood Institute (NHLBI)'s trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Tuberous Sclerosis condition card totals 7 registered trials; most-linked intervention Toshibia Aquilion One CT; top US site state Maryland. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.