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ClinicalTrials.gov 36 recruiting now early-phase tilt

Refractory Acute Myeloid Leukemia: early-phase trial registry

36 of 64 indexed Refractory Acute Myeloid Leukemia trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #215 of 28,707 conditions by registered trial count.

64 US clinical trials · 36 currently recruiting · #215 of 28,707 conditions by registered trial count

Refractory Acute Myeloid Leukemia: 64 US clinical trials tracked, 36 recruiting.

Refractory Acute Myeloid Leukemia is the subject of 64 registered US clinical trials on ClinicalTrials.gov, 36 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 64 in Phase 1-2 (earlier-stage). The most active sponsor is M.D. Anderson Cancer Center, running 20 of these trials.

Enrollment posture brief

Registry condition refractory-acute-myeloid-leukemia

OPEN 36 | RECR 56% | LATE 0 | EARLY 64 | RANK #215 | SPON 20

Nearest open-share peer: Alcohol Intoxication (56% recruiting · 16 trials)

Refractory Acute Myeloid (th…56%Anatomic Stage I Breast Canc54.7%Congenital Heart Disease51.6%Non-Hodgkin's Lymphoma18.8%Diabetic Macular Edema15.6%
Open-enrollment share among volume-matched conditions near Refractory Acute Myeloid Leukemia

Refractory Acute Myeloid Leukemia lists 36 open slots (56% of 64 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Refractory Acute Myeloid Leukemia on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Refractory Acute Myeloid Leukemia is recruiting above its size-band peers.

    36 of 64 indexed trials (56.3%) are open to enrollment, against a 39.7% average across 762 conditions with 20-99 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Refractory Acute Myeloid Leukemia research.

    M.D. Anderson Cancer Center accounts for 20 of 64 trials (31.3%). 23 distinct sponsors appear on at least one study for this condition label.

  3. Most Refractory Acute Myeloid Leukemia trials plan to enrol fewer than 100 people.

    Median target enrolment is 32 among the 64 trials that report a genuine target (sentinel values excluded). 58 of those (90.6%) plan for fewer than 100 participants.

  4. Refractory Acute Myeloid Leukemia research is mostly interventional.

    64 interventional and 0 observational studies make up this index (100% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 152Phase 212

Open and recent trials

64 total, page 1 of 2

RECRUITING Phase 1 170 participants

A Study of BH-30236 in Relapsed/ Refractory Acute Myelogenous Leukemia and Higher Risk Myelodysplastic Syndrome

BlossomHill Therapeutics

NCT06501196

RECRUITING Phase 1 120 participants

CLAG-M or FLAG-Ida Chemotherapy and Reduced-Intensity Conditioning Donor Stem Cell Transplant for the Treatment of Relapsed or Refractory Acute Myeloid Leukemia, Myelodysplastic Syndrome, or Chronic Myelomonocytic Leukemia

Fred Hutchinson Cancer Center

NCT04375631

RECRUITING Phase 1 120 participants

ONC201 in Treating Patients With Relapsed or Refractory Acute Leukemia or High-Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT02392572

RECRUITING Phase 1 116 participants

Venetoclax With Combination Chemotherapy in Treating Patients With Newly Diagnosed or Relapsed or Refractory Acute Myeloid Leukemia

M.D. Anderson Cancer Center

NCT03214562

RECRUITING Phase 1 97 participants

Azacitidine, Venetoclax, and Gilteritinib in Treating Patients With Recurrent/Refractory FLT3-Mutated Acute Myeloid Leukemia, Chronic Myelomonocytic Leukemia, or High-Risk Myelodysplastic Syndrome/Myeloproliferative Neoplasm

M.D. Anderson Cancer Center

NCT04140487

RECRUITING Phase 1 96 participants

Ivosidenib and Venetoclax With or Without Azacitidine in Treating Patients With IDH1 Mutated Hematologic Malignancies

M.D. Anderson Cancer Center

NCT03471260

RECRUITING Phase 1 84 participants

Decitabine/Cedazuridine and Venetoclax in Combination With Ivosidenib or Enasidenib for the Treatment of Relapsed or Refractory Acute Myeloid Leukemia

M.D. Anderson Cancer Center

NCT04774393

RECRUITING Phase 1 80 participants

Cladribine, Idarubicin, Cytarabine, and Quizartinib in Treating Patients With Newly Diagnosed, Relapsed, or Refractory Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT04047641

RECRUITING Phase 1 75 participants

211^At-BC8-B10 Before Donor Stem Cell Transplant in Treating Patients With High-Risk Acute Myeloid Leukemia, Acute Lymphoblastic Leukemia, Myelodysplastic Syndrome, or Mixed-Phenotype Acute Leukemia

Fred Hutchinson Cancer Center

NCT03128034

RECRUITING Phase 1 73 participants

Quizartinib, Decitabine, and Venetoclax in Treating Participants With Untreated or Relapsed Acute Myeloid Leukemia or High Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT03661307

RECRUITING Phase 1 62 participants

Venetoclax and CLAG-M for the Treatment of Acute Myeloid Leukemia and High-Grade Myeloid Neoplasms

University of Washington

NCT04797767

RECRUITING Phase 1 60 participants

Eltanexor and Venetoclax in Relapsed or Refractory Myelodysplastic Syndrome and Acute Myeloid Leukemia

Vanderbilt-Ingram Cancer Center

NCT06399640

RECRUITING Phase 1 54 participants

Pembrolizumab and Decitabine With or Without Venetoclax in Treating Patients With Acute Myeloid Leukemia or Myelodysplastic Syndrome That Is Newly-Diagnosed, Recurrent, or Refractory

City of Hope Medical Center

NCT03969446

RECRUITING Phase 1 54 participants

Testing the Anti-cancer Drug, Cirtuvivint, and Its Combination With ASTX727 to Improve Outcomes in Patients With Acute Myeloid Leukemia and Myelodysplastic Syndromes

National Cancer Institute (NCI)

NCT06484062

RECRUITING Phase 1 52 participants

Liposomal Cytarabine and Daunorubicin (CPX-351) and Quizartinib for the Treatment of Acute Myeloid Leukemia and High Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT04128748

RECRUITING Phase 2 52 participants

Liposome-encapsulated Daunorubicin-Cytarabine and Venetoclax in Treating Participants With Relapsed, Refractory or Untreated Acute Myeloid Leukemia

M.D. Anderson Cancer Center

NCT03629171

RECRUITING Phase 1 51 participants

Ruxolitinib in Combination With Venetoclax With and Without Azacitidine in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia

Jennifer Saultz

NCT03874052

RECRUITING Phase 2 50 participants

Enasidenib and Azacitidine in Treating Patients With Recurrent or Refractory Acute Myeloid Leukemia and IDH2 Gene Mutation

M.D. Anderson Cancer Center

NCT03683433

RECRUITING Phase 1 42 participants

TAK-243 in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia or Myelodysplastic Syndromes With Increased Blasts

National Cancer Institute (NCI)

NCT03816319

RECRUITING Phase 1 42 participants

ASTX727, Venetoclax, and Gilteritinib for the Treatment of Newly Diagnosed, Relapsed or Refractory FLT3-Mutated Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT05010122

RECRUITING Phase 1 36 participants

Chemotherapy (Decitabine in Combination With FLAG-Ida) and Total-Body Irradiation Followed by Donor Stem Cell Transplant for the Treatment of Adults With Myeloid Malignancies at High Risk of Relapse

Fred Hutchinson Cancer Center

NCT06928662

RECRUITING Phase 1 30 participants

8-Chloroadenosine in Combination With Venetoclax for the Treatment of Patients With Relapsed/Refractory Acute Myeloid Leukemia

City of Hope Medical Center

NCT05263284

RECRUITING Phase 1 30 participants

211At-BC8-B10 Followed by Donor Stem Cell Transplant in Treating Patients With Relapsed or Refractory High-Risk Acute Leukemia or Myelodysplastic Syndrome

Fred Hutchinson Cancer Center

NCT03670966

RECRUITING Phase 2 30 participants

CPX-351 and Ivosidenib for the Treatment of IDH1 Mutated Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT04493164

RECRUITING Phase 1 30 participants

SNDX-5613 and Gilteritinib for the Treatment of Relapsed or Refractory FLT3-Mutated Acute Myeloid Leukemia and Concurrent MLL-Rearrangement or NPM1 Mutation

Uma Borate

NCT06222580

RECRUITING Phase 1 28 participants

Vyxeos for Re-induction Treatment of Acute Myeloid Leukemia Patients With Persistent Disease After Induction

Ohio State University Comprehensive Cancer Center

NCT04049539

RECRUITING Phase 1 27 participants

CD33-CAR T Cell Therapy for the Treatment of Recurrent or Refractory Acute Myeloid Leukemia

City of Hope Medical Center

NCT05672147

RECRUITING Phase 1 26 participants

Genetically Engineered Cells (CD83 CAR T Cells) for the Treatment of Relapsed or Refractory Acute Myeloid Leukemia

Roswell Park Cancer Institute

NCT06871410

RECRUITING Phase 1 24 participants

Tazemetostat and Palbociclib With CPX-351for R/R AML

Thomas Jefferson University

NCT05627232

RECRUITING Phase 1 24 participants

Study of Revumenib, Azacitidine, and Venetoclax in Pediatric and Young Adult Patients With Refractory or Relapsed Acute Myeloid Leukemia

St. Jude Children's Research Hospital

NCT06177067

RECRUITING Phase 1 20 participants

Tagraxofusp and Low-Intensity Chemotherapy for CD123-Positive Relapsed or Refractory AML

Stanford University

NCT06561152

RECRUITING Phase 1 18 participants

CER-1236 in Patients With Acute Myeloid Leukemia (AML)

CERo Therapeutics Holdings

NCT06834282

RECRUITING Phase 1 18 participants

Venetoclax and Bomedemstat in Patients With Relapsed/Refractory Acute Myeloid Leukemia

Terrence J Bradley, MD

NCT05597306

RECRUITING Phase 1 15 participants

A Study of CD371-YSNVZIL-18 CAR T Cells in People With Acute Myeloid Leukemia

Memorial Sloan Kettering Cancer Center

NCT06017258

RECRUITING Phase 1 12 participants

MiRisten for the Treatment of Relapsed or Refractory Acute Myeloid Leukemia

City of Hope Medical Center

NCT07025564

RECRUITING Phase 1 12 participants

A Phase 1 Study of AOH1996 in Patients With Relapsed/Refractory Acute Myeloid Leukemia

City of Hope Medical Center

NCT06763341

ACTIVE NOT RECRUITING Phase 1 144 participants

FHD-286 as Monotherapy or Combination Therapy in Subjects With Advanced Hematologic Malignancies

Foghorn Therapeutics

NCT04891757

ACTIVE NOT RECRUITING Phase 2 85 participants

Venetoclax and ASTX727 for the Treatment of Relapsed, Refractory, or Newly Diagnosed Acute Myeloid Leukemia

M.D. Anderson Cancer Center

NCT04746235

ACTIVE NOT RECRUITING Phase 1 74 participants

Sorafenib, Busulfan and Fludarabine in Treating Patients With Recurrent or Refractory Acute Myeloid Leukemia Undergoing Donor Stem Cell Transplant

M.D. Anderson Cancer Center

NCT03247088

ACTIVE NOT RECRUITING Phase 1 58 participants

Testing a New Chemotherapy Drug, KRT-232 (AMG-232) in Combination With Decitabine and Venetoclax in Patients With Acute Myeloid Leukemia

National Cancer Institute (NCI)

NCT03041688

ACTIVE NOT RECRUITING Phase 1 54 participants

Ipilimumab and Decitabine in Treating Patients With Relapsed or Refractory Myelodysplastic Syndrome or Acute Myeloid Leukemia

National Cancer Institute (NCI)

NCT02890329

ACTIVE NOT RECRUITING Phase 2 50 participants

Liposome-encapsulated Daunorubicin-Cytarabine and Gemtuzumab Ozogamicin in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia (AML) or High Risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT03672539

ACTIVE NOT RECRUITING Phase 1 48 participants

Testing the Addition of an Anti-cancer Drug, M3814, to the Usual Treatment (Mitoxantrone, Etoposide, and Cytarabine) for Relapsed or Refractory Acute Myeloid Leukemia

National Cancer Institute (NCI)

NCT03983824

ACTIVE NOT RECRUITING Phase 1 44 participants

Nintedanib and Azacitidine in Treating Participants With HOX Gene Overexpression Relapsed or Refractory Acute Myeloid Leukemia

Northwestern University

NCT03513484

ACTIVE NOT RECRUITING Phase 1 37 participants

Study of Selinexor and Venetoclax in Combination With Chemotherapy in Pediatric and Young Adult Patients With Refractory or Relapsed Acute Myeloid Leukemia

St. Jude Children's Research Hospital

NCT04898894

ACTIVE NOT RECRUITING Phase 1 32 participants

Palbociclib and Sorafenib, Decitabine, or Dexamethasone in Treating Patients With Recurrent or Refractory Leukemia

M.D. Anderson Cancer Center

NCT03132454

ACTIVE NOT RECRUITING Phase 1 30 participants

Pevonedistat and Decitabine in Treating Patients With High Risk Acute Myeloid Leukemia

City of Hope Medical Center

NCT03009240

ACTIVE NOT RECRUITING Phase 2 25 participants

Topotecan Hydrochloride and Carboplatin With or Without Veliparib in Treating Advanced Myeloproliferative Disorders and Acute Myeloid Leukemia or Chronic Myelomonocytic Leukemia

National Cancer Institute (NCI)

NCT03289910

ACTIVE NOT RECRUITING Phase 2 20 participants

Venetoclax in Combination With Decitabine and Cedazuridine for the Treatment of Relapsed or Refractory Acute Myeloid Leukemia

M.D. Anderson Cancer Center

NCT04975919

ACTIVE NOT RECRUITING Phase 2 20 participants

Decitabine, Venetoclax, and Ponatinib for the Treatment of Philadelphia Chromosome-Positive Acute Myeloid Leukemia or Myeloid Blast Phase or Accelerated Phase Chronic Myelogenous Leukemia

M.D. Anderson Cancer Center

NCT04188405

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Phase Distribution

PhaseTrial count
Phase 1 52
Phase 2 12

Named interventions

Most-linked intervention names on Refractory Acute Myeloid Leukemia records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Venetoclax Drug
21 trials
Cytarabine Drug
14 trials
Biospecimen Collection Procedure
13 trials
Decitabine Drug
11 trials
Azacitidine Drug
8 trials
Bone Marrow Aspiration Procedure
8 trials
Filgrastim Biological
7 trials
Fludarabine Drug
7 trials

US sites by state

Facility locations filed on Refractory Acute Myeloid Leukemia trials. A trial with sites in several states counts in each.

Texas 28 trials
California 23 trials
Ohio 15 trials
New York 11 trials
Washington 9 trials
Tennessee 8 trials
Illinois 8 trials
Massachusetts 7 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Refractory Acute Myeloid Leukemia page

64 registered trials, 36 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 36 Refractory Acute Myeloid Leukemia trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • M.D. Anderson Cancer Center sponsors the most Refractory Acute Myeloid Leukemia trials on record, review their full trial history before evaluating a specific study. See M.D. Anderson Cancer Center's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Refractory Acute Myeloid Leukemia condition card totals 64 registered trials; most-linked intervention Venetoclax; top US site state Texas. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.