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NCT03816319 · ClinicalTrials.gov registry record · Phase 1

TAK-243 in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia or Myelodysplastic Syndromes With Increased Blasts

A Phase 1 study of Refractory Acute Myeloid Leukemia and Recurrent Acute Myeloid Leukemia, sponsored by National Cancer Institute (NCI).

Recruiting
Registry status
Phase 1
Development phase
42
Enrollment target
5
Study locations

NCT03816319: Recruiting Phase 1 study of Refractory Acute Myeloid Leukemia and Recurrent Acute Myeloid Leukemia, sponsored by National Cancer Institute (NCI).

NCT03816319 is a Phase 1 study of Refractory Acute Myeloid Leukemia and Recurrent Acute Myeloid Leukemia that is actively recruiting participants, run by National Cancer Institute (NCI). The registered enrollment target is 42 participants, below the 47-participant average among 63 other Refractory Acute Myeloid Leukemia trials with a reported enrollment target (11% lower). The trial reports 5 study locations across 5 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT03816319, a Phase 1 study of Refractory Acute Myeloid Leukemia and Recurrent Acute Myeloid Leukemia, is actively recruiting participants, sponsored by National Cancer Institute (NCI).

RECRUITING
Registry status
Phase 1
Development phase
42 participants
Enrollment target
5
Study locations

Study Summary

This phase I trial studies the side effects and best dose of TAK-243 in treating patients with acute myeloid leukemia or myelodysplastic syndromes with increased blasts that has come back (relapsed) or that is not responding to treatment (refractory). TAK-243 may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth.

Interventions

  • PROCEDURE Biospecimen Collection
  • PROCEDURE Bone Marrow Aspiration
  • PROCEDURE Bone Marrow Biopsy
  • PROCEDURE Echocardiography Test
  • PROCEDURE Multigated Acquisition Scan

Study Locations (5)

Florida

  • Moffitt Cancer Center - Tampa

Illinois

  • Northwestern University - Chicago

Ohio

  • Ohio State University Comprehensive Cancer Center - Columbus

Virginia

  • VCU Massey Comprehensive Cancer Center - Richmond

Ontario

  • University Health Network-Princess Margaret Hospital - Toronto

Trial Details

FieldValue
Enrollment Target 42 participants
Start Date 2025-03-12
Est. Completion 2026-10-24
Phase Phase 1
National Cancer Institute (NCI)

3,257 total trials

What NCT03816319 shows while recruiting

NCT03816319 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 42 participants, a relatively small participant target, below the 47-participant average among 63 other Refractory Acute Myeloid Leukemia trials with a reported enrollment target (11% lower).

The record links to 7 conditions, with Refractory Acute Myeloid Leukemia appearing as the primary indexed condition, and to 5 interventions - of which Biospecimen Collection is the first listed.

NCT03816319 lists 5 locations in 5 states (Florida, Illinois, Ohio).

Frequently Asked Questions

What is clinical trial NCT03816319 about?

NCT03816319 is a clinical study titled "TAK-243 in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia or Myelodysplastic Syndromes With Increased Blasts". This phase I trial studies the side effects and best dose of TAK-243 in treating patients with acute myeloid leukemia or myelodysplastic syndromes with increased blasts that has come back (relapsed) or that is not responding to treatment (refractory). TAK-243 may stop the growth of cancer cells by b...

What is the current status of trial NCT03816319?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 42 participants. The study started on 2025-03-12. Estimated completion is 2026-10-24.

What conditions does trial NCT03816319 study?

This clinical trial studies the following conditions: Refractory Acute Myeloid Leukemia, Recurrent Acute Myeloid Leukemia, Recurrent Myelodysplastic Syndrome, Refractory Myelodysplastic Syndrome, Myelodysplastic Syndrome With Excess Blasts.

What interventions are being tested in trial NCT03816319?

The interventions under investigation include: Biospecimen Collection (PROCEDURE), Bone Marrow Aspiration (PROCEDURE), Bone Marrow Biopsy (PROCEDURE), Echocardiography Test (PROCEDURE), Multigated Acquisition Scan (PROCEDURE).

Who is sponsoring clinical trial NCT03816319?

This trial is sponsored by National Cancer Institute (NCI), which has 3,257 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT03816319 being conducted?

This trial has 5 study locations across Florida, Illinois, Ohio, Virginia, Ontario. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Refractory Acute Myeloid Leukemia

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT03816319's enrollment target sits among peer trials

42 28th of 63 higher than 35 of 63 other Refractory Acute Myeloid Leukemia trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Refractory Acute Myeloid Leukemia trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT03816319, the US trial registry maintained by the National Library of Medicine. NCT03816319 (small enrollment · multi site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.