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ClinicalTrials.gov 15 recruiting now full pipeline

Hemophilia A: full-pipeline trial registry

15 of 43 indexed Hemophilia A trials are currently recruiting.

Corpus placement: #339 of 28,707 conditions by registered trial count.

43 US clinical trials · 15 currently recruiting · #339 of 28,707 conditions by registered trial count

Hemophilia A: 43 US clinical trials tracked, 15 recruiting.

Hemophilia A is the subject of 43 registered US clinical trials on ClinicalTrials.gov, 15 of them currently open to new participants. 18 are in Phase 3-4 (later-stage) and 12 in Phase 1-2 (earlier-stage). The most active sponsor is Bayer, running 8 of these trials.

Enrollment posture brief

Registry condition hemophilia-a

OPEN 15 | RECR 35% | LATE 18 | EARLY 12 | RANK #339 | SPON 8

Nearest open-share peer: Obsessive - Compulsive Disorder (35% recruiting · 86 trials)

Caregiver Burden62.8%Aphasia58.1%Chronic Pancreatitis51.2%Degenerative Disc Disease41.9%Hemophilia A (this)35%
Open-enrollment share among volume-matched conditions near Hemophilia A

Hemophilia A lists 15 open slots (35% of 43 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Hemophilia A on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Hemophilia A is recruiting below its size-band peers.

    15 of 43 indexed trials (34.9%) are open to enrollment, against a 39.7% average across 762 conditions with 20-99 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Hemophilia A research.

    Bayer accounts for 8 of 43 trials (18.6%). 24 distinct sponsors appear on at least one study for this condition label.

  3. Most Hemophilia A trials plan to enrol fewer than 100 people.

    Median target enrolment is 60 among the 43 trials that report a genuine target (sentinel values excluded). 30 of those (69.8%) plan for fewer than 100 participants.

  4. Hemophilia A research is mostly interventional.

    31 interventional and 12 observational studies make up this index (72.1% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 111Phase 21Phase 312Phase 46

Open and recent trials

43 total, page 1 of 1

RECRUITING 500 participants

Hemophilia A Research Program

University of Washington

NCT07414511

RECRUITING Phase 3 245 participants

Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors

Pfizer

NCT05145127

RECRUITING Phase 3 173 participants

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

Pfizer

NCT05568719

RECRUITING 120 participants

Treatment of Hemophilia A Patients With FVIII Inhibitors

Emory University

NCT04023019

RECRUITING Phase 3 100 participants

A Clinical Trial of Study Medicine (Marstacimab) in Pediatric Patients With Hemophilia A or Hemophilia B

Pfizer

NCT05611801

RECRUITING 72 participants

Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis

Wayne State University

NCT05022459

RECRUITING Phase 1 60 participants

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A

Hoffmann-La Roche

NCT05987449

RECRUITING 40 participants

Effects of Emicizumab vs. Factor VIII Prophylaxis on Joint and Bone Health in Severe Hemophilia A

Washington Institute for Coagulation

NCT04131036

RECRUITING Phase 1 31 participants

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

Equilibra Bioscience

NCT06349473

RECRUITING Phase 4 28 participants

Nuwiq Dosing and Outcomes In the ManagEment of Women/Girls With Haemophilia A Needing FVIII Treatment for Surgery

Octapharma

NCT05936580

RECRUITING Phase 4 28 participants

POCUS: Hemostatic Potential and Joint Health in Patients With Severe Hemophilia A on Novel Replacement Therapies

University of Texas Southwestern Medical Center

NCT04690322

RECRUITING Phase 4 20 participants

A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab

Sanofi

NCT06145373

RECRUITING Phase 1 12 participants

ASC618 Gene Therapy in Hemophilia A Patients

ASC Therapeutics

NCT04676048

RECRUITING Phase 1 5 participants

A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A

Hoffmann-La Roche

NCT07226206

RECRUITING Phase 3 5 participants

SAFE Study: Safety of aPCC Following Emicizumab Prophylaxis

Emory University

NCT04563520

ACTIVE NOT RECRUITING 371 participants

Evaluating Effectiveness and Long Term Safety of Damoctocog Alfa Pegol in Patients, Who Have Been Diagnosed With Hemophilia A

Bayer

NCT03932201

ACTIVE NOT RECRUITING Phase 3 261 participants

Long-term Safety and Efficacy of Efanesoctocog Alfa (BIVV001) in Previously Treated Patients With Hemophilia A

Bioverativ, a Sanofi company

NCT04644575

ACTIVE NOT RECRUITING 207 participants

A Long-term Study of ADYNOVI/ADYNOVATE in Participants With Haemophilia A

Baxalta now part of Shire

NCT04158934

ACTIVE NOT RECRUITING 200 participants

A Study to Evaluate Impact of Efanesoctocog Alfa on Long-term Joint Health in Participants With Hemophilia A

Sanofi

NCT05911763

ACTIVE NOT RECRUITING Phase 3 77 participants

Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults

Pfizer

NCT04370054

ACTIVE NOT RECRUITING 29 participants

Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A

Spark Therapeutics

NCT03432520

ACTIVE NOT RECRUITING Phase 1 14 participants

Gene Therapy for Haemophilia A.

University College, London

NCT03001830

ACTIVE NOT RECRUITING Phase 1 11 participants

Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle"

Bayer

NCT03588299

ACTIVE NOT RECRUITING Phase 1 5 participants

Gene Therapy Trial for Platelet Derived Factor VIII Production in Hemophilia A

Medical College of Wisconsin

NCT03818763

COMPLETED 200 participants

Females With Severe or Moderate Hemophilia A or B: an International Multi-center Study

Weill Medical College of Cornell University

NCT00936312

COMPLETED Phase 2 175 participants

An Open-label Safety, Efficacy and Pharmacokinetic Study of a Recombinant FVIII Compared to Recombinant Human Antihemophilic FVIII in Patients With Severe Hemophilia A

CSL Behring

NCT01486927

COMPLETED Phase 3 120 participants

A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients Without Inhibitors

Genzyme, a Sanofi Company

NCT03417245

COMPLETED 108 participants

ADVATE Post Authorization Safety Surveillance

Baxalta now part of Shire

NCT00214734

COMPLETED Phase 3 88 participants

A Study of Emicizumab Administered Subcutaneously (SC) in Pediatric Participants With Hemophilia A and Factor VIII (FVIII) Inhibitors

Hoffmann-La Roche

NCT02795767

COMPLETED Phase 4 85 participants

Phase 3/4 Study of a Recombinant Protein-Free Factor VIII (rAHF-PFM): Comparison of Continuous Infusion Versus Intermittent Bolus Infusion in Hemophilia A Subjects Undergoing Major Orthopedic Surgery

Baxalta now part of Shire

NCT00357656

COMPLETED Phase 3 84 participants

Trial to Evaluate the Effect of Secondary Prophylaxis With rFVIII Therapy in Severe Hemophilia A Adult and/or Adolescent Subjects Compared to That of Episodic Treatment

Bayer

NCT00623480

COMPLETED Phase 3 80 participants

A Trial to Compare Prophylaxis Therapy to On-demand Therapy With a New Full Length Recombinant FVIII in Patients With Severe Hemophilia A

Bayer

NCT01233258

COMPLETED Phase 3 74 participants

Safety, Efficacy and PK of BIVV001 in Pediatric Patients With Hemophilia A

Bioverativ, a Sanofi company

NCT04759131

COMPLETED 74 participants

Case and Use Scenario Study to Gain Knowledge on the User Needs for a Medical Device for Hemophilia a Monitoring

Enzyre B.V.

NCT06369740

COMPLETED Phase 3 30 participants

Study Evaluating B-Domain Deleted Recombinant Factor VIII (BDDrFVIII, ReFacto AF) in Patients With Hemophilia A Undergoing Elective Major Surgery

Wyeth is now a wholly owned subsidiary of Pfizer

NCT00243659

COMPLETED Phase 1 27 participants

Pharmacokinetics and Safety of a Single Intravenous Infusion of BAY 79-4980

Bayer

NCT00629837

COMPLETED Phase 4 21 participants

Prophylaxis Regimen for Hemophilia A Patients

Bayer

NCT05036278

COMPLETED NA 20 participants

Correlation Between Vitamin D Status and Bone Mineral Density in Patients With Hemophilia

Virginia Commonwealth University

NCT01090206

COMPLETED Phase 4 16 participants

Study of rFVIIIFc for Immune Tolerance Induction (ITI) in Haemophilia A Patients With Inhibitors Who Have Failed Previous ITI Therapies

Swedish Orphan Biovitrum

NCT03103542

COMPLETED Phase 1 14 participants

Trial to Evaluate the Pharmacokinetics and Safety Profile of BAY94-9027 Following Single and Multiple Dose Administration

Bayer

NCT01184820

COMPLETED 10 participants

Study to Learn More About the Physical Activity Level of Patients Suffering From Hemophilia A Treated With Damoctocog Alfa Pegol (LIFE ACTIVE Study)

Bayer

NCT04091386

COMPLETED Phase 1 4 participants

A Study of BAX 888 in Male Adults With Severe Hemophilia A

Baxalta now part of Shire

NCT03370172

COMPLETED Phase 1 2 participants

Characterization of Laboratory Response to DDAVP in Adult Hemophilia A Carriers

Emory University

NCT02506023

Phase Distribution

PhaseTrial count
Phase 1 11
Phase 2 1
Phase 3 12
Phase 4 6

Named interventions

Most-linked intervention names on Hemophilia A records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Emicizumab Drug
4 trials
Recombinant Factor VIII (Kogenate FS, BAY14-2222) Biological
2 trials
efanesoctocog alfa (BIVV001) Drug
2 trials
Emicizumab Biological
2 trials
rFVIII (BAY81-8973) prophylaxis high-dose Biological
1 trials
rFVIII (BAY81-8973) prophylaxis low-dose Biological
1 trials
rFVIII (BAY81-8973) on demand Biological
1 trials
Recombinant Protein-Free Factor VIII (rAHF-PFM) Drug
1 trials

US sites by state

Facility locations filed on Hemophilia A trials. A trial with sites in several states counts in each.

California 23 trials
Illinois 11 trials
Florida 11 trials
New York 10 trials
Michigan 10 trials
Texas 9 trials
Iowa 8 trials
Georgia 8 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Hemophilia A page

43 registered trials, 15 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 15 Hemophilia A trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • Bayer sponsors the most Hemophilia A trials on record, review their full trial history before evaluating a specific study. See Bayer's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Hemophilia A condition card totals 43 registered trials; most-linked intervention Emicizumab; top US site state California. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.