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2026 data Public-data reference. official source

Hemophilia A

Open-data reference.

42 US clinical trials · 15 currently recruiting

Active & Recent Trials

RECRUITING 500 participants

Hemophilia A Research Program

University of Washington

NCT07414511

RECRUITING Phase 3 245 participants

Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors

Pfizer

NCT05145127

RECRUITING Phase 3 173 participants

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

Pfizer

NCT05568719

RECRUITING 120 participants

Treatment of Hemophilia A Patients With FVIII Inhibitors

Emory University

NCT04023019

RECRUITING Phase 3 100 participants

A Clinical Trial of Study Medicine (Marstacimab) in Pediatric Patients With Hemophilia A or Hemophilia B

Pfizer

NCT05611801

RECRUITING 72 participants

Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis

Wayne State University

NCT05022459

RECRUITING Phase 1 60 participants

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A

Hoffmann-La Roche

NCT05987449

RECRUITING 40 participants

Effects of Emicizumab vs. Factor VIII Prophylaxis on Joint and Bone Health in Severe Hemophilia A

Washington Institute for Coagulation

NCT04131036

RECRUITING Phase 1 31 participants

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

Equilibra Bioscience

NCT06349473

RECRUITING Phase 4 28 participants

Nuwiq Dosing and Outcomes In the ManagEment of Women/Girls With Haemophilia A Needing FVIII Treatment for Surgery

Octapharma

NCT05936580

RECRUITING Phase 4 28 participants

POCUS: Hemostatic Potential and Joint Health in Patients With Severe Hemophilia A on Novel Replacement Therapies

University of Texas Southwestern Medical Center

NCT04690322

RECRUITING Phase 4 20 participants

A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab

Sanofi

NCT06145373

RECRUITING Phase 1 12 participants

ASC618 Gene Therapy in Hemophilia A Patients

ASC Therapeutics

NCT04676048

RECRUITING Phase 1 5 participants

A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A

Hoffmann-La Roche

NCT07226206

RECRUITING Phase 3 5 participants

SAFE Study: Safety of aPCC Following Emicizumab Prophylaxis

Emory University

NCT04563520

ACTIVE NOT RECRUITING 371 participants

Evaluating Effectiveness and Long Term Safety of Damoctocog Alfa Pegol in Patients, Who Have Been Diagnosed With Hemophilia A

Bayer

NCT03932201

ACTIVE NOT RECRUITING Phase 3 261 participants

Long-term Safety and Efficacy of Efanesoctocog Alfa (BIVV001) in Previously Treated Patients With Hemophilia A

Bioverativ, a Sanofi company

NCT04644575

ACTIVE NOT RECRUITING 207 participants

A Long-term Study of ADYNOVI/ADYNOVATE in Participants With Haemophilia A

Baxalta now part of Shire

NCT04158934

ACTIVE NOT RECRUITING 200 participants

A Study to Evaluate Impact of Efanesoctocog Alfa on Long-term Joint Health in Participants With Hemophilia A

Sanofi

NCT05911763

ACTIVE NOT RECRUITING Phase 3 77 participants

Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults

Pfizer

NCT04370054

ACTIVE NOT RECRUITING 29 participants

Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A

Spark Therapeutics

NCT03432520

ACTIVE NOT RECRUITING Phase 1 14 participants

Gene Therapy for Haemophilia A.

University College, London

NCT03001830

ACTIVE NOT RECRUITING Phase 1 11 participants

Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle"

Bayer

NCT03588299

ACTIVE NOT RECRUITING Phase 1 5 participants

Gene Therapy Trial for Platelet Derived Factor VIII Production in Hemophilia A

Medical College of Wisconsin

NCT03818763

COMPLETED 200 participants

Females With Severe or Moderate Hemophilia A or B: an International Multi-center Study

Weill Medical College of Cornell University

NCT00936312

COMPLETED Phase 2 175 participants

An Open-label Safety, Efficacy and Pharmacokinetic Study of a Recombinant FVIII Compared to Recombinant Human Antihemophilic FVIII in Patients With Severe Hemophilia A

CSL Behring

NCT01486927

COMPLETED Phase 3 120 participants

A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients Without Inhibitors

Genzyme, a Sanofi Company

NCT03417245

COMPLETED 108 participants

ADVATE Post Authorization Safety Surveillance

Baxalta now part of Shire

NCT00214734

COMPLETED Phase 3 88 participants

A Study of Emicizumab Administered Subcutaneously (SC) in Pediatric Participants With Hemophilia A and Factor VIII (FVIII) Inhibitors

Hoffmann-La Roche

NCT02795767

COMPLETED Phase 4 85 participants

Phase 3/4 Study of a Recombinant Protein-Free Factor VIII (rAHF-PFM): Comparison of Continuous Infusion Versus Intermittent Bolus Infusion in Hemophilia A Subjects Undergoing Major Orthopedic Surgery

Baxalta now part of Shire

NCT00357656

COMPLETED Phase 3 84 participants

Trial to Evaluate the Effect of Secondary Prophylaxis With rFVIII Therapy in Severe Hemophilia A Adult and/or Adolescent Subjects Compared to That of Episodic Treatment

Bayer

NCT00623480

COMPLETED Phase 3 80 participants

A Trial to Compare Prophylaxis Therapy to On-demand Therapy With a New Full Length Recombinant FVIII in Patients With Severe Hemophilia A

Bayer

NCT01233258

COMPLETED Phase 3 74 participants

Safety, Efficacy and PK of BIVV001 in Pediatric Patients With Hemophilia A

Bioverativ, a Sanofi company

NCT04759131

COMPLETED Phase 3 30 participants

Study Evaluating B-Domain Deleted Recombinant Factor VIII (BDDrFVIII, ReFacto AF) in Patients With Hemophilia A Undergoing Elective Major Surgery

Wyeth is now a wholly owned subsidiary of Pfizer

NCT00243659

COMPLETED Phase 1 27 participants

Pharmacokinetics and Safety of a Single Intravenous Infusion of BAY 79-4980

Bayer

NCT00629837

COMPLETED Phase 4 21 participants

Prophylaxis Regimen for Hemophilia A Patients

Bayer

NCT05036278

COMPLETED NA 20 participants

Correlation Between Vitamin D Status and Bone Mineral Density in Patients With Hemophilia

Virginia Commonwealth University

NCT01090206

COMPLETED Phase 4 16 participants

Study of rFVIIIFc for Immune Tolerance Induction (ITI) in Haemophilia A Patients With Inhibitors Who Have Failed Previous ITI Therapies

Swedish Orphan Biovitrum

NCT03103542

COMPLETED Phase 1 14 participants

Trial to Evaluate the Pharmacokinetics and Safety Profile of BAY94-9027 Following Single and Multiple Dose Administration

Bayer

NCT01184820

COMPLETED 10 participants

Study to Learn More About the Physical Activity Level of Patients Suffering From Hemophilia A Treated With Damoctocog Alfa Pegol (LIFE ACTIVE Study)

Bayer

NCT04091386

COMPLETED Phase 1 4 participants

A Study of BAX 888 in Male Adults With Severe Hemophilia A

Baxalta now part of Shire

NCT03370172

COMPLETED Phase 1 2 participants

Characterization of Laboratory Response to DDAVP in Adult Hemophilia A Carriers

Emory University

NCT02506023

Phase Distribution

PhaseTrial count
Early Phase 1 11
Phase 2 1
Phase 3 12
Phase 4 6

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

Reading the Hemophilia A Trial Landscape

ClinicalTrials.gov lists 42 US studies indexed under Hemophilia A, and 15 of those are currently open to recruitment — roughly 36% of the total volume on the registry. That ratio is a useful proxy for activity level: a high share of recruiting studies often signals that research interest is current and that new enrollment opportunities are appearing, while a low share typically means the field is dominated by completed or follow-up work where most participant spots have already been filled. These counts reflect the public registry only and include studies at every stage of design, so they should be read as an index of research attention rather than as a measure of treatment availability.

The phase distribution for Hemophilia A shows 18 late-stage studies (Phase 3 and Phase 4 combined) alongside 12 earlier-phase entries (Phase 1 through Phase 2). Phase 1 and Phase 2 studies focus on early safety signals, dosing, and preliminary effect, while Phase 3 studies are typically the larger efficacy and safety trials submitted toward regulatory review, and Phase 4 studies follow approved interventions in real-world use. A condition weighted toward later phases often reflects a mature research pipeline with several interventions already close to or past approval, whereas a heavier early-phase tilt suggests the field is still exploring new mechanisms and candidate approaches.

Top sponsor activity for Hemophilia A is led by Bayer with 8 indexed trials, alongside 9 other organizations in the top contributor list. The list on this page surfaces up to 42 of the most relevant recent and active entries, ordered with recruiting studies first so practical options are visible. All figures are derived from the public ClinicalTrials.gov dataset maintained by the National Library of Medicine and are reproduced here for reference. Inclusion of a trial, sponsor, or intervention on this page is neither an endorsement nor a recommendation — eligibility, protocol changes, and site-level status can shift frequently, so always verify current details on ClinicalTrials.gov and consult a qualified healthcare provider before acting on anything you see here.

Frequently Asked Questions

How many clinical trials are there for Hemophilia A?

PlainTrial tracks 42 US clinical trials for Hemophilia A, of which 15 are currently recruiting participants. Data sourced from ClinicalTrials.gov.

How do I find a recruiting trial for Hemophilia A?

Use the trial list above filtered by "Recruiting" status, or visit our trial finder at /recruiting to search by condition and state. Always discuss trial participation with your healthcare provider before enrolling.

Is this data current?

Data is sourced from ClinicalTrials.gov and reflects our most recent data pull. Trial status may have changed since then. Always verify current information at ClinicalTrials.gov before making decisions about participation.

Related

Data sourced from official U.S. government datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Disclaimer: This information is provided for informational purposes only and does not constitute professional advice. Data is sourced from ClinicalTrials.gov (National Library of Medicine). Consult a qualified professional before making decisions based on this data.

Source: ClinicalTrials.gov (NIH/NLM) ClinicalTrials.gov AACT registry · 2024 Trial counts and statuses sourced from ClinicalTrials.gov. Sponsor counts include both industry and federal/academic sponsors.

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