Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT03432520 · ClinicalTrials.gov registry record

Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A

A clinical trial of Hemophilia A, sponsored by Spark Therapeutics.

Active
Registry status
29
Enrollment target
12
Study locations

NCT03432520: Active study of Hemophilia A, sponsored by Spark Therapeutics.

NCT03432520 is a study of Hemophilia A that is active but no longer recruiting, run by Spark Therapeutics. The registered enrollment target is 29 participants, below the 91-participant average among 42 other Hemophilia A trials with a reported enrollment target (68% lower). The trial reports 12 study locations across 9 states. According to ClinicalTrials.gov, the official US trial registry.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT03432520, a study of Hemophilia A, is active but no longer recruiting, sponsored by Spark Therapeutics.

ACTIVE NOT RECRUITING
Registry status
29 participants
Enrollment target
12
Study locations

Study Summary

This long-term follow-up study will continue to evaluate the long-term safety and efficacy of SPK-8011 and SPK-8016 in males with hemophilia A, who have received a single intravenous administration of SPK-8011 or SPK-8016 in any Spark-sponsored SPK-8011 or SPK-8016 study.

Conditions Studied

Interventions

  • GENETIC SPK-8011
  • GENETIC SPK-8016

Study Locations (12)

Pennsylvania

  • Pennsylvania State University Milton S. Hershey Medical Center - Hershey
  • The Children's Hospital of Philadelphia - Philadelphia
  • Thomas Jefferson University - Philadelphia
  • Hemophilia Center of Western Pennsylvania - Pittsburgh

Massachusetts

  • Boston Children's Hospital - Boston

Mississippi

  • Mississippi Center for Advanced Medicine - Madison

Missouri

  • Truman Medical Centers - Kansas City

Oregon

  • Oregon Health & Science University - Portland

Virginia

  • Virginia Commonwealth University - Richmond

New South Wales

  • Royal Prince Alfred Hospital Department of Cell & Molecular Therapies - Sydney

Victoria

  • The Alfred Hospital & Monash Medical Centre - Melbourne

Trial Details

FieldValue
Enrollment Target 29 participants
Start Date 2018-08-14
Est. Completion 2032-12
Spark Therapeutics

13 total trials

What the registry record for NCT03432520 still lists

NCT03432520 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 29 participants, a relatively small participant target, below the 91-participant average among 42 other Hemophilia A trials with a reported enrollment target (68% lower).

The record links to 1 condition, with Hemophilia A appearing as the primary indexed condition, and to 2 interventions - of which SPK-8011 is the first listed.

NCT03432520 lists 12 locations in 9 states (Pennsylvania, Massachusetts, Mississippi).

Frequently Asked Questions

What is clinical trial NCT03432520 about?

NCT03432520 is a clinical study titled "Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A". This long-term follow-up study will continue to evaluate the long-term safety and efficacy of SPK-8011 and SPK-8016 in males with hemophilia A, who have received a single intravenous administration of SPK-8011 or SPK-8016 in any Spark-sponsored SPK-8011 or SPK-8016 study.

What is the current status of trial NCT03432520?

This trial is currently active not recruiting. The enrollment target is 29 participants. The study started on 2018-08-14. Estimated completion is 2032-12.

What conditions does trial NCT03432520 study?

This clinical trial studies the following conditions: Hemophilia A.

What interventions are being tested in trial NCT03432520?

The interventions under investigation include: SPK-8011 (GENETIC), SPK-8016 (GENETIC).

Who is sponsoring clinical trial NCT03432520?

This trial is sponsored by Spark Therapeutics, which has 13 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT03432520 being conducted?

This trial has 12 study locations across Massachusetts, Mississippi, Missouri, Oregon, Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Hemophilia A

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT03432520's enrollment target sits among peer trials

29 26th of 42 higher than 17 of 42 other Hemophilia A trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Hemophilia A trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

Nationwide trials with similar profiles

Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.

Similar enrollment target

  • NCT02429557 · 29 participants · Phase 1

    Hemodynamic Mechanisms of Abdominal Compression in the Treatment of Orthostatic Hypotension in Autonomic Failure

  • NCT02568878 · 29 participants · Phase 3

    Creatine for Depressed Male and Female Methamphetamine Users

  • NCT03014401 · 29 participants · NA

    The Effect of Adipose-Derived Stem Cells for Knee Osteoarthritis

  • NCT03128996 · 29 participants · Phase 1

    Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders

Similar registry start date

  • NCT05962346 · started 2026-12 · NA

    Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia

  • NCT07125183 · started 2026-12 · Phase 2

    Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma

  • NCT07292298 · started 2026-11 · Phase 2

    Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates

  • NCT04263285 · started 2026-10 · NA

    Treatment of Depression Post-SCI

Source: ClinicalTrials.gov NCT03432520, the US trial registry maintained by the National Library of Medicine. NCT03432520 (small enrollment · multi site footprint · active not recruiting) retrieved and formatted by PlainTrial, see methodology.