Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT04644575 · ClinicalTrials.gov registry record · Phase 3

Long-term Safety and Efficacy of Efanesoctocog Alfa (BIVV001) in Previously Treated Patients With Hemophilia A

A Phase 3 study of Hemophilia A, sponsored by Bioverativ, a Sanofi company.

Active
Registry status
Phase 3
Development phase
261
Enrollment target
20
Study locations

NCT04644575 is a Phase 3 study of Hemophilia A that is active but no longer recruiting, run by Bioverativ, a Sanofi company. The registered enrollment target is 261 participants, above the 85-participant average among 42 other Hemophilia A trials with a reported enrollment target (207% higher). The trial reports 20 study locations across 16 states.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT04644575, a Phase 3 study of Hemophilia A, is active but no longer recruiting, sponsored by Bioverativ, a Sanofi company.

ACTIVE NOT RECRUITING
Registry status
Phase 3
Development phase
261 participants
Enrollment target
20
Study locations

Study Summary

Primary Objective: \- To evaluate the long-term safety of BIVV001 in previously treated subjects with hemophilia A Secondary Objectives: * To evaluate the efficacy of BIVV001 as a prophylaxis treatment. * To evaluate the efficacy of BIVV001 in the treatment of bleeding episodes. * To evaluate BIVV001 consumption for prevention and treatment of bleeding episodes. * To evaluate the effect of BIVV001 prophylaxis on joint health outcomes. * To evaluate the effect of BIVV001 prophylaxis on Quality of Life (QoL) outcomes. * To evaluate the safety and tolerability of BIVV001 treatment. * To assess the PK of BIVV001 based on the one stage activated partial thromboplastin time (aPTT) and two-stage chromogenic FVIII activity assays (only applicable to Arm B). * To evaluate the efficacy of BIVV001 for perioperative management

Conditions Studied

Interventions

  • DRUG efanesoctocog alfa (BIVV001)

Study Locations (20)

California

  • Orthopaedic Institute for Children Site Number : 8400003 - Los Angeles
  • Children's Hospital Los Angeles Site Number : 8400009 - Los Angeles
  • University of California San Diego Site Number : 8400007 - San Diego

Michigan

  • University of Michigan Medical Center Site Number : 8400006 - Ann Arbor
  • Michigan State University School Of Med Site Number : 8400002 - East Lansing

Ohio

  • Cincinnati Children's Hospital Medical Center Site Number : 8400012 - Cincinnati
  • Children's Research Institute Site Number : 8400013 - Columbus

Florida

  • University of Florida Health Site Number : 8400008 - Gainesville

Georgia

  • Children's Healthcare of Atlanta Site Number : 8400016 - Atlanta

Illinois

  • Rush University Medical Center Site Number : 8400010 - Chicago

Iowa

  • Children's Hospital Of Iowa Site Number : 8400011 - Iowa City

Nevada

  • Hemostasis and Thrombosis Center of Nevada Site Number : 8400001 - Las Vegas

Trial Details

FieldValue
Enrollment Target 261 participants
Start Date 2021-02-23
Est. Completion 2027-01-15
Phase Phase 3

Sponsor

Bioverativ, a Sanofi company

14 total trials

What the Registry Record Tells You About NCT04644575

The ClinicalTrials.gov registry entry for NCT04644575 describes a study currently listed as active not recruiting, categorized as Phase 3. The registered enrollment target is 261 participants, a figure that helps gauge the scale of data the investigators plan to collect, above the 85-participant average among 42 other Hemophilia A trials with a reported enrollment target (207% higher). The listed sponsor is Bioverativ, a Sanofi company, which has 14 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Hemophilia A appearing as the primary indexed condition, and to 1 intervention - of which efanesoctocog alfa (BIVV001) is the first listed.

NCT04644575 reports 20 study locations spanning 16 distinct geographic areas - top geographies include California, Michigan, Ohio.

Frequently Asked Questions

What is clinical trial NCT04644575 about?

NCT04644575 is a clinical study titled "Long-term Safety and Efficacy of Efanesoctocog Alfa (BIVV001) in Previously Treated Patients With Hemophilia A". Primary Objective: \- To evaluate the long-term safety of BIVV001 in previously treated subjects with hemophilia A Secondary Objectives: * To evaluate the efficacy of BIVV001 as a prophylaxis treatment. * To evaluate the efficacy of BIVV001 in the treatment of bleeding episodes. * To evaluate BIV...

What is the current status of trial NCT04644575?

This trial is currently active not recruiting. It is a Phase 3 study. The enrollment target is 261 participants. The study started on 2021-02-23. Estimated completion is 2027-01-15.

What conditions does trial NCT04644575 study?

This clinical trial studies the following conditions: Hemophilia A.

What interventions are being tested in trial NCT04644575?

The interventions under investigation include: efanesoctocog alfa (BIVV001) (DRUG).

Who is sponsoring clinical trial NCT04644575?

This trial is sponsored by Bioverativ, a Sanofi company, which has 14 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04644575 being conducted?

This trial has 20 study locations across California, Florida, Georgia, Illinois, Iowa. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Hemophilia A

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.