Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.
Dyskeratosis Congenita: early-phase trial registry
5 of 8 indexed Dyskeratosis Congenita trials are currently recruiting, with more weight in Phase 1-2.
Corpus placement: #2,176 of 28,707 conditions by registered trial count.
8 US clinical trials · 5 currently recruiting · #2,176 of 28,707 conditions by registered trial count
Dyskeratosis Congenita: 8 US clinical trials tracked, 5 recruiting.
Dyskeratosis Congenita is the subject of 8 registered US clinical trials on ClinicalTrials.gov, 5 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 4 in Phase 1-2 (earlier-stage). The most active sponsor is Masonic Cancer Center, University of Minnesota, running 2 of these trials.
Enrollment posture brief
Registry condition dyskeratosis-congenita
OPEN 5 | RECR 63% | LATE 0 | EARLY 4 | RANK #2176 | SPON 2
Volume-matched condition peers
Nearest open-share peer: Adolescent (63% recruiting · 16 trials)
Dyskeratosis Congenita lists 5 open slots (63% of 8 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Dyskeratosis Congenita on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Dyskeratosis Congenita is recruiting above its size-band peers.
5 of 8 indexed trials (62.5%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
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One sponsor concentrates Dyskeratosis Congenita research.
Masonic Cancer Center, University of Minnesota accounts for 2 of 8 trials (25%). 6 distinct sponsors appear on at least one study for this condition label.
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Most Dyskeratosis Congenita trials plan to enrol fewer than 100 people.
Median target enrolment is 53 among the 8 trials that report a genuine target (sentinel values excluded). 6 of those (75%) plan for fewer than 100 participants.
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Dyskeratosis Congenita splits between interventional and observational designs.
5 interventional and 3 observational studies make up this index (62.5% interventional). Study type is sponsor-reported on ClinicalTrials.gov.
Open and recent trials
8 total, page 1 of 1
Cancer in Inherited Bone Marrow Failure Syndromes
National Cancer Institute (NCI)
NCT00027274
Investigation of the Genetics of Hematologic Diseases
St. Jude Children's Research Hospital
NCT02720679
Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders
Masonic Cancer Center, University of Minnesota
NCT03579875
Nucleoside Therapy in Patients With Telomere Biology Disorders
Suneet Agarwal
NCT06817590
Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
NCT04232085
Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita
Boston Children's Hospital
NCT01659606
Hematopoietic Stem Cell Transplant for Dyskeratosis Congenita or Severe Aplastic Anemia
Masonic Cancer Center, University of Minnesota
NCT02162420
Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD)
National Cancer Institute (NCI)
NCT04959188
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 1 | 1 |
| Phase 2 | 3 |
Top Sponsors
Named interventions
Most-linked intervention names on Dyskeratosis Congenita records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Dyskeratosis Congenita trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Dyskeratosis Congenita page
8 registered trials, 5 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 5 Dyskeratosis Congenita trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- Masonic Cancer Center, University of Minnesota sponsors the most Dyskeratosis Congenita trials on record, review their full trial history before evaluating a specific study. See Masonic Cancer Center, University of Minnesota's trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Dyskeratosis Congenita condition card totals 8 registered trials; most-linked intervention Fludarabine; top US site state Maryland. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.