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ClinicalTrials.gov 7 recruiting now early-phase tilt small index

Refractory Neuroblastoma: early-phase trial registry

7 of 10 indexed Refractory Neuroblastoma trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #1,724 of 28,707 conditions by registered trial count.

10 US clinical trials · 7 currently recruiting · #1,724 of 28,707 conditions by registered trial count

Refractory Neuroblastoma: 10 US clinical trials tracked, 7 recruiting.

Refractory Neuroblastoma is the subject of 10 registered US clinical trials on ClinicalTrials.gov, 7 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 10 in Phase 1-2 (earlier-stage). The most active sponsor is Stephan Grupp MD PhD, running 2 of these trials.

Enrollment posture brief

Registry condition refractory-neuroblastoma

OPEN 7 | RECR 70% | LATE 0 | EARLY 10 | RANK #1724 | SPON 2

Nearest open-share peer: Advanced Solid Tumor (70% recruiting · 190 trials)

Acute Leukemia of Ambiguous 80%Refractory Neuroblastoma (th…70%Achondroplasia40%Accelerated Phase Chronic My20%Accidental Fall20%
Open-enrollment share among volume-matched conditions near Refractory Neuroblastoma

Refractory Neuroblastoma lists 7 open slots (70% of 10 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Refractory Neuroblastoma on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Refractory Neuroblastoma is recruiting above its size-band peers.

    7 of 10 indexed trials (70%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Refractory Neuroblastoma research.

    Stephan Grupp MD PhD accounts for 2 of 10 trials (20%). 9 distinct sponsors appear on at least one study for this condition label.

  3. Most Refractory Neuroblastoma trials plan to enrol fewer than 100 people.

    Median target enrolment is 42 among the 10 trials that report a genuine target (sentinel values excluded). 10 of those (100%) plan for fewer than 100 participants.

  4. Refractory Neuroblastoma research is mostly interventional.

    10 interventional and 0 observational studies make up this index (100% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 19Phase 21

Open and recent trials

10 total, page 1 of 1

RECRUITING Phase 1 59 participants

PEEL-224, Vincristine and Temozolomide in Pediatric Solid Tumors

Theodore Laetsch

NCT06721689

RECRUITING Phase 1 45 participants

GPC2 CAR T Cells for Relapsed or Refractory Neuroblastoma and Metastatic Retinoblastoma

Stephan Grupp MD PhD

NCT05650749

RECRUITING Phase 1 42 participants

Study of hALK.CAR T Cells for Patients With Relapsed/Refractory High-risk Neuroblastoma

Roberto Chiarle

NCT06803875

RECRUITING Phase 1 38 participants

PHOX2B PC-CAR T Cells for Relapsed Neuroblastoma

Stephan Grupp MD PhD

NCT07007117

RECRUITING Phase 1 31 participants

NK Cells Infusions With Irinotecan, Temozolomide, and Dinutuximab

Nationwide Children's Hospital

NCT04211675

RECRUITING Phase 1 24 participants

Allogeneic Expanded Gamma Delta T Cells With GD2 Chemoimmunotherapy in Relapsed /Refractory Neuroblastoma or Refractory/ Relapsed Osteosarcoma

Emory University

NCT05400603

RECRUITING Phase 1 18 participants

Feasibility Study of Prolonged Administration of Naxitamab, Irinotecan, and Temozolomide for Patients With Relapsed or Refractory Neuroblastoma

Steven DuBois, MD

NCT07027748

ACTIVE NOT RECRUITING Phase 2 94 participants

Irinotecan Hydrochloride, Temozolomide, and Dinutuximab With or Without Eflornithine in Treating Patients With Relapsed or Refractory Neuroblastoma

Children's Oncology Group

NCT03794349

ACTIVE NOT RECRUITING Phase 1 94 participants

C7R-GD2.CART Cells for Patients With Relapsed or Refractory Neuroblastoma and Other GD2 Positive Cancers (GAIL-N)

Baylor College of Medicine

NCT03635632

ACTIVE NOT RECRUITING Phase 1 27 participants

Lenalidomide and Dinutuximab With or Without Isotretinoin in Treating Younger Patients With Refractory or Recurrent Neuroblastoma

National Cancer Institute (NCI)

NCT01711554

Phase Distribution

PhaseTrial count
Phase 1 9
Phase 2 1

Named interventions

Most-linked intervention names on Refractory Neuroblastoma records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Temozolomide Drug
3 trials
Dinutuximab Biological
2 trials
Irinotecan Drug
2 trials
C7R-GD2.CART cells Genetic
1 trials
Eflornithine Hydrochloride Drug
1 trials
Pharmacological Study Other
1 trials
Autologous hALK.CAR T cells Biological
1 trials
Ex Vivo Expanded Allogeneic γδ T Cells in Combination with Dinutuximab, Temozolomide, Irinotecan and Zoledronate Combination
1 trials

US sites by state

Facility locations filed on Refractory Neuroblastoma trials. A trial with sites in several states counts in each.

Pennsylvania 4 trials
Massachusetts 3 trials
Texas 2 trials
Ohio 2 trials
Georgia 2 trials
Colorado 2 trials
California 2 trials
Washington 1 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Refractory Neuroblastoma page

10 registered trials, 7 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 7 Refractory Neuroblastoma trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • Stephan Grupp MD PhD sponsors the most Refractory Neuroblastoma trials on record, review their full trial history before evaluating a specific study. See Stephan Grupp MD PhD's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Refractory Neuroblastoma condition card totals 10 registered trials; most-linked intervention Temozolomide; top US site state Pennsylvania. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.