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ClinicalTrials.gov 46 recruiting now early-phase tilt #85 of 28,707 conditions

Myelodysplastic Syndrome: early-phase trial registry

46 of 135 indexed Myelodysplastic Syndrome trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #85 of 28,707 conditions by registered trial count.

135 US clinical trials · 46 currently recruiting · #85 of 28,707 conditions by registered trial count

Myelodysplastic Syndrome: 135 US clinical trials tracked, 46 recruiting.

Myelodysplastic Syndrome is the subject of 135 registered US clinical trials on ClinicalTrials.gov, 46 of them currently open to new participants. 7 are in Phase 3-4 (later-stage) and 121 in Phase 1-2 (earlier-stage). The most active sponsor is M.D. Anderson Cancer Center, running 33 of these trials.

Enrollment posture brief

Registry condition myelodysplastic-syndrome

OPEN 46 | RECR 34% | LATE 7 | EARLY 121 | RANK #85 | SPON 33

Nearest open-share peer: Physical Activity (34% recruiting · 132 trials)

Inflammation38.3%Myelodysplastic Syndrome (th…34%Carcinoma, Non-Small Cell Lu32.3%Osteoarthritis21.3%Cardiovascular Disease14.5%
Open-enrollment share among volume-matched conditions near Myelodysplastic Syndrome

Myelodysplastic Syndrome lists 46 open slots (34% of 135 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Myelodysplastic Syndrome on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Myelodysplastic Syndrome is recruiting below its size-band peers.

    46 of 135 indexed trials (34.1%) are open to enrollment, against a 37.1% average across 139 conditions with 100+ trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Myelodysplastic Syndrome research.

    M.D. Anderson Cancer Center accounts for 33 of 135 trials (24.4%). 51 distinct sponsors appear on at least one study for this condition label.

  3. Most Myelodysplastic Syndrome trials plan to enrol fewer than 100 people.

    Median target enrolment is 51 among the 135 trials that report a genuine target (sentinel values excluded). 99 of those (73.3%) plan for fewer than 100 participants.

  4. Myelodysplastic Syndrome research is mostly interventional.

    130 interventional and 5 observational studies make up this index (96.3% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 157Phase 264Phase 37

Open and recent trials

135 total, page 3 of 3

COMPLETED Phase 2 72 participants

Busulfan, Fludarabine, Clofarabine With Allogeneic Stem Cell Transplantation for Acute Myeloid Leukemia

M.D. Anderson Cancer Center

NCT00469014

COMPLETED Phase 2 71 participants

Decitabine and Gemtuzumab Ozogamicin in Acute Myelogenous Leukemia and High-risk Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT00968071

COMPLETED Phase 2 67 participants

A Study of Decitabine Given Subcutaneously to Adults With Low or Intermediate-1 Risk Myelodysplastic Syndromes (MDS)

Eisai

NCT00619099

COMPLETED Phase 1 66 participants

A Phase I/II Study of MGCD0103 With Azacitidine in Patients With High-Risk Myelodysplastic Syndrome (MDS) or Acute Myelogenous Leukemia

Mirati Therapeutics

NCT00324220

COMPLETED Phase 2 65 participants

Oral Clofarabine Study in Patients With Myelodysplastic Syndrome

M.D. Anderson Cancer Center

NCT00299156

COMPLETED Phase 1 54 participants

Natural Killer Cells Before and After Donor Stem Cell Transplant in Treating Patients With Acute Myeloid Leukemia, Myelodysplastic Syndrome, or Chronic Myelogenous Leukemia

M.D. Anderson Cancer Center

NCT01904136

COMPLETED Phase 1 51 participants

Idarubicin + Cytarabine and Lenalidomide in Patients With Myelodysplastic Syndrome (MDS), Acute Myeloid Leukemia (AML)

H. Lee Moffitt Cancer Center and Research Institute

NCT00831766

COMPLETED Phase 2 51 participants

INCB018424 in Patients With Advanced Hematologic Malignancies

M.D. Anderson Cancer Center

NCT00674479

COMPLETED Phase 2 50 participants

Chemotherapy in Treating Patients With Myelodysplastic Syndrome Before Donor Stem Cell Transplant

Fred Hutchinson Cancer Center

NCT01812252

COMPLETED Phase 1 47 participants

A Novel Sequential Treatment of Salvage and Reduced Intensity Conditioning (RIC) Chemotherapy for Allogeneic Stem-Cell Transplantation (SCT) for Primary Refractory and Relapsed Acute Myelogenous Leukemia (AML)

Weill Medical College of Cornell University

NCT00875693

COMPLETED Phase 2 46 participants

T Cell Depletion for Recipients of HLA Haploidentical Related Donor Stem Cell Grafts

Baylor College of Medicine

NCT00368355

COMPLETED Phase 1 38 participants

Blinded Cross-Over Bioequivalence (BE) Trial of Luitpold Azacitidine vs Vidaza

American Regent

NCT01290302

COMPLETED Phase 1 36 participants

Study of 72-Hour Infusion of ON 01910.Na in Patients With MDS or AML

Traws Pharma

NCT00854945

COMPLETED Phase 1 36 participants

Phase I/II Study of 5-Azacytidine With Ara-C in Patients With Relapsed/Refractory Acute Myelogenous Leukemia (AML) or High Risk Myelodysplastic Syndrome (MDS)

M.D. Anderson Cancer Center

NCT00569010

COMPLETED Phase 1 36 participants

Safety and Pharmacokinetic Study of Oral ON 01910.Na in Patients With Myelodysplastic Syndrome

Traws Pharma

NCT01048619

COMPLETED Phase 2 34 participants

Phase II 5-Azacytidine Plus VPA Plus ATRA

M.D. Anderson Cancer Center

NCT00326170

COMPLETED Early Phase 1 30 participants

Pilot Study of Non-Myeloablative, HLA-Matched Allogeneic Stem Cell Transplantation for Pediatric Hematopoietic Malignancies

National Cancer Institute (NCI)

NCT00013533

COMPLETED Phase 2 26 participants

SCT Plus Immune Therapy in Average Risk AML/MDS

New York Medical College

NCT02117297

COMPLETED Phase 2 25 participants

Phase II Study of Azacitidine and Sargramostim as Maintenance Treatment for Poor-Risk AML or MDS

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

NCT01700673

COMPLETED Phase 2 25 participants

Immunochemotherapy and AlloSCT in Patients With High Risk CD33+ AML/MDS

New York Medical College

NCT02221310

COMPLETED Phase 2 25 participants

Reduced Intensity Conditioning Transplant Using Haploidentical Donors

Northside Hospital

NCT02581007

COMPLETED Phase 2 25 participants

NK Cell Based Non-Myeloablative Transplantation in Acute Myeloid Diseases

Masonic Cancer Center, University of Minnesota

NCT01370213

COMPLETED Phase 2 24 participants

Off-the-shelf NK Cells + SCT for Myeloid Malignancies

M.D. Anderson Cancer Center

NCT05115630

COMPLETED Phase 1 22 participants

Dose Escalation Trial of WT1-Sensitized T Cells for Residual or Relapsed Leukemia After Allogeneic Hematopoietic Progenitor Cell Transplantation

Memorial Sloan Kettering Cancer Center

NCT00620633

COMPLETED Phase 2 18 participants

CD8+ Memory T-Cells as Consolidative Therapy After Donor Non-myeloablative Hematopoietic Cell Transplant in Treating Patients With Leukemia or Lymphoma

Robert Lowsky

NCT02424968

COMPLETED Phase 2 18 participants

Study to Determine the Safety and Preliminary Efficacy of CC-1088 in the Treatment of Myelodysplastic Syndromes

Celgene

NCT00045786

COMPLETED Phase 1 15 participants

Alloreactive NK Cells for Allogeneic Stem Cell Transplantation for Acute Myeloid Leukemia (AML) and Myelodysplastic Syndrome (MDS)

M.D. Anderson Cancer Center

NCT00402558

COMPLETED Phase 2 14 participants

Leucovorin for the Treatment of 5 q Minus Syndrome

National Institutes of Health Clinical Center (CC)

NCT00004997

COMPLETED Phase 2 14 participants

Efficacy and Safety of ON 01910.Na in Myelodysplastic Syndrome (MDS) Patients With Trisomy 8 or Classified as Intermediate-1, -2 or High Risk

Traws Pharma

NCT00906334

COMPLETED Phase 1 14 participants

Targeted Marrow Irradiation, Fludarabine Phosphate, and Busulfan Before Donor Progenitor Cell Transplant in Treating Patients With Hematologic Malignancies

Case Comprehensive Cancer Center

NCT02129582

COMPLETED Phase 2 12 participants

Study of Clinical Efficacy and Safety of Tosedostat in MDS

Weill Medical College of Cornell University

NCT02452346

COMPLETED NA 12 participants

Decitabine and Cytarabine in Treating Older Patients With Newly Diagnosed Acute Myeloid Leukemia, High Risk Myelodysplastic Syndrome, or Myeloproliferative Neoplasm

University of Washington

NCT02121418

COMPLETED Phase 1 10 participants

Infusion of Specially Treated Umbilical Cord Stem Cells After Chemoradiation Treatment for Blood Cancers

ViaCell

NCT00089596

COMPLETED Phase 1 10 participants

Ibrutinib for the Treatment of COVID-19 in Patients Requiring Hospitalization

Jennifer Woyach

NCT04439006

COMPLETED Phase 2 4 participants

Wilm's Tumor 1 (WT1) Peptide Vaccine for High Risk Hematologic Malignancy

National Heart, Lung, and Blood Institute (NHLBI)

NCT00433745

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Phase Distribution

PhaseTrial count
Phase 1 57
Phase 2 64
Phase 3 7

Named interventions

Most-linked intervention names on Myelodysplastic Syndrome records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Biospecimen Collection Procedure
22 trials
Azacitidine Drug
17 trials
Cyclophosphamide Drug
15 trials
Bone Marrow Biopsy Procedure
13 trials
Venetoclax Drug
13 trials
Fludarabine Drug
12 trials
Laboratory Biomarker Analysis Other
11 trials
Bone Marrow Aspiration Procedure
11 trials

US sites by state

Facility locations filed on Myelodysplastic Syndrome trials. A trial with sites in several states counts in each.

Texas 47 trials
California 40 trials
New York 32 trials
Ohio 15 trials
Florida 14 trials
Maryland 13 trials
Washington 12 trials
Massachusetts 12 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Myelodysplastic Syndrome page

135 registered trials, 46 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Myelodysplastic Syndrome condition card totals 135 registered trials; most-linked intervention Biospecimen Collection; top US site state Texas. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.