Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.
Genetic Diseases clinical trials
4 of 4 indexed Genetic Diseases trials are currently recruiting.
Corpus placement: #4,115 of 28,707 conditions by registered trial count.
4 US clinical trials · 4 currently recruiting · #4,115 of 28,707 conditions by registered trial count
Genetic Diseases: 4 US clinical trials tracked, 4 recruiting.
Genetic Diseases is the subject of 4 registered US clinical trials on ClinicalTrials.gov, 4 of them currently open to new participants. The most active sponsor is Rocket Pharmaceuticals, running 1 of these trials.
Enrollment posture brief
Registry condition genetic-diseases
OPEN 4 | RECR 100% | LATE 0 | EARLY 0 | RANK #4115 | SPON 1
Volume-matched condition peers
Nearest open-share peer: Aortic Arch Aneurysm (100% recruiting · 5 trials)
Genetic Diseases lists 4 open slots (100% of 4 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Genetic Diseases on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Genetic Diseases is recruiting above its size-band peers.
4 of 4 indexed trials (100%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
Open and recent trials
4 total, page 1 of 1
Rady Children's Institute Genomic Biorepository
Rady Pediatric Genomics & Systems Medicine Institute
NCT02917460
Familial Mediterranean Fever and Related Disorders: Genetics and Disease Characteristics
National Human Genome Research Institute (NHGRI)
NCT00001373
Genetic and Metabolic Disease in Children
University of Texas Southwestern Medical Center
NCT02650622
PKP2-ACM Natural History Study
Rocket Pharmaceuticals
NCT06644742
Phase Distribution
Phase data not available
Top Sponsors
Named interventions
Most-linked intervention names on Genetic Diseases records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Genetic Diseases trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Genetic Diseases page
4 registered trials, 4 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 4 Genetic Diseases trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- Rocket Pharmaceuticals sponsors the most Genetic Diseases trials on record, review their full trial history before evaluating a specific study. See Rocket Pharmaceuticals's trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Genetic Diseases condition card totals 4 registered trials; most-linked intervention Genomic sequencing and molecular diagnostic results, if any; top US site state Texas. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.