Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.

2026 data Public-data reference. official source

Dravet Syndrome

Open-data reference.

13 US clinical trials · 5 currently recruiting

Active & Recent Trials

RECRUITING Phase 3 170 participants

A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet Syndrome

Stoke Therapeutics

NCT06872125

RECRUITING Phase 3 160 participants

A Phase 3, Placebo-Controlled Study to Investigate LP352 in Children and Adults With Dravet Syndrome (DS)

Longboard Pharmaceuticals

NCT06660394

RECRUITING Phase 3 150 participants

A Study of EPX-100 (Clemizole Hydrochloride) in Participants With Dravet Syndrome

Epygenix

NCT04462770

RECRUITING Phase 1 47 participants

A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome

Encoded Therapeutics

NCT05419492

RECRUITING 36 participants

GABA Biomarkers in Dravet Syndrome

Cook Children's Health Care System

NCT05651204

ACTIVE NOT RECRUITING Phase 4 154 participants

Assessment of Potential for Chronic Liver Injury in Participants Treated With Epidiolex (Cannabidiol) Oral Solution

Jazz Pharmaceuticals

NCT05044819

ACTIVE NOT RECRUITING Phase 2 60 participants

An Open-Label Extension Study of STK-001 for Patients With Dravet Syndrome

Stoke Therapeutics

NCT04740476

ACTIVE NOT RECRUITING Phase 3 25 participants

A Study to Evaluate Safety, Tolerability, and Pharmacokinetics of Fenfluramine (Hydrochloride) in Infants 1 Year to Less Than 2 Years of Age With Dravet Syndrome

UCB BIOSCIENCES

NCT06118255

COMPLETED Phase 3 412 participants

A Study to Investigate the Long-Term Safety of ZX008 (Fenfluramine Hydrochloride) Oral Solution in Children and Adults With Epileptic Encephalopathy Including Dravet Syndrome and Lennox-Gastaut Syndrome

Zogenix

NCT03936777

COMPLETED Phase 1 52 participants

Study to Investigate LP352 in Subjects With Developmental and Epileptic Encephalopathies

Longboard Pharmaceuticals

NCT05364021

COMPLETED Phase 2 41 participants

Open-label, Long-term Safety Study of LP352 in Subjects With Developmental and Epileptic Encephalopathy

Longboard Pharmaceuticals

NCT05626634

COMPLETED Phase 1 9 participants

A Study to Assess the Safety and Tolerability of ZX008 in Children and Young Adults With Dravet Syndrome or Lennox Gastaut Syndrome Currently Taking Cannabidiol

Zogenix International Limited, Inc., a subsidiary of Zogenix

NCT03467113

COMPLETED Phase 2 2 participants

Verapamil as Therapy for Children and Young Adults With Dravet Syndrome

Gillette Children's Specialty Healthcare

NCT01607073

Phase Distribution

PhaseTrial count
Early Phase 1 3
Phase 2 3
Phase 3 5
Phase 4 1

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

Reading the Dravet Syndrome Trial Landscape

ClinicalTrials.gov lists 13 US studies indexed under Dravet Syndrome, and 5 of those are currently open to recruitment — roughly 38% of the total volume on the registry. That ratio is a useful proxy for activity level: a high share of recruiting studies often signals that research interest is current and that new enrollment opportunities are appearing, while a low share typically means the field is dominated by completed or follow-up work where most participant spots have already been filled. These counts reflect the public registry only and include studies at every stage of design, so they should be read as an index of research attention rather than as a measure of treatment availability.

The phase distribution for Dravet Syndrome shows 6 late-stage studies (Phase 3 and Phase 4 combined) alongside 6 earlier-phase entries (Phase 1 through Phase 2). Phase 1 and Phase 2 studies focus on early safety signals, dosing, and preliminary effect, while Phase 3 studies are typically the larger efficacy and safety trials submitted toward regulatory review, and Phase 4 studies follow approved interventions in real-world use. A condition weighted toward later phases often reflects a mature research pipeline with several interventions already close to or past approval, whereas a heavier early-phase tilt suggests the field is still exploring new mechanisms and candidate approaches.

Top sponsor activity for Dravet Syndrome is led by Longboard Pharmaceuticals with 3 indexed trials, alongside 9 other organizations in the top contributor list. The list on this page surfaces up to 13 of the most relevant recent and active entries, ordered with recruiting studies first so practical options are visible. All figures are derived from the public ClinicalTrials.gov dataset maintained by the National Library of Medicine and are reproduced here for reference. Inclusion of a trial, sponsor, or intervention on this page is neither an endorsement nor a recommendation — eligibility, protocol changes, and site-level status can shift frequently, so always verify current details on ClinicalTrials.gov and consult a qualified healthcare provider before acting on anything you see here.

Frequently Asked Questions

How many clinical trials are there for Dravet Syndrome?

PlainTrial tracks 13 US clinical trials for Dravet Syndrome, of which 5 are currently recruiting participants. Data sourced from ClinicalTrials.gov.

How do I find a recruiting trial for Dravet Syndrome?

Use the trial list above filtered by "Recruiting" status, or visit our trial finder at /recruiting to search by condition and state. Always discuss trial participation with your healthcare provider before enrolling.

Is this data current?

Data is sourced from ClinicalTrials.gov and reflects our most recent data pull. Trial status may have changed since then. Always verify current information at ClinicalTrials.gov before making decisions about participation.

Related

Data sourced from official U.S. government datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Disclaimer: This information is provided for informational purposes only and does not constitute professional advice. Data is sourced from ClinicalTrials.gov (National Library of Medicine). Consult a qualified professional before making decisions based on this data.

Source: ClinicalTrials.gov (NIH/NLM) ClinicalTrials.gov AACT registry · 2024 Trial counts and statuses sourced from ClinicalTrials.gov. Sponsor counts include both industry and federal/academic sponsors.

Verify with NIH →