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Charcot Marie Tooth Disease: later-stage trial registry
3 of 8 indexed Charcot Marie Tooth Disease trials are currently recruiting, with more weight in Phase 3-4.
Corpus placement: #2,176 of 28,707 conditions by registered trial count.
8 US clinical trials · 3 currently recruiting · #2,176 of 28,707 conditions by registered trial count
Charcot Marie Tooth Disease: 8 US clinical trials tracked, 3 recruiting.
Charcot Marie Tooth Disease is the subject of 8 registered US clinical trials on ClinicalTrials.gov, 3 of them currently open to new participants. 1 are in Phase 3-4 (later-stage) and 0 in Phase 1-2 (earlier-stage). The most active sponsor is Pharnext S.C.A., running 1 of these trials.
Enrollment posture brief
Registry condition charcot-marie-tooth-disease
OPEN 3 | RECR 38% | LATE 1 | EARLY 0 | RANK #2176 | SPON 1
Volume-matched condition peers
Nearest open-share peer: Acute-graft-versus-host Disease (38% recruiting · 8 trials)
Charcot Marie Tooth Disease lists 3 open slots (38% of 8 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Charcot Marie Tooth Disease on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Charcot Marie Tooth Disease is recruiting below its size-band peers.
3 of 8 indexed trials (37.5%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
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Sponsorship of Charcot Marie Tooth Disease trials is spread across many organizations.
Pharnext S.C.A. accounts for 1 of 8 trials (12.5%). 8 distinct sponsors appear on at least one study for this condition label.
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Typical Charcot Marie Tooth Disease enrolment sits around 350 participants.
Median target enrolment is 350 among the 8 trials that report a genuine target (sentinel values excluded). 2 of those (25%) plan for fewer than 100 participants.
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Charcot Marie Tooth Disease research leans observational.
1 interventional and 7 observational studies make up this index (12.5% interventional). Study type is sponsor-reported on ClinicalTrials.gov.
Open and recent trials
8 total, page 1 of 1
Natural History Study for Charcot Marie Tooth Disease
Hereditary Neuropathy Foundation
NCT05902351
Natural History Evaluation of Charcot Marie Tooth Disease (CMT) Types CMT1B, CMT2A, CMT4A, CMT4C, and Others
Michael Shy
NCT01193075
Charcot-Marie-Tooth Disease (CMT) Biological Sample Collection for IPSC Generation and Biobanking
New York Stem Cell Foundation Research Institute
NCT06203093
Phase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients
Pharnext S.C.A.
NCT04762758
Disability Severity Scale (DSI) and Hereditary Motor and Sensory Neuropathy Overall Disability Scale (HMSN-R-ODS)
University of Iowa
NCT02194010
Patient Reported Outcomes Measures (PROM) in Carpal Tunnel Therapies in Patients With Inherited Neuropathies
University of South Florida
NCT02788734
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases
Nemours Children's Clinic
NCT02532244
Observational Study of Neuromuscular Function in CMT Type 1&2 and Healthy Controls
NMD Pharma A/S
NCT04980807
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 3 | 1 |
Top Sponsors
Named interventions
Most-linked intervention names on Charcot Marie Tooth Disease records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Charcot Marie Tooth Disease trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Charcot Marie Tooth Disease page
8 registered trials, 3 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 3 Charcot Marie Tooth Disease trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- Pharnext S.C.A. sponsors the most Charcot Marie Tooth Disease trials on record, review their full trial history before evaluating a specific study. See Pharnext S.C.A.'s trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Charcot Marie Tooth Disease condition card totals 8 registered trials; most-linked intervention Web-based survey; top US site state New York. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.