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ClinicalTrials.gov 8 recruiting now full pipeline small index

Neuromuscular Diseases: full-pipeline trial registry

8 of 16 indexed Neuromuscular Diseases trials are currently recruiting.

Corpus placement: #1,060 of 28,707 conditions by registered trial count.

16 US clinical trials · 8 currently recruiting · #1,060 of 28,707 conditions by registered trial count

Neuromuscular Diseases: 16 US clinical trials tracked, 8 recruiting.

Neuromuscular Diseases is the subject of 16 registered US clinical trials on ClinicalTrials.gov, 8 of them currently open to new participants. 4 are in Phase 3-4 (later-stage) and 4 in Phase 1-2 (earlier-stage). The most active sponsor is Scholar Rock, running 3 of these trials.

Enrollment posture brief

Registry condition neuromuscular-diseases

OPEN 8 | RECR 50% | LATE 4 | EARLY 4 | RANK #1060 | SPON 3

Nearest open-share peer: Abdominal Aortic Aneurysms (50% recruiting · 6 trials)

Adolescent62.5%Alcohol Intoxication56.3%Neuromuscular Diseases (this)50%AL Amyloidosis43.8%Allergy18.8%
Open-enrollment share among volume-matched conditions near Neuromuscular Diseases

Neuromuscular Diseases lists 8 open slots (50% of 16 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Neuromuscular Diseases on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Neuromuscular Diseases is recruiting above its size-band peers.

    8 of 16 indexed trials (50%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Neuromuscular Diseases research.

    Scholar Rock accounts for 3 of 16 trials (18.8%). 14 distinct sponsors appear on at least one study for this condition label.

  3. Typical Neuromuscular Diseases enrolment sits around 90 participants.

    Median target enrolment is 90 among the 16 trials that report a genuine target (sentinel values excluded). 9 of those (56.3%) plan for fewer than 100 participants.

  4. Neuromuscular Diseases splits between interventional and observational designs.

    10 interventional and 6 observational studies make up this index (62.5% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 11Phase 23Phase 34

Open and recent trials

16 total, page 1 of 1

RECRUITING 500 participants

CIMR Neuromuscular Research Biobank

Virginia Commonwealth University

NCT05434572

RECRUITING 100 participants

Spastic Paraplegia - Centers of Excellence Research Network

Boston Children's Hospital

NCT06553976

RECRUITING 90 participants

Genesis Electrical Impedance Tomography (EIT): A Preliminary Study

University of Colorado, Denver

NCT03797183

RECRUITING Phase 2 51 participants

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

Satellos Bioscience

NCT07287189

RECRUITING 40 participants

Measuring Physical Activity With ActivPal

Columbia University

NCT06084026

RECRUITING 20 participants

A Prospective Natural History and Outcome Measure Discovery Study of Charcot-Marie-Tooth Disease, Type 4J

Elpida Therapeutics SPC

NCT06151600

RECRUITING NA 20 participants

Non-Invasive Respiratory Monitor

Nemours Children's Clinic

NCT02851043

RECRUITING NA 20 participants

Mechanical Insufflation in the Philadelphia Amyotrophic Lateral Sclerosis Cohort (MI-PALS) Study

University of Pennsylvania

NCT06119087

ACTIVE NOT RECRUITING Phase 3 269 participants

A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy

Biohaven Pharmaceuticals

NCT05337553

ACTIVE NOT RECRUITING Phase 3 238 participants

Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab

Scholar Rock

NCT05626855

ACTIVE NOT RECRUITING Phase 3 106 participants

A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

Capricor

NCT05126758

COMPLETED 215 participants

Expediting Myasthenia Gravis (MG) Diagnostic Evaluation: A Novel, Proof-of-Concept for Undiagnosed, Symptomatic Patients That Uses Social Media Targeting and Self-Assessment

ZS Associates

NCT06381284

COMPLETED Phase 3 188 participants

Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

Scholar Rock

NCT05156320

COMPLETED Phase 2 58 participants

An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy

Scholar Rock

NCT03921528

COMPLETED Phase 2 37 participants

Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients

Avidity Biosciences

NCT05479981

COMPLETED Phase 1 19 participants

Study of Pioglitazone in Sporadic Inclusion Body Myositis

Johns Hopkins University

NCT03440034

Phase Distribution

PhaseTrial count
Phase 1 1
Phase 2 3
Phase 3 4

Named interventions

Most-linked intervention names on Neuromuscular Diseases records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Placebo Drug
4 trials
Apitegromab Drug
2 trials
AOC 1001 Drug
1 trials
SRK-015 Biological
1 trials
Deramiocel (CAP-1002) Biological
1 trials
taldefgrobep alfa Drug
1 trials
Mechanical insufflation Device
1 trials
ActivPal Other
1 trials

US sites by state

Facility locations filed on Neuromuscular Diseases trials. A trial with sites in several states counts in each.

Colorado 8 trials
California 8 trials
Ohio 7 trials
New York 7 trials
Massachusetts 7 trials
Illinois 6 trials
Iowa 6 trials
Virginia 5 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Neuromuscular Diseases page

16 registered trials, 8 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 8 Neuromuscular Diseases trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • Scholar Rock sponsors the most Neuromuscular Diseases trials on record, review their full trial history before evaluating a specific study. See Scholar Rock's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Neuromuscular Diseases condition card totals 16 registered trials; most-linked intervention Placebo; top US site state Colorado. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.