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NCT05626855 · ClinicalTrials.gov registry record · Phase 3

Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab

A Phase 3 study of Spinal Muscular Atrophy and Neuromuscular Diseases, sponsored by Scholar Rock.

Active
Registry status
Phase 3
Development phase
238
Enrollment target
20
Study locations

NCT05626855 is a Phase 3 study of Spinal Muscular Atrophy and Neuromuscular Diseases that is active but no longer recruiting, run by Scholar Rock. The registered enrollment target is 238 participants, above the 98-participant average among 22 other Spinal Muscular Atrophy trials with a reported enrollment target (143% higher). The trial reports 20 study locations across 18 states.

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The verdict

NCT05626855, a Phase 3 study of Spinal Muscular Atrophy and Neuromuscular Diseases, is active but no longer recruiting, sponsored by Scholar Rock.

ACTIVE NOT RECRUITING
Registry status
Phase 3
Development phase
238 participants
Enrollment target
20
Study locations

Study Summary

The ONYX study is an Open-Label, Multicenter, Extension study that will evaluate the long-term safety and efficacy of Apitegromab in Patients with Type 2 and Type 3 SMA who have completed TOPAZ or SAPPHIRE.

Interventions

  • DRUG Apitegromab

Study Locations (20)

California

  • UCSD Altman Clinical and Translational Research - La Jolla
  • Children's Hospital Los Angeles - Los Angeles
  • Stanford Neuroscience Health Center - Palo Alto

Arizona

  • Phoenix Childrens Hospital - Phoenix

Colorado

  • Children's Hospital Colorado - Aurora

Florida

  • Nemours Biomedical Research - Orlando

Illinois

  • Lurie Children's Hospital of Chicago - Chicago

Iowa

  • University of Iowa - Iowa City

Kansas

  • University of Kansas Medical Center - Fairway

Maryland

  • Johns HopkinsHospital - Baltimore

Trial Details

FieldValue
Enrollment Target 238 participants
Start Date 2023-04-17
Est. Completion 2029-05-02
Phase Phase 3

Sponsor

Scholar Rock

7 total trials

What the Registry Record Tells You About NCT05626855

The ClinicalTrials.gov registry entry for NCT05626855 describes a study currently listed as active not recruiting, categorized as Phase 3. The registered enrollment target is 238 participants, a figure that helps gauge the scale of data the investigators plan to collect, above the 98-participant average among 22 other Spinal Muscular Atrophy trials with a reported enrollment target (143% higher). The listed sponsor is Scholar Rock, which has 7 total studies on file at ClinicalTrials.gov.

The record links to 10 conditions, with Spinal Muscular Atrophy appearing as the primary indexed condition, and to 1 intervention - of which Apitegromab is the first listed.

NCT05626855 reports 20 study locations spanning 18 distinct geographic areas - top geographies include California, Arizona, Colorado.

Frequently Asked Questions

What is clinical trial NCT05626855 about?

NCT05626855 is a clinical study titled "Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab". The ONYX study is an Open-Label, Multicenter, Extension study that will evaluate the long-term safety and efficacy of Apitegromab in Patients with Type 2 and Type 3 SMA who have completed TOPAZ or SAPPHIRE.

What is the current status of trial NCT05626855?

This trial is currently active not recruiting. It is a Phase 3 study. The enrollment target is 238 participants. The study started on 2023-04-17. Estimated completion is 2029-05-02.

What conditions does trial NCT05626855 study?

This clinical trial studies the following conditions: Spinal Muscular Atrophy, Neuromuscular Diseases, Muscular Atrophy, Spinal, Spinal Muscular Atrophy Type 3, Neuromuscular Manifestations.

What interventions are being tested in trial NCT05626855?

The interventions under investigation include: Apitegromab (DRUG).

Who is sponsoring clinical trial NCT05626855?

This trial is sponsored by Scholar Rock, which has 7 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05626855 being conducted?

This trial has 20 study locations across Arizona, California, Colorado, Florida, Illinois. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.