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ClinicalTrials.gov 5 recruiting now early-phase tilt small index

Neurofibromatosis Type 1: early-phase trial registry

5 of 18 indexed Neurofibromatosis Type 1 trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #953 of 28,707 conditions by registered trial count.

18 US clinical trials · 5 currently recruiting · #953 of 28,707 conditions by registered trial count

Neurofibromatosis Type 1: 18 US clinical trials tracked, 5 recruiting.

Neurofibromatosis Type 1 is the subject of 18 registered US clinical trials on ClinicalTrials.gov, 5 of them currently open to new participants. 2 are in Phase 3-4 (later-stage) and 8 in Phase 1-2 (earlier-stage). The most active sponsor is National Cancer Institute (NCI), running 7 of these trials.

Enrollment posture brief

Registry condition neurofibromatosis-type-1

OPEN 5 | RECR 28% | LATE 2 | EARLY 8 | RANK #953 | SPON 7

Nearest open-share peer: Diabetic Peripheral Neuropathy (28% recruiting · 18 trials)

Neurofibromatosis Type 1 (th…28%Arrhythmias, Cardiac27.8%Androgenetic Alopecia16.7%Anemia, Sickle Cell16.7%Acquired Immunodeficiency Sy5.6%
Open-enrollment share among volume-matched conditions near Neurofibromatosis Type 1

Neurofibromatosis Type 1 lists 5 open slots (28% of 18 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Neurofibromatosis Type 1 on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Neurofibromatosis Type 1 is recruiting below its size-band peers.

    5 of 18 indexed trials (27.8%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Neurofibromatosis Type 1 research.

    National Cancer Institute (NCI) accounts for 7 of 18 trials (38.9%). 11 distinct sponsors appear on at least one study for this condition label.

  3. Most Neurofibromatosis Type 1 trials plan to enrol fewer than 100 people.

    Median target enrolment is 71 among the 18 trials that report a genuine target (sentinel values excluded). 11 of those (61.1%) plan for fewer than 100 participants.

  4. Neurofibromatosis Type 1 research is mostly interventional.

    13 interventional and 5 observational studies make up this index (72.2% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 14Phase 24Phase 32

Open and recent trials

18 total, page 1 of 1

RECRUITING 1,000 participants

Neurofibromatosis Type 1 Tumor Early Detection Study

David Miller

NCT06515860

RECRUITING 110 participants

Development of Patient-Reported Outcome Measures Assessing Tumor Visibility and Appearance Concerns in Neurofibromatosis Type 1: A Qualitative Study

National Cancer Institute (NCI)

NCT06880991

RECRUITING NA 70 participants

A Study to Evaluate the Feasibility of a Physiologic Biomarker to Assess Pain and Other Sensory Problems Using Pupillometry in Participants With Neurofibromatosis Type 1 (NF1)

National Cancer Institute (NCI)

NCT06507748

RECRUITING Phase 2 25 participants

A Phase 2, Open-Label Study to Evaluate the Safety and Effects of HLX-1502 in Patients With Neurofibromatosis Type 1

Healx Limited

NCT06541847

RECRUITING NA 15 participants

Identification of Pre-Malignant Lesions In Pediatric Patients With Neurofibromatosis Type 1 Using Novel Magnetic Resonance Imaging Techniques Paired With Artificial Intelligence

Nicole Baca

NCT04763109

ACTIVE NOT RECRUITING 500 participants

Natural History Study of Cutaneous Neurofibromas in People With NF1

Johns Hopkins University

NCT05581511

ACTIVE NOT RECRUITING 259 participants

Natural History Study of Patients With Neurofibromatosis Type I

National Cancer Institute (NCI)

NCT00924196

ACTIVE NOT RECRUITING Phase 3 165 participants

A Study of the Drugs Selumetinib Versus Carboplatin/Vincristine in Patients With Neurofibromatosis and Low-Grade Glioma

National Cancer Institute (NCI)

NCT03871257

ACTIVE NOT RECRUITING Phase 2 120 participants

Interventions for Reading Disabilities in NF1

Vanderbilt University

NCT02964884

ACTIVE NOT RECRUITING Phase 1 99 participants

AZD6244 Hydrogen Sulfate for Children With Nervous System Tumors

National Cancer Institute (NCI)

NCT01362803

ACTIVE NOT RECRUITING Phase 1 36 participants

Pharmacokinetics, Safety and Efficacy of the Selumetinib Granule Formulation in Children Aged ≥1 to <7 Years With NF1-related Symptomatic, Inoperable PN

AstraZeneca

NCT05309668

ACTIVE NOT RECRUITING Phase 1 24 participants

Phase I Study to Assess the Effect of Food on the PK and Gastrointestinal Tolerability of Selumetinib in Adolescent Children With Neurofibromatosis Type 1 Related Plexiform Neurofibromas

AstraZeneca

NCT05101148

ACTIVE NOT RECRUITING Phase 2 10 participants

Trametinib in Treating Patients With Relapsed or Refractory Juvenile Myelomonocytic Leukemia

National Cancer Institute (NCI)

NCT03190915

COMPLETED NA 103 participants

Efficacy of Computerized Cognitive Training and Stimulant Medication in Neurofibromatosis Type 1

Kristina Hardy

NCT02944032

COMPLETED 71 participants

Targeting the Mechanisms Underlying Cutaneous Neurofibroma Formation in NF1: A Clinical Translational Approach.

Corewell Health West

NCT02777775

COMPLETED Phase 3 66 participants

Acceptance and Commitment Training for Adolescents and Young Adults With Neurofibromatosis Type 1, Plexiform Neurofibromas, and Chronic Pain

National Cancer Institute (NCI)

NCT02471339

COMPLETED Phase 2 48 participants

Combination Chemotherapy in Treating Patients With Stage III or Stage IV Malignant Peripheral Nerve Sheath Tumors

Sarcoma Alliance for Research through Collaboration

NCT00304083

COMPLETED Phase 1 9 participants

Vaccine Therapy in Treating Patients with Malignant Peripheral Nerve Sheath Tumor That is Recurrent or Cannot Be Removed by Surgery

Mayo Clinic

NCT02700230

Phase Distribution

PhaseTrial count
Phase 1 4
Phase 2 4
Phase 3 2

Named interventions

Most-linked intervention names on Neurofibromatosis Type 1 records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Quality-of-Life Assessment Other
2 trials
Mobymax Other
1 trials
CogmedRM Other
1 trials
Other Academic "sham" tutoring Behavioral
1 trials
reading tutoring intervention Behavioral
1 trials
Selumetinib capsule formulation Drug
1 trials
Selumetinib granule formulation Drug
1 trials
doxorubicin hydrochloride Drug
1 trials

US sites by state

Facility locations filed on Neurofibromatosis Type 1 trials. A trial with sites in several states counts in each.

Maryland 8 trials
Ohio 5 trials
California 5 trials
Pennsylvania 4 trials
Alabama 4 trials
Texas 3 trials
Minnesota 3 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Neurofibromatosis Type 1 page

18 registered trials, 5 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Neurofibromatosis Type 1 condition card totals 18 registered trials; most-linked intervention Quality-of-Life Assessment; top US site state Maryland. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.