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ClinicalTrials.gov 3 recruiting now later-stage tilt small index

Hemophilia: later-stage trial registry

3 of 10 indexed Hemophilia trials are currently recruiting, with more weight in Phase 3-4.

Corpus placement: #1,724 of 28,707 conditions by registered trial count.

10 US clinical trials · 3 currently recruiting · #1,724 of 28,707 conditions by registered trial count

Hemophilia: 10 US clinical trials tracked, 3 recruiting.

Hemophilia is the subject of 10 registered US clinical trials on ClinicalTrials.gov, 3 of them currently open to new participants. 4 are in Phase 3-4 (later-stage) and 2 in Phase 1-2 (earlier-stage). The most active sponsor is Genzyme, a Sanofi Company, running 2 of these trials.

Enrollment posture brief

Registry condition hemophilia

OPEN 3 | RECR 30% | LATE 4 | EARLY 2 | RANK #1724 | SPON 2

Nearest open-share peer: Adrenocortical Carcinoma (30% recruiting · 10 trials)

Acute Leukemia of Ambiguous 80%Achondroplasia40%Hemophilia (this)30%Accelerated Phase Chronic My20%Accidental Fall20%
Open-enrollment share among volume-matched conditions near Hemophilia

Hemophilia lists 3 open slots (30% of 10 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Hemophilia on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Hemophilia is recruiting below its size-band peers.

    3 of 10 indexed trials (30%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Hemophilia research.

    Genzyme, a Sanofi Company accounts for 2 of 10 trials (20%). 8 distinct sponsors appear on at least one study for this condition label.

  3. Most Hemophilia trials plan to enrol fewer than 100 people.

    Median target enrolment is 72 among the 10 trials that report a genuine target (sentinel values excluded). 8 of those (80%) plan for fewer than 100 participants.

  4. Hemophilia research is mostly interventional.

    8 interventional and 2 observational studies make up this index (80% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 11Phase 21Phase 34

Open and recent trials

10 total, page 1 of 1

RECRUITING 3,000 participants

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

American Thrombosis and Hemostasis Network

NCT04398628

RECRUITING Phase 3 85 participants

A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B

Sanofi

NCT07285460

RECRUITING Early Phase 1 50 participants

Topical and Local TXA in Facelifts - A Randomized Controlled Double Blinded Study

University of Minnesota

NCT06345833

ACTIVE NOT RECRUITING Phase 3 281 participants

Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX

Genzyme, a Sanofi Company

NCT03754790

ACTIVE NOT RECRUITING Phase 3 91 participants

A Study to Test a Medicine (Fitusiran) Injected Under the Skin for Preventing Bleeding Episodes in Male Adolescent or Adult Participants With Severe Hemophilia

Sanofi

NCT05662319

ACTIVE NOT RECRUITING Phase 3 32 participants

Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B

Genzyme, a Sanofi Company

NCT03974113

COMPLETED NA 72 participants

Clinical Trial of Factor XIII (FXIII) Concentrate

Children's Hospital of Orange County

NCT00640289

COMPLETED 45 participants

Motor Proficiency of People With Bleeding Disorders Using the BOT-2 (TM)

Oregon Health and Science University

NCT02279199

COMPLETED Phase 2 22 participants

Treatment of Hepatitis C in Hemophilic Patients With HIV

National Institute of Allergy and Infectious Diseases (NIAID)

NCT00055341

COMPLETED NA 13 participants

The Use of Cyclokapron for Treatment and Management of Women With Bleeding Disorders

Mary M. Gooley Hemophilia Center

NCT00697385

Phase Distribution

PhaseTrial count
Phase 1 1
Phase 2 1
Phase 3 4

Named interventions

Most-linked intervention names on Hemophilia records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Fitusiran Drug
4 trials
Fibrogammin P Drug
1 trials
Cyclokapron Drug
1 trials
Peginterferon alfa-2a Drug
1 trials
Ribavirin Drug
1 trials
Antithrombin concentrate (ATIIIC) Drug
1 trials
Clotting factor concentrates (CFC) or bypassing agents (BPA) Drug
1 trials
Antithrombin concentrate (ATIIIC) Biological
1 trials

US sites by state

Facility locations filed on Hemophilia trials. A trial with sites in several states counts in each.

California 6 trials
Ohio 4 trials
Pennsylvania 2 trials
New York 2 trials
New Jersey 2 trials
Minnesota 2 trials
Florida 2 trials
Arizona 2 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Hemophilia page

10 registered trials, 3 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Hemophilia condition card totals 10 registered trials; most-linked intervention Fitusiran; top US site state California. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.