Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT03754790 · ClinicalTrials.gov registry record · Phase 3

Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX

A Phase 3 study of Hemophilia, sponsored by Genzyme, a Sanofi Company.

Active
Registry status
Phase 3
Development phase
281
Enrollment target
20
Study locations

NCT03754790 is a Phase 3 study of Hemophilia that is active but no longer recruiting, run by Genzyme, a Sanofi Company. The registered enrollment target is 281 participants, below the 379-participant average among 9 other Hemophilia trials with a reported enrollment target (26% lower). The trial reports 20 study locations across 13 states.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT03754790, a Phase 3 study of Hemophilia, is active but no longer recruiting, sponsored by Genzyme, a Sanofi Company.

ACTIVE NOT RECRUITING
Registry status
Phase 3
Development phase
281 participants
Enrollment target
20
Study locations

Study Summary

Primary Objective: To characterize the long-term safety and tolerability of fitusiran Secondary Objectives: * To characterize the efficacy and long-term efficacy of fitusiran as assessed by the frequency of: * Bleeding episodes * Spontaneous bleeding episodes * Joint bleeding episodes * To characterize the effects of fitusiran on health-related quality of life (HRQOL) measures in participants ≥17 years of age

Conditions Studied

Interventions

  • DRUG Fitusiran

Study Locations (20)

Other

  • Investigational Site Number : 1560004 - Beijing
  • Investigational Site Number : 1560007 - Beijing
  • Investigational Site Number : 1560014 - Changsha
  • Investigational Site Number : 1560009 - Chengdu
  • Investigational Site Number : 1560002 - Guangzhou
  • Investigational Site Number : 1560011 - Guiyang

California

  • Children's Hospital Los Angeles Site Number : 8400019 - Los Angeles
  • Center for Inherited Blood Disorders (CIBD) Site Number : 8400016 - Orange

Florida

  • Nemours Children's Clinic Site Number : 8400008 - Jacksonville
  • St Joseph's Children's Hospital of Tampa Site Number : 8400002 - Tampa

Arizona

  • Phoenix Childrens Hospital Site Number : 8400009 - Phoenix

Illinois

  • Rush University Medical Center -1725 W Harrison St Site Number : 8400001 - Chicago

Massachusetts

  • ~Massachusetts General Hospital Site Number : 8400011 - Boston

Michigan

  • University of Michigan Hospital - 1500 E Medical Center Dr Site Number : 8400012 - Ann Arbor

Nevada

  • Alliance for Childhood Diseases Site Number : 8400007 - Las Vegas

Trial Details

FieldValue
Enrollment Target 281 participants
Start Date 2019-01-09
Est. Completion 2026-11-05
Phase Phase 3

Sponsor

Genzyme, a Sanofi Company

196 total trials

What the Registry Record Tells You About NCT03754790

The ClinicalTrials.gov registry entry for NCT03754790 describes a study currently listed as active not recruiting, categorized as Phase 3. The registered enrollment target is 281 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 379-participant average among 9 other Hemophilia trials with a reported enrollment target (26% lower). The listed sponsor is Genzyme, a Sanofi Company, which has 196 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Hemophilia appearing as the primary indexed condition, and to 1 intervention - of which Fitusiran is the first listed.

NCT03754790 reports 20 study locations spanning 13 distinct geographic areas - top geographies include Other, California, Florida.

Frequently Asked Questions

What is clinical trial NCT03754790 about?

NCT03754790 is a clinical study titled "Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX". Primary Objective: To characterize the long-term safety and tolerability of fitusiran Secondary Objectives: * To characterize the efficacy and long-term efficacy of fitusiran as assessed by the frequency of: * Bleeding episodes * Spontaneous bleeding episodes * Joint bleeding episodes * To...

What is the current status of trial NCT03754790?

This trial is currently active not recruiting. It is a Phase 3 study. The enrollment target is 281 participants. The study started on 2019-01-09. Estimated completion is 2026-11-05.

What conditions does trial NCT03754790 study?

This clinical trial studies the following conditions: Hemophilia.

What interventions are being tested in trial NCT03754790?

The interventions under investigation include: Fitusiran (DRUG).

Who is sponsoring clinical trial NCT03754790?

This trial is sponsored by Genzyme, a Sanofi Company, which has 196 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT03754790 being conducted?

This trial has 20 study locations across Arizona, California, Florida, Illinois, Massachusetts. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Hemophilia

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.