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NCT05794139 · ClinicalTrials.gov registry record · Phase 2

Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy

A Phase 2 study of Spinal Muscular Atrophy, sponsored by NMD Pharma A/S.

Recruiting
Registry status
Phase 2
Development phase
54
Enrollment target
20
Study locations

NCT05794139: Recruiting Phase 2 study of Spinal Muscular Atrophy, sponsored by NMD Pharma A/S.

NCT05794139 is a Phase 2 study of Spinal Muscular Atrophy that is actively recruiting participants, run by NMD Pharma A/S. The registered enrollment target is 54 participants, below the 107-participant average among 22 other Spinal Muscular Atrophy trials with a reported enrollment target (50% lower). The trial reports 20 study locations across 11 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT05794139, a Phase 2 study of Spinal Muscular Atrophy, is actively recruiting participants, sponsored by NMD Pharma A/S.

RECRUITING
Registry status
Phase 2
Development phase
54 participants
Enrollment target
20
Study locations

Study Summary

The purpose of this study is to evaluate the efficacy, safety, tolerability and pharmacokinetics of NMD670 in the treatment of ambulatory adults with spinal muscular atrophy type 3

Primary Outcome

Distance walked (meters)

Conditions Studied

Interventions

  • DRUG Placebo
  • DRUG NMD670

Study Locations (20)

Other

  • UZ Leuven - Neurochirurgie Campus Gasthuisberg - Leuven
  • CHR de la Citadelle - Neurologie - Liège
  • Heritage Medical Research Clinic - Calgary
  • Genge Partners Inc. - Montreal
  • Aarhus Universitetshospital, Neurologisk Afdeling - Aarhus
  • Rigshospitalet - Neurologisk Afdeling - Copenhagen
  • Charite - Campus Virchow-Klinikum (CVK) - Berlin
  • Universitätsklinikum Essen - Klinik Für Neurologie - Essen

California

  • UCLA David Geffen School Of Medicine - Neurology - Los Angeles
  • Stanford University Medical Center - Palo Alto

Missouri

  • Roy Blunt NextGen Precision Health Institute - Columbia
  • Washington University School of Medicine - St Louis

Colorado

  • University of Colorado Neurology Clinic - Aurora

Florida

  • UF Fixel Institute for Neurological Diseases - Gainesville

Georgia

  • Rare Disease Center - Atlanta

Kansas

  • University of Kansas Medical Center - Kansas City

Maryland

  • The Johns Hopkins Medicine, Spinal Muscular Atrophy Center - Baltimore

Trial Details

FieldValue
Enrollment Target 54 participants
Start Date 2023-09-21
Est. Completion 2026-05
Phase Phase 2
NMD Pharma A/S

5 total trials

What NCT05794139 shows while recruiting

NCT05794139 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 54 participants, a relatively small participant target, below the 107-participant average among 22 other Spinal Muscular Atrophy trials with a reported enrollment target (50% lower).

The record links to 1 condition, with Spinal Muscular Atrophy appearing as the primary indexed condition, and to 2 interventions - of which Placebo is the first listed.

NCT05794139 names 20 study sites across 11 states, led by Other, California, Missouri.

Frequently Asked Questions

What is clinical trial NCT05794139 about?

NCT05794139 is a clinical study titled "Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy". The purpose of this study is to evaluate the efficacy, safety, tolerability and pharmacokinetics of NMD670 in the treatment of ambulatory adults with spinal muscular atrophy type 3

What is the current status of trial NCT05794139?

This trial is currently recruiting. It is a Phase 2 study. The enrollment target is 54 participants. The study started on 2023-09-21. Estimated completion is 2026-05.

What conditions does trial NCT05794139 study?

This clinical trial studies the following conditions: Spinal Muscular Atrophy.

What interventions are being tested in trial NCT05794139?

The interventions under investigation include: Placebo (DRUG), NMD670 (DRUG).

Who is sponsoring clinical trial NCT05794139?

This trial is sponsored by NMD Pharma A/S, which has 5 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05794139 being conducted?

This trial has 20 study locations across California, Colorado, Florida, Georgia, Kansas. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Spinal Muscular Atrophy

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT05794139's enrollment target sits among peer trials

54 12th of 22 higher than 11 of 22 other Spinal Muscular Atrophy trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Spinal Muscular Atrophy trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT05794139, the US trial registry maintained by the National Library of Medicine. NCT05794139 (small enrollment · wide site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.