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ClinicalTrials.gov 3 recruiting now early-phase tilt small index

Myotonic Dystrophy 1: early-phase trial registry

3 of 5 indexed Myotonic Dystrophy 1 trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #3,391 of 28,707 conditions by registered trial count.

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5 US clinical trials · 3 currently recruiting · #3,391 of 28,707 conditions by registered trial count

Myotonic Dystrophy 1: 5 US clinical trials tracked, 3 recruiting.

Myotonic Dystrophy 1 is the subject of 5 registered US clinical trials on ClinicalTrials.gov, 3 of them currently open to new participants. 1 are in Phase 3-4 (later-stage) and 2 in Phase 1-2 (earlier-stage). The most active sponsor is Avidity Biosciences, running 2 of these trials.

Enrollment posture brief

Registry condition myotonic-dystrophy-1

OPEN 3 | RECR 60% | LATE 1 | EARLY 2 | RANK #3391 | SPON 2

Volume-matched condition peers

Nearest open-share peer: Acute Kidney Injury (AKI) (60% recruiting · 5 trials)

Ablation80%ACL Reconstruction80%Abuse, Drug60%Acceptability60%Myotonic Dystrophy 1 (this)60%
Open-enrollment share among volume-matched conditions near Myotonic Dystrophy 1

Myotonic Dystrophy 1 lists 3 open slots (60% of 5 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Myotonic Dystrophy 1 on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Myotonic Dystrophy 1 is recruiting above its size-band peers.

    3 of 5 indexed trials (60%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Myotonic Dystrophy 1 research.

    Avidity Biosciences accounts for 2 of 5 trials (40%). 4 distinct sponsors appear on at least one study for this condition label.

  3. Typical Myotonic Dystrophy 1 enrolment sits around 159 participants.

    Median target enrolment is 159 among the 5 trials that report a genuine target (sentinel values excluded). 2 of those (40%) plan for fewer than 100 participants.

  4. Myotonic Dystrophy 1 splits between interventional and observational designs.

    3 interventional and 2 observational studies make up this index (60% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 11Phase 21Phase 31

Phase Distribution

PhaseTrial count
Phase 1 1
Phase 2 1
Phase 3 1

Top Sponsors

Avidity Biosciences 2 trials
ARTHEx Biotech S.L. 1 trials
Myotonic Dystrophy Foundation 1 trials
Virginia Commonwealth University 1 trials

Named interventions

Most-linked intervention names on Myotonic Dystrophy 1 records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Placebo Drug
3 trials
AOC 1001 Drug
1 trials
AOC 1001 (del-desiran) Drug
1 trials
ATX-01 Drug
1 trials
Patient-entered data Other
1 trials

US sites by state

Facility locations filed on Myotonic Dystrophy 1 trials. A trial with sites in several states counts in each.

California 5 trials
Virginia 4 trials
Kansas 4 trials
Florida 4 trials
Ohio 3 trials
New York 3 trials
Colorado 3 trials
Texas 2 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

Related

Read our methodology - how this data is sourced, computed, and verified.

What to do with this Myotonic Dystrophy 1 page

5 registered trials, 3 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 3 Myotonic Dystrophy 1 trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • Avidity Biosciences sponsors the most Myotonic Dystrophy 1 trials on record, review their full trial history before evaluating a specific study. See Avidity Biosciences's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Myotonic Dystrophy 1 condition card totals 5 registered trials; most-linked intervention Placebo; top US site state California. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.