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Limb Girdle Muscular Dystrophy: early-phase trial registry
3 of 7 indexed Limb Girdle Muscular Dystrophy trials are currently recruiting, with more weight in Phase 1-2.
Corpus placement: #2,497 of 28,707 conditions by registered trial count.
7 US clinical trials · 3 currently recruiting · #2,497 of 28,707 conditions by registered trial count
Limb Girdle Muscular Dystrophy: 7 US clinical trials tracked, 3 recruiting.
Limb Girdle Muscular Dystrophy is the subject of 7 registered US clinical trials on ClinicalTrials.gov, 3 of them currently open to new participants. 1 are in Phase 3-4 (later-stage) and 2 in Phase 1-2 (earlier-stage). The most active sponsor is Sarepta Therapeutics, running 3 of these trials.
Enrollment posture brief
Registry condition limb-girdle-muscular-dystrophy
OPEN 3 | RECR 43% | LATE 1 | EARLY 2 | RANK #2497 | SPON 3
Volume-matched condition peers
Nearest open-share peer: Adrenoleukodystrophy (43% recruiting · 7 trials)
Limb Girdle Muscular Dystrophy lists 3 open slots (43% of 7 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Limb Girdle Muscular Dystrophy on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Limb Girdle Muscular Dystrophy is recruiting below its size-band peers.
3 of 7 indexed trials (42.9%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
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One sponsor concentrates Limb Girdle Muscular Dystrophy research.
Sarepta Therapeutics accounts for 3 of 7 trials (42.9%). 5 distinct sponsors appear on at least one study for this condition label.
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Typical Limb Girdle Muscular Dystrophy enrolment sits around 100 participants.
Median target enrolment is 100 among the 7 trials that report a genuine target (sentinel values excluded). 3 of those (42.9%) plan for fewer than 100 participants.
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Limb Girdle Muscular Dystrophy splits between interventional and observational designs.
3 interventional and 4 observational studies make up this index (42.9% interventional). Study type is sponsor-reported on ClinicalTrials.gov.
Open and recent trials
7 total, page 1 of 1
Molecular Analysis of Patients With Neuromuscular Disease
Boston Children's Hospital
NCT00390104
LGMD R1 Natural History Study
Virginia Commonwealth University
NCT05618080
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
AskBio
NCT05230459
A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice
Sarepta Therapeutics
NCT04475926
A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4
Sarepta Therapeutics
NCT06246513
A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)
Sarepta Therapeutics
NCT05876780
Biomarker Development in LGMD2i
ML Bio Solutions
NCT04202627
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 1 | 2 |
| Phase 3 | 1 |
Top Sponsors
Named interventions
Most-linked intervention names on Limb Girdle Muscular Dystrophy records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Limb Girdle Muscular Dystrophy trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Limb Girdle Muscular Dystrophy page
7 registered trials, 3 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 3 Limb Girdle Muscular Dystrophy trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- Sarepta Therapeutics sponsors the most Limb Girdle Muscular Dystrophy trials on record, review their full trial history before evaluating a specific study. See Sarepta Therapeutics's trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Limb Girdle Muscular Dystrophy condition card totals 7 registered trials; most-linked intervention SRP-9003; top US site state Virginia. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.