Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.
Congenital Myotonic Dystrophy: early-phase trial registry
5 of 5 indexed Congenital Myotonic Dystrophy trials are currently recruiting, with more weight in Phase 1-2.
Corpus placement: #3,391 of 28,707 conditions by registered trial count.
5 US clinical trials · 5 currently recruiting · #3,391 of 28,707 conditions by registered trial count
Congenital Myotonic Dystrophy: 5 US clinical trials tracked, 5 recruiting.
Congenital Myotonic Dystrophy is the subject of 5 registered US clinical trials on ClinicalTrials.gov, 5 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 1 in Phase 1-2 (earlier-stage). The most active sponsor is Virginia Commonwealth University, running 2 of these trials.
Enrollment posture brief
Registry condition congenital-myotonic-dystrophy
OPEN 5 | RECR 100% | LATE 0 | EARLY 1 | RANK #3391 | SPON 2
Volume-matched condition peers
Nearest open-share peer: Aortic Arch Aneurysm (100% recruiting · 5 trials)
Congenital Myotonic Dystrophy lists 5 open slots (100% of 5 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Congenital Myotonic Dystrophy on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Congenital Myotonic Dystrophy is recruiting above its size-band peers.
5 of 5 indexed trials (100%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
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One sponsor concentrates Congenital Myotonic Dystrophy research.
Virginia Commonwealth University accounts for 2 of 5 trials (40%). 4 distinct sponsors appear on at least one study for this condition label.
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Typical Congenital Myotonic Dystrophy enrolment sits around 200 participants.
Median target enrolment is 200 among the 5 trials that report a genuine target (sentinel values excluded). 2 of those (40%) plan for fewer than 100 participants.
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Congenital Myotonic Dystrophy research leans observational.
1 interventional and 4 observational studies make up this index (20% interventional). Study type is sponsor-reported on ClinicalTrials.gov.
Open and recent trials
5 total, page 1 of 1
Myotonic Dystrophy Family Registry
Myotonic Dystrophy Foundation
NCT02398786
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
University of Rochester
NCT00082108
Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
Virginia Commonwealth University
NCT06747884
Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
AMO Pharma Limited
NCT05004129
DMCRN-02-001: Assessing Pediatric Endpoints in DM1
Virginia Commonwealth University
NCT05224778
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 2 | 1 |
Top Sponsors
Named interventions
Most-linked intervention names on Congenital Myotonic Dystrophy records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Congenital Myotonic Dystrophy trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Congenital Myotonic Dystrophy page
5 registered trials, 5 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 5 Congenital Myotonic Dystrophy trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- Virginia Commonwealth University sponsors the most Congenital Myotonic Dystrophy trials on record, review their full trial history before evaluating a specific study. See Virginia Commonwealth University's trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Congenital Myotonic Dystrophy condition card totals 5 registered trials; most-linked intervention Patient-entered data; top US site state Virginia. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.