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NCT04603001 · ClinicalTrials.gov registry record · Phase 1

Study of Oral LY3410738 in Patients With Advanced Hematologic Malignancies With IDH1 or IDH2 Mutations

A Phase 1 study of Acute Myeloid Leukemia (AML) and Myelodysplastic Syndrome (MDS), sponsored by Eli Lilly and Company.

Active
Registry status
Phase 1
Development phase
260
Enrollment target
20
Study locations

NCT04603001: Active Phase 1 study of Acute Myeloid Leukemia (AML) and Myelodysplastic Syndrome (MDS), sponsored by Eli Lilly and Company.

NCT04603001 is a Phase 1 study of Acute Myeloid Leukemia (AML) and Myelodysplastic Syndrome (MDS) that is active but no longer recruiting, run by Eli Lilly and Company. The registered enrollment target is 260 participants, above the 136-participant average among 29 other Acute Myeloid Leukemia (AML) trials with a reported enrollment target (91% higher). The trial reports 20 study locations across 14 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT04603001, a Phase 1 study of Acute Myeloid Leukemia (AML) and Myelodysplastic Syndrome (MDS), is active but no longer recruiting, sponsored by Eli Lilly and Company.

ACTIVE NOT RECRUITING
Registry status
Phase 1
Development phase
260 participants
Enrollment target
20
Study locations

Study Summary

This is an open-label, multi-center Phase 1 study of LY3410738, an oral, covalent isocitrate dehydrogenase (IDH) inhibitor, in patients with IDH1 and/or IDH2-mutant advanced hematologic malignancies who may have received standard therapy

Primary Outcome

For Dose Escalation

Interventions

  • DRUG Venetoclax
  • DRUG Azacitidine
  • DRUG LY3410738

Study Locations (20)

California

  • City of Hope National Medical Center - Duarte
  • UCLA Medical Center - Los Angeles
  • University of California, Davis - Health Systems - Sacramento

Illinois

  • Northwestern University - Chicago
  • University of Chicago Hospital - Chicago

New York

  • Roswell Park Cancer Institute - Buffalo
  • Memorial Sloan Kettering Cancer Center - New York

Victoria

  • Peter MacCallum Cancer Centre - Melbourne
  • The Alfred Hospital - Melbourne

Other

  • Cliniques universitaires Saint-Luc - Brussels
  • Helsinki University Hospital - Comprehensive Cancer Center (HYKS - Syöpäkeskus) - Helsinki

Florida

  • H Lee Moffitt Cancer Center - Tampa

Massachusetts

  • Massachusetts General Hospital - Boston

North Carolina

  • University of North Carolina at Chapel Hill - Chapel Hill

Trial Details

FieldValue
Enrollment Target 260 participants
Start Date 2020-11-19
Est. Completion 2026-05
Phase Phase 1
Eli Lilly and Company

1,341 total trials

What the registry record for NCT04603001 still lists

NCT04603001 is an interventional study that assigns participants to a tested intervention. The registered 260 participants enrollment target is mid-sized for trials with a published cap, above the 136-participant average among 29 other Acute Myeloid Leukemia (AML) trials with a reported enrollment target (91% higher).

The record links to 4 conditions, with Acute Myeloid Leukemia (AML) appearing as the primary indexed condition, and to 3 interventions - of which Venetoclax is the first listed.

NCT04603001 names 20 study sites across 14 states, led by California, Illinois, New York.

Frequently Asked Questions

What is clinical trial NCT04603001 about?

NCT04603001 is a clinical study titled "Study of Oral LY3410738 in Patients With Advanced Hematologic Malignancies With IDH1 or IDH2 Mutations". This is an open-label, multi-center Phase 1 study of LY3410738, an oral, covalent isocitrate dehydrogenase (IDH) inhibitor, in patients with IDH1 and/or IDH2-mutant advanced hematologic malignancies who may have received standard therapy

What is the current status of trial NCT04603001?

This trial is currently active not recruiting. It is a Phase 1 study. The enrollment target is 260 participants. The study started on 2020-11-19. Estimated completion is 2026-05.

What conditions does trial NCT04603001 study?

This clinical trial studies the following conditions: Acute Myeloid Leukemia (AML), Myelodysplastic Syndrome (MDS), Chronic Myelomonocytic Leukemia (CMML), Myeloproliferative Neoplasms (MPNs).

What interventions are being tested in trial NCT04603001?

The interventions under investigation include: Venetoclax (DRUG), Azacitidine (DRUG), LY3410738 (DRUG).

Who is sponsoring clinical trial NCT04603001?

This trial is sponsored by Eli Lilly and Company, which has 1,341 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04603001 being conducted?

This trial has 20 study locations across California, Florida, Illinois, Massachusetts, New York. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Acute Myeloid Leukemia (AML)

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT04603001's enrollment target sits among peer trials

260 4th of 29 higher than 26 of 29 other Acute Myeloid Leukemia (AML) trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Acute Myeloid Leukemia (AML) trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT04603001, the US trial registry maintained by the National Library of Medicine. NCT04603001 (mid enrollment · wide site footprint · active not recruiting) retrieved and formatted by PlainTrial, see methodology.