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NCT00065455 · ClinicalTrials.gov registry record · Phase 1

Investigating the Effect of Vitamin A Supplementation on Retinitis Pigmentosa

A Phase 1 study of Retinitis Pigmentosa, sponsored by National Eye Institute (NEI).

Completed
Registry status
Phase 1
Development phase
11
Enrollment target
1
Study location

NCT00065455 is a Phase 1 study of Retinitis Pigmentosa that has completed, run by National Eye Institute (NEI). The registered enrollment target is 11 participants, below the 261-participant average among 37 other Retinitis Pigmentosa trials with a reported enrollment target (96% lower). The trial reports 1 study location across 1 state.

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The verdict

NCT00065455, a Phase 1 study of Retinitis Pigmentosa, has completed, sponsored by National Eye Institute (NEI).

COMPLETED
Registry status
Phase 1
Development phase
11 participants
Enrollment target
1
Study location

Study Summary

Retinitis pigmentosa (RP) is a collective term for a group of inherited retinal dystrophies that are a major cause of irreversible blindness. RP of some type occurs in approximately 1 out of 3500 persons in the United States(1). Gene mutations are responsible for the majority of RP. To date, mutations have been identified in 30 different genes linked to RP(2). The visual prognosis of RP is poor, since the gradual but relentless visual field loss leads eventually to some degree of blindness(3). Although no effective treatment for RP has been identified, participants supplemented with a daily oral dose of 15,000 IU vitamin A palmitate have shown, on average, a slower rate of deterioration of retinal function when the intervention is continued over several years(4). The purpose of this research is to determine whether administration of high oral doses of vitamin A can acutely improve cone photoreceptor function in RP participants as measured by electroretinography (ERG). In this interventional, non-randomized, prospective, pilot study, 5 participants will receive a daily oral dose of 50,000 IU of vitamin A palmitate for 4 weeks, followed by a maintenance dose of 15,000 IU daily for the subsequent 2 weeks. The primary efficacy outcome is a relative percentage change in ERG response amplitude subsequent to vitamin A supplementation. A secondary efficacy outcome is a relative percentage change in implicit time from pre- to post- vitamin A supplementation, with improvement specified as a shorter response implicit time. Other secondary outcomes will be improvements in visual field (Humphery, 10-2; sum of thresholds). Safety outcomes include visual fields, ETDRS visual acuity, intraocular pressure, serum vitamin A level and liver function tests.

Conditions Studied

Interventions

  • DRUG Vitamin A

Study Locations (1)

Maryland

  • National Institutes of Health Clinical Center, 9000 Rockville Pike - Bethesda

Trial Details

FieldValue
Enrollment Target 11 participants
Start Date 2003-07-17
Est. Completion 2009-05-06
Phase Phase 1

Sponsor

National Eye Institute (NEI)

221 total trials

What the Registry Record Tells You About NCT00065455

The ClinicalTrials.gov registry entry for NCT00065455 describes a study currently listed as completed, categorized as Phase 1. The registered enrollment target is 11 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 261-participant average among 37 other Retinitis Pigmentosa trials with a reported enrollment target (96% lower). The listed sponsor is National Eye Institute (NEI), which has 221 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Retinitis Pigmentosa appearing as the primary indexed condition, and to 1 intervention - of which Vitamin A is the first listed.

NCT00065455 reports 1 study location spanning 1 distinct geographic area - top geographies include Maryland.

Frequently Asked Questions

What is clinical trial NCT00065455 about?

NCT00065455 is a clinical study titled "Investigating the Effect of Vitamin A Supplementation on Retinitis Pigmentosa". Retinitis pigmentosa (RP) is a collective term for a group of inherited retinal dystrophies that are a major cause of irreversible blindness. RP of some type occurs in approximately 1 out of 3500 persons in the United States(1). Gene mutations are responsible for the majority of RP. To date, mutatio...

What is the current status of trial NCT00065455?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 11 participants. The study started on 2003-07-17. Estimated completion is 2009-05-06.

What conditions does trial NCT00065455 study?

This clinical trial studies the following conditions: Retinitis Pigmentosa.

What interventions are being tested in trial NCT00065455?

The interventions under investigation include: Vitamin A (DRUG).

Who is sponsoring clinical trial NCT00065455?

This trial is sponsored by National Eye Institute (NEI), which has 221 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT00065455 being conducted?

This trial has 1 study location across Maryland. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

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