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ClinicalTrials.gov 2 recruiting now early-phase tilt small index

Smith-Lemli-Opitz Syndrome: early-phase trial registry

2 of 5 indexed Smith-Lemli-Opitz Syndrome trials are currently recruiting, with more weight in Phase 1-2.

Corpus placement: #3,391 of 28,707 conditions by registered trial count.

5 US clinical trials · 2 currently recruiting · #3,391 of 28,707 conditions by registered trial count

Smith-Lemli-Opitz Syndrome: 5 US clinical trials tracked, 2 recruiting.

Smith-Lemli-Opitz Syndrome is the subject of 5 registered US clinical trials on ClinicalTrials.gov, 2 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 2 in Phase 1-2 (earlier-stage). The most active sponsor is Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD), running 3 of these trials.

Enrollment posture brief

Registry condition smith-lemli-opitz-syndrome

OPEN 2 | RECR 40% | LATE 0 | EARLY 2 | RANK #3391 | SPON 3

Nearest open-share peer: Achondroplasia (40% recruiting · 10 trials)

Ablation80%ACL Reconstruction80%Abuse, Drug60%Acceptability60%Smith-Lemli-Opitz Syndro (th…40%
Open-enrollment share among volume-matched conditions near Smith-Lemli-Opitz Syndrome

Smith-Lemli-Opitz Syndrome lists 2 open slots (40% of 5 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Smith-Lemli-Opitz Syndrome on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Smith-Lemli-Opitz Syndrome is recruiting below its size-band peers.

    2 of 5 indexed trials (40%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Smith-Lemli-Opitz Syndrome research.

    Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) accounts for 3 of 5 trials (60%). 3 distinct sponsors appear on at least one study for this condition label.

  3. Typical Smith-Lemli-Opitz Syndrome enrolment sits around 130 participants.

    Median target enrolment is 130 among the 5 trials that report a genuine target (sentinel values excluded). 1 of those (20%) plan for fewer than 100 participants.

  4. Smith-Lemli-Opitz Syndrome research leans observational.

    2 interventional and 3 observational studies make up this index (40% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 22

Phase Distribution

PhaseTrial count
Phase 2 2

Named interventions

Most-linked intervention names on Smith-Lemli-Opitz Syndrome records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

Cholesterol Drug
2 trials
CRH Drug
1 trials
Cholesterol Suspension Drug
1 trials
OraPlus Drug
1 trials
Simvastatin Susp. Drug
1 trials
Antioxidants Drug
1 trials

US sites by state

Facility locations filed on Smith-Lemli-Opitz Syndrome trials. A trial with sites in several states counts in each.

Maryland 4 trials
Colorado 1 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Smith-Lemli-Opitz Syndrome page

5 registered trials, 2 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Smith-Lemli-Opitz Syndrome condition card totals 5 registered trials; most-linked intervention Cholesterol; top US site state Maryland. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.