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ClinicalTrials.gov enrollment closed early-phase tilt small index

Carnitine Palmitoyltransferase (CPT II) Deficiency: early-phase trial registry

A small indexed set (1 trial) with no open enrollment listed right now.

Corpus placement: #11,370 of 28,707 conditions by registered trial count.

1 US clinical trials · none currently recruiting · #11,370 of 28,707 conditions by registered trial count

Carnitine Palmitoyltransferase (CPT II) Deficiency: 1 US clinical trial tracked, none currently recruiting.

Carnitine Palmitoyltransferase (CPT II) Deficiency is the subject of 1 registered US clinical trials on ClinicalTrials.gov, none currently recruiting. 0 are in Phase 3-4 (later-stage) and 1 in Phase 1-2 (earlier-stage). The most active sponsor is Ultragenyx Pharmaceutical, running 1 of these trials.

Enrollment posture brief

Registry condition carnitine-palmitoyltransferase-cpt-ii-deficiency

OPEN 0 | RECR 0% | LATE 0 | EARLY 1 | RANK #11370 | SPON 1

Nearest open-share peer: Accelerated Phase Chronic Myelogenous Leukemia (0% recruiting · 12 trials)

Ablation80%ACL Reconstruction80%Abuse, Drug60%Acceptability60%Carnitine Palmitoyltrans (th…0%
Open-enrollment share among volume-matched conditions near Carnitine Palmitoyltransferase (CPT II) Deficiency

Carnitine Palmitoyltransferase (CPT II) Deficiency has no open enrollment in this registry pull (1 archived studies). Peers show how other volume-matched labels compare on open share. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Carnitine Palmitoyltransferase (CPT II) Deficiency on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Carnitine Palmitoyltransferase (CPT II) Deficiency is recruiting below its size-band peers.

    0 of 1 indexed trials (0%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

Phase 21

Phase Distribution

PhaseTrial count
Phase 2 1

Top Sponsors

Named interventions

Most-linked intervention names on Carnitine Palmitoyltransferase (CPT II) Deficiency records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

UX007 Drug
1 trials

US sites by state

Facility locations filed on Carnitine Palmitoyltransferase (CPT II) Deficiency trials. A trial with sites in several states counts in each.

Utah 1 trials
Tennessee 1 trials
Pennsylvania 1 trials
Massachusetts 1 trials
Illinois 1 trials
Florida 1 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Carnitine Palmitoyltransferase (CPT II) Deficiency page

1 registered trials, 0 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • No Carnitine Palmitoyltransferase (CPT II) Deficiency trials are currently recruiting in this registry; that can change as new trials post, or check the broader research index. Browse research indexes
  • Ultragenyx Pharmaceutical sponsors the most Carnitine Palmitoyltransferase (CPT II) Deficiency trials on record, review their full trial history before evaluating a specific study. See Ultragenyx Pharmaceutical's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Carnitine Palmitoyltransferase (CPT II) Deficiency condition card totals 1 registered trials; most-linked intervention UX007; top US site state Utah. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.