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NCT07290062 · ClinicalTrials.gov registry record · Phase 1

A Study to Investigate the Safety and Pharmacodynamics of a Single Intrathecal Injection (IT) of INS1202 in Participants With Amyotrophic Lateral Sclerosis (ALS)

A Phase 1 study of Amyotrophic Lateral Sclerosis, sponsored by Insmed Gene Therapy.

Recruiting
Registry status
Phase 1
Development phase
23
Enrollment target
3
Study locations

NCT07290062: Recruiting Phase 1 study of Amyotrophic Lateral Sclerosis, sponsored by Insmed Gene Therapy.

NCT07290062 is a Phase 1 study of Amyotrophic Lateral Sclerosis that is actively recruiting participants, run by Insmed Gene Therapy. The registered enrollment target is 23 participants, below the 898-participant average among 102 other Amyotrophic Lateral Sclerosis trials with a reported enrollment target (97% lower). The trial reports 3 study locations across 3 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT07290062, a Phase 1 study of Amyotrophic Lateral Sclerosis, is actively recruiting participants, sponsored by Insmed Gene Therapy.

RECRUITING
Registry status
Phase 1
Development phase
23 participants
Enrollment target
3
Study locations

Study Summary

The primary objective of this dose-finding study is to evaluate the safety, tolerability and pharmacodynamics of single dose of INS1202 via IT administration in participants ≥ 18 to \<80 years of age with ALS who carry superoxide dismutase type 1 (SOD1) mutations or harbor no known ALS-related genetic mutation.

Interventions

  • GENETIC INS1202

Study Locations (3)

Missouri

  • USA001 - Columbia

Ohio

  • USA007 - Columbus

Pennsylvania

  • USA006 - Philadelphia

Trial Details

FieldValue
Enrollment Target 23 participants
Start Date 2026-01-09
Est. Completion 2030-03-31
Phase Phase 1
Insmed Gene Therapy

2 total trials

What NCT07290062 shows while recruiting

NCT07290062 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 23 participants, a relatively small participant target, below the 898-participant average among 102 other Amyotrophic Lateral Sclerosis trials with a reported enrollment target (97% lower).

The record links to 1 condition, with Amyotrophic Lateral Sclerosis appearing as the primary indexed condition, and to 1 intervention - of which INS1202 is the first listed.

NCT07290062 reports a single indexed study location in Missouri, Ohio, Pennsylvania.

Frequently Asked Questions

What is clinical trial NCT07290062 about?

NCT07290062 is a clinical study titled "A Study to Investigate the Safety and Pharmacodynamics of a Single Intrathecal Injection (IT) of INS1202 in Participants With Amyotrophic Lateral Sclerosis (ALS)". The primary objective of this dose-finding study is to evaluate the safety, tolerability and pharmacodynamics of single dose of INS1202 via IT administration in participants ≥ 18 to \<80 years of age with ALS who carry superoxide dismutase type 1 (SOD1) mutations or harbor no known ALS-related genet...

What is the current status of trial NCT07290062?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 23 participants. The study started on 2026-01-09. Estimated completion is 2030-03-31.

What conditions does trial NCT07290062 study?

This clinical trial studies the following conditions: Amyotrophic Lateral Sclerosis.

What interventions are being tested in trial NCT07290062?

The interventions under investigation include: INS1202 (GENETIC).

Who is sponsoring clinical trial NCT07290062?

This trial is sponsored by Insmed Gene Therapy, which has 2 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT07290062 being conducted?

This trial has 3 study locations across Missouri, Ohio, Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Amyotrophic Lateral Sclerosis

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT07290062's enrollment target sits among peer trials

23 74th of 102 higher than 29 of 102 other Amyotrophic Lateral Sclerosis trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Amyotrophic Lateral Sclerosis trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT07290062, the US trial registry maintained by the National Library of Medicine. NCT07290062 (small enrollment · single site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.