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NCT06607627 · ClinicalTrials.gov registry record · Phase 3

PK, PD, Safety, and Efficacy Study of Gefurulimab in Pediatric Patients With AChR+ Generalized Myasthenia Gravis

A Phase 3 study of Generalized Myasthenia Gravis and gMG, sponsored by Alexion Pharmaceuticals.

Recruiting
Registry status
Phase 3
Development phase
12
Enrollment target
13
Study locations

NCT06607627: Recruiting Phase 3 study of Generalized Myasthenia Gravis and gMG, sponsored by Alexion Pharmaceuticals.

NCT06607627 is a Phase 3 study of Generalized Myasthenia Gravis and gMG that is actively recruiting participants, run by Alexion Pharmaceuticals. The registered enrollment target is 12 participants, below the 131-participant average among 26 other Generalized Myasthenia Gravis trials with a reported enrollment target (91% lower). The trial reports 13 study locations across 3 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT06607627, a Phase 3 study of Generalized Myasthenia Gravis and gMG, is actively recruiting participants, sponsored by Alexion Pharmaceuticals.

RECRUITING
Registry status
Phase 3
Development phase
12 participants
Enrollment target
13
Study locations

Study Summary

The primary objective of this study is to assess the pharmacokinetics and pharmacodynamics of gefurulimab in pediatric participants with AChR+ gMG for the duration of the study.

Interventions

  • COMBINATION_PRODUCT Gefurulimab

Study Locations (13)

Other

  • Research Site - Joinville
  • Research Site - Salvador
  • Research Site - São José do Rio Preto
  • Research Site - São Paulo
  • Research Site - São Paulo
  • Research Site - Saitama-Shi
  • Research Site - Bydgoszcz
  • Research Site - Lodz
  • Research Site - Warsaw
  • Research Site - New Taipei City
  • Research Site - Taipei

District of Columbia

  • Research Site - Washington D.C.

Virginia

  • Research Site - Norfolk

Trial Details

FieldValue
Enrollment Target 12 participants
Start Date 2024-11-13
Est. Completion 2029-01-23
Phase Phase 3
Alexion Pharmaceuticals

162 total trials

What NCT06607627 shows while recruiting

NCT06607627 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 12 participants, a relatively small participant target, below the 131-participant average among 26 other Generalized Myasthenia Gravis trials with a reported enrollment target (91% lower).

The record links to 2 conditions, with Generalized Myasthenia Gravis appearing as the primary indexed condition, and to 1 intervention - of which Gefurulimab is the first listed.

NCT06607627 lists 13 locations in 3 states (Other, District of Columbia, Virginia).

Frequently Asked Questions

What is clinical trial NCT06607627 about?

NCT06607627 is a clinical study titled "PK, PD, Safety, and Efficacy Study of Gefurulimab in Pediatric Patients With AChR+ Generalized Myasthenia Gravis". The primary objective of this study is to assess the pharmacokinetics and pharmacodynamics of gefurulimab in pediatric participants with AChR+ gMG for the duration of the study.

What is the current status of trial NCT06607627?

This trial is currently recruiting. It is a Phase 3 study. The enrollment target is 12 participants. The study started on 2024-11-13. Estimated completion is 2029-01-23.

What conditions does trial NCT06607627 study?

This clinical trial studies the following conditions: Generalized Myasthenia Gravis, gMG.

What interventions are being tested in trial NCT06607627?

The interventions under investigation include: Gefurulimab (COMBINATION_PRODUCT).

Who is sponsoring clinical trial NCT06607627?

This trial is sponsored by Alexion Pharmaceuticals, which has 162 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT06607627 being conducted?

This trial has 13 study locations across District of Columbia, Virginia. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Generalized Myasthenia Gravis

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT06607627's enrollment target sits among peer trials

12 22nd of 26 higher than 1 of 26 other Generalized Myasthenia Gravis trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Generalized Myasthenia Gravis trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT06607627, the US trial registry maintained by the National Library of Medicine. NCT06607627 (small enrollment · multi site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.