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NCT04483778 · ClinicalTrials.gov registry record · Phase 1

B7H3 CAR T Cell Immunotherapy for Recurrent/Refractory Solid Tumors in Children and Young Adults

A Phase 1 study of Osteosarcoma and Rhabdomyosarcoma, sponsored by Seattle Children's Hospital.

Active
Registry status
Phase 1
Development phase
68
Enrollment target
1
Study location

NCT04483778 is a Phase 1 study of Osteosarcoma and Rhabdomyosarcoma that is active but no longer recruiting, run by Seattle Children's Hospital. The registered enrollment target is 68 participants, below the 300-participant average among 46 other Osteosarcoma trials with a reported enrollment target (77% lower). The trial reports 1 study location across 1 state.

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The verdict

NCT04483778, a Phase 1 study of Osteosarcoma and Rhabdomyosarcoma, is active but no longer recruiting, sponsored by Seattle Children's Hospital.

ACTIVE NOT RECRUITING
Registry status
Phase 1
Development phase
68 participants
Enrollment target
1
Study location

Study Summary

This is a phase I, open-label, non-randomized study that will enroll pediatric and young adult research participants with relapsed or refractory non-CNS solid tumors to evaluate the safety, feasibility, and efficacy of administering T cell products derived from the research participant's blood that have been genetically modified to express a B7H3-specific receptor (chimeric antigen receptor, or CAR) that will target and kill solid tumors that express B7H3. On Arm A of the study, research participants will receive B7H3-specific CAR T cells only. On Arm B of the study, research participants will receive CAR T cells directed at B7H3 and CD19, a marker on the surface of B lymphocytes, following the hypothesis that CD19+ B cells serving in their normal role as antigen presenting cells to T cells will promote the expansion and persistence of the CAR T cells. Arm A CAR T cells include the protein EGFRt and Arm B CAR T cells include the protein HER2tG. These proteins can be used to both track and destroy the CAR T cells in case of undue toxicity. The primary objectives of the study will be to determine the feasibility of manufacturing the cell products, the safety of the T cell product infusion, to determine the maximum tolerated dose of the CAR T cells products, to describe the full toxicity profile of each product, and determine the persistence of the modified cell in the participant's body on each arm. Participants will receive a single dose of T cells comprised of two different subtypes of T cells (CD4 and CD8 T cells) felt to benefit one another once administered to the research participants for improved potential therapeutic effect. The secondary objectives of this protocol are to study the number of modified cells in the patients and the duration they continue to be at detectable levels. The investigators will also quantitate anti-tumor efficacy on each arm. Participants who experience significant and potentially life-threatening toxicities (other than clinically man

Interventions

  • DRUG Pembrolizumab
  • BIOLOGICAL second generation 4-1BBζ B7H3-EGFRt-DHFR
  • BIOLOGICAL second generation 4-1BBζ B7H3-EGFRt-DHFR(selected) and a second generation 4-1BBζ CD19-Her2tG

Study Locations (1)

Washington

  • Seattle Children's Hospital - Seattle

Trial Details

FieldValue
Enrollment Target 68 participants
Start Date 2020-07-13
Est. Completion 2040-12
Phase Phase 1

Sponsor

Seattle Children's Hospital

168 total trials

What the Registry Record Tells You About NCT04483778

The ClinicalTrials.gov registry entry for NCT04483778 describes a study currently listed as active not recruiting, categorized as Phase 1. The registered enrollment target is 68 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 300-participant average among 46 other Osteosarcoma trials with a reported enrollment target (77% lower). The listed sponsor is Seattle Children's Hospital, which has 168 total studies on file at ClinicalTrials.gov.

The record links to 10 conditions, with Osteosarcoma appearing as the primary indexed condition, and to 3 interventions - of which Pembrolizumab is the first listed.

NCT04483778 reports 1 study location spanning 1 distinct geographic area - top geographies include Washington.

Frequently Asked Questions

What is clinical trial NCT04483778 about?

NCT04483778 is a clinical study titled "B7H3 CAR T Cell Immunotherapy for Recurrent/Refractory Solid Tumors in Children and Young Adults". This is a phase I, open-label, non-randomized study that will enroll pediatric and young adult research participants with relapsed or refractory non-CNS solid tumors to evaluate the safety, feasibility, and efficacy of administering T cell products derived from the research participant's blood that ...

What is the current status of trial NCT04483778?

This trial is currently active not recruiting. It is a Phase 1 study. The enrollment target is 68 participants. The study started on 2020-07-13. Estimated completion is 2040-12.

What conditions does trial NCT04483778 study?

This clinical trial studies the following conditions: Osteosarcoma, Rhabdomyosarcoma, Carcinoma, Ewing Sarcoma, Germ Cell Tumor.

What interventions are being tested in trial NCT04483778?

The interventions under investigation include: Pembrolizumab (DRUG), second generation 4-1BBζ B7H3-EGFRt-DHFR (BIOLOGICAL), second generation 4-1BBζ B7H3-EGFRt-DHFR(selected) and a second generation 4-1BBζ CD19-Her2tG (BIOLOGICAL).

Who is sponsoring clinical trial NCT04483778?

This trial is sponsored by Seattle Children's Hospital, which has 168 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04483778 being conducted?

This trial has 1 study location across Washington. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.