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NCT04322383 · ClinicalTrials.gov registry record · Phase 2

Binimetinib for People With Relapsed/Refractory BRAF Wild Type Hairy Cell Leukemia and Variant

A Phase 2 study of Hairy Cell Leukemia, sponsored by National Cancer Institute (NCI).

Recruiting
Registry status
Phase 2
Development phase
40
Enrollment target
1
Study location

NCT04322383: Recruiting Phase 2 study of Hairy Cell Leukemia, sponsored by National Cancer Institute (NCI).

NCT04322383 is a Phase 2 study of Hairy Cell Leukemia that is actively recruiting participants, run by National Cancer Institute (NCI). The registered enrollment target is 40 participants, below the 70-participant average among 15 other Hairy Cell Leukemia trials with a reported enrollment target (43% lower). The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT04322383, a Phase 2 study of Hairy Cell Leukemia, is actively recruiting participants, sponsored by National Cancer Institute (NCI).

RECRUITING
Registry status
Phase 2
Development phase
40 participants
Enrollment target
1
Study location

Study Summary

Background: Most people with hairy cell leukemia have a BRAF gene mutation. They can be treated with BRAF inhibitors, drugs that target this mutation. For people who do not have this mutation, BRAF inhibitors are not a treatment option. We found that in hairy cell leukemia, when BRAF is not mutated, the MEK gene frequently is. Binimetinib is a MEK inhibitor which targets MEK. It is important to determine if this drug can be a good treatment option in those who cannot benefit treatment with BRAF inhibitors. Objective: To see if binimetinib is an effective treatment for hairy cell leukemia that does not have a BRAF mutation. Eligibility: People ages 18 and older with hairy cell leukemia without a mutation in the BRAF gene and whose disease either did not respond to treatment or came back after treatment Design: Participants will be screened with: * Medical history * Physical exam * Blood and urine tests * Lung and heart tests * Eye exam * Bone marrow biopsy: A needle will be injected through the participant s skin into the bone to remove a sample of marrow. * CT or MRI scan: Participants will lie in a machine that takes pictures of the body. They might receive a contrast agent by vein. Before they start treatment, participants will have an abdominal ultrasound, pulmonary function tests, and exercise stress tests. Participants will take binimetinib by mouth twice daily in 28-day cycles. They will keep a medication diary. Participants will have at least one visit before every cycle. Visits will include repeats of some screening tests. Participants may continue treatment as long as their disease does not get worse and they do not have bad side effects. About a month after their last dose of treatment, participants will have a follow-up visit. They will then have visits once a year....

Primary Outcome

Percentage of participants with the best overall response of CR or PR to therapy

Conditions Studied

Interventions

  • DRUG binimetinib

Study Locations (1)

Maryland

  • National Institutes of Health Clinical Center - Bethesda

Trial Details

FieldValue
Enrollment Target 40 participants
Start Date 2021-01-07
Est. Completion 2028-07-31
Phase Phase 2
National Cancer Institute (NCI)

3,257 total trials

What NCT04322383 shows while recruiting

NCT04322383 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 40 participants, a relatively small participant target, below the 70-participant average among 15 other Hairy Cell Leukemia trials with a reported enrollment target (43% lower).

The record links to 1 condition, with Hairy Cell Leukemia appearing as the primary indexed condition, and to 1 intervention - of which binimetinib is the first listed.

NCT04322383 reports a single indexed study location in Maryland.

Frequently Asked Questions

What is clinical trial NCT04322383 about?

NCT04322383 is a clinical study titled "Binimetinib for People With Relapsed/Refractory BRAF Wild Type Hairy Cell Leukemia and Variant". Background: Most people with hairy cell leukemia have a BRAF gene mutation. They can be treated with BRAF inhibitors, drugs that target this mutation. For people who do not have this mutation, BRAF inhibitors are not a treatment option. We found that in hairy cell leukemia, when BRAF is not mutated...

What is the current status of trial NCT04322383?

This trial is currently recruiting. It is a Phase 2 study. The enrollment target is 40 participants. The study started on 2021-01-07. Estimated completion is 2028-07-31.

What conditions does trial NCT04322383 study?

This clinical trial studies the following conditions: Hairy Cell Leukemia.

What interventions are being tested in trial NCT04322383?

The interventions under investigation include: binimetinib (DRUG).

Who is sponsoring clinical trial NCT04322383?

This trial is sponsored by National Cancer Institute (NCI), which has 3,257 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04322383 being conducted?

This trial has 1 study location across Maryland. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Hairy Cell Leukemia

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT04322383's enrollment target sits among peer trials

40 11th of 15 higher than 5 of 15 other Hairy Cell Leukemia trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Hairy Cell Leukemia trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT04322383, the US trial registry maintained by the National Library of Medicine. NCT04322383 (small enrollment · single site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.