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NCT03810508 · ClinicalTrials.gov registry record
A Natural History Study of Charcot-Marie-Tooth 4J (CMT4J)
A clinical trial, sponsored by Neurogene.
- Terminated
- Registry status
- 21
- Enrollment target
NCT03810508 is a clinical trial that was terminated before completion, run by Neurogene. The registered enrollment target is 21 participants.
The verdict
NCT03810508 was terminated before completion, sponsored by Neurogene.
- TERMINATED
- Registry status
- 21 participants
- Enrollment target
Study Summary
Charcot-Marie-Tooth 4J (CMT4J) is a rare inherited peripheral neuropathy often characterized by rapidly progressive, asymmetrical upper and lower extremity weakness, muscle atrophy leading to loss of ambulation, respiratory compromise and premature death with no available treatment. The purpose of this study is to investigate the clinical characteristics and natural clinical progression of symptoms in individuals with CMT4J. This natural history study is important to better understand disease course to be able to determine clinically meaningful outcome measures for use in future clinical trials.
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 21 participants |
| Start Date | 2019-07-18 |
| Est. Completion | 2022-02-15 |
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Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT03810508
The ClinicalTrials.gov registry entry for NCT03810508 describes a study currently listed as terminated, categorized as an unspecified phase. The registered enrollment target is 21 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Neurogene, which has 6 total studies on file at ClinicalTrials.gov.
The record links to 0 conditions, and to 0 interventions.
NCT03810508 reports 0 study locations.
Frequently Asked Questions
What is clinical trial NCT03810508 about?
NCT03810508 is a clinical study titled "A Natural History Study of Charcot-Marie-Tooth 4J (CMT4J)". Charcot-Marie-Tooth 4J (CMT4J) is a rare inherited peripheral neuropathy often characterized by rapidly progressive, asymmetrical upper and lower extremity weakness, muscle atrophy leading to loss of ambulation, respiratory compromise and premature death with no available treatment. The purpose of ...
What is the current status of trial NCT03810508?
This trial is currently terminated. The enrollment target is 21 participants. The study started on 2019-07-18. Estimated completion is 2022-02-15.
Who is sponsoring clinical trial NCT03810508?
This trial is sponsored by Neurogene, which has 6 total clinical trials registered on ClinicalTrials.gov.
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