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NCT01417520 · ClinicalTrials.gov registry record

Clinical and Pathophysiological Investigations Into Erdheim Chester Disease

A clinical trial, sponsored by National Human Genome Research Institute (NHGRI).

Completed
Registry status
88
Enrollment target

NCT01417520 is a clinical trial that has completed, run by National Human Genome Research Institute (NHGRI). The registered enrollment target is 88 participants.

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The verdict

NCT01417520 has completed, sponsored by National Human Genome Research Institute (NHGRI).

COMPLETED
Registry status
88 participants
Enrollment target

Study Summary

Background: \- Erdheim Chester Disease (ECD) is a very rare disease in which abnormal white blood cells start growing and affect the bones, kidneys, skin, and brain. ECD can cause severe lung disease, kidney failure, heart disease, and other complications that lead to death. Because ECD is a rare disease, found mostly in men over 40 years of age, there is no standard treatment for it. More information is needed to find out what genes can cause ECD and how best to treat it. Objectives: \- To collect study samples and medical information on people with Erdheim Chester Disease. Eligibility: \- Individuals 2 to 80 year of age who have been diagnosed with Erdheim Chester Disease. Design: * Participants will be screened with a physical exam and medical history. * Participants will have a study visit to provide samples for study, including blood, urine, and skin tissue samples. Participants will also have lung, heart, and muscle function tests; imaging studies of the brain, chest, and whole body; a treadmill running stress test; an eye exam; and other tests as needed by the study doctors. * Participants will be asked to return for a similar set of tests every 2 years, and to remain in contact for possible treatment options.

Trial Details

FieldValue
Enrollment Target 88 participants
Start Date 2011-08-01
Est. Completion 2019-07-24

What the Registry Record Tells You About NCT01417520

The ClinicalTrials.gov registry entry for NCT01417520 describes a study currently listed as completed, categorized as an unspecified phase. The registered enrollment target is 88 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is National Human Genome Research Institute (NHGRI), which has 185 total studies on file at ClinicalTrials.gov.

The record links to 0 conditions, and to 0 interventions.

NCT01417520 reports 0 study locations.

Frequently Asked Questions

What is clinical trial NCT01417520 about?

NCT01417520 is a clinical study titled "Clinical and Pathophysiological Investigations Into Erdheim Chester Disease". Background: \- Erdheim Chester Disease (ECD) is a very rare disease in which abnormal white blood cells start growing and affect the bones, kidneys, skin, and brain. ECD can cause severe lung disease, kidney failure, heart disease, and other complications that lead to death. Because ECD is a rare d...

What is the current status of trial NCT01417520?

This trial is currently completed. The enrollment target is 88 participants. The study started on 2011-08-01. Estimated completion is 2019-07-24.

Who is sponsoring clinical trial NCT01417520?

This trial is sponsored by National Human Genome Research Institute (NHGRI), which has 185 total clinical trials registered on ClinicalTrials.gov.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial

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