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NCT00176904 · ClinicalTrials.gov registry record · Phase 2
Stem Cell Transplant for Inborn Errors of Metabolism
A Phase 2 study of Batten Disease and Adrenoleukodystrophy, sponsored by Masonic Cancer Center, University of Minnesota.
- Completed
- Registry status
- Phase 2
- Development phase
- 135
- Enrollment target
- 1
- Study location
NCT00176904: Completed Phase 2 study of Batten Disease and Adrenoleukodystrophy, sponsored by Masonic Cancer Center, University of Minnesota.
NCT00176904 is a Phase 2 study of Batten Disease and Adrenoleukodystrophy that has completed, run by Masonic Cancer Center, University of Minnesota. The registered enrollment target is 135 participants, below the 2,817-participant average among 11 other Batten Disease trials with a reported enrollment target (95% lower). The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT00176904, a Phase 2 study of Batten Disease and Adrenoleukodystrophy, has completed, sponsored by Masonic Cancer Center, University of Minnesota.
- COMPLETED
- Registry status
- Phase 2
- Development phase
- 135 participants
- Enrollment target
- 1
- Study location
Study Summary
The purpose of this study is to determine the safety and engraftment of donor hematopoietic cells using this conditioning regimen in patients undergoing a hematopoietic (blood forming) cell transplant for an inherited metabolic storage disease.
Primary Outcome
Number of patients alive at designated timepoints after transplant.
Conditions Studied
Interventions
- PROCEDURE Stem Cell Transplant
- DRUG Busulfan, Cyclophosphamide, Antithymocyte Globulin
Study Locations (1)
Minnesota
- Masonic Cancer Center, University of Minnesota - Minneapolis
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 135 participants |
| Start Date | 1995-01 |
| Est. Completion | 2010-06 |
| Phase | Phase 2 |
What the finished NCT00176904 record still lists
NCT00176904 is an interventional study that assigns participants to a tested intervention. The registered 135 participants enrollment target is mid-sized for trials with a published cap, below the 2,817-participant average among 11 other Batten Disease trials with a reported enrollment target (95% lower).
The record links to 10 conditions, with Batten Disease appearing as the primary indexed condition, and to 2 interventions - of which Stem Cell Transplant is the first listed.
NCT00176904 reports a single indexed study location in Minnesota.
Frequently Asked Questions
What is clinical trial NCT00176904 about?
NCT00176904 is a clinical study titled "Stem Cell Transplant for Inborn Errors of Metabolism". The purpose of this study is to determine the safety and engraftment of donor hematopoietic cells using this conditioning regimen in patients undergoing a hematopoietic (blood forming) cell transplant for an inherited metabolic storage disease.
What is the current status of trial NCT00176904?
This trial is currently completed. It is a Phase 2 study. The enrollment target is 135 participants. The study started on 1995-01. Estimated completion is 2010-06.
What conditions does trial NCT00176904 study?
This clinical trial studies the following conditions: Batten Disease, Adrenoleukodystrophy, GM1 Gangliosidosis, Tay-Sachs Disease, Wolman Disease.
What interventions are being tested in trial NCT00176904?
The interventions under investigation include: Stem Cell Transplant (PROCEDURE), Busulfan, Cyclophosphamide, Antithymocyte Globulin (DRUG).
Who is sponsoring clinical trial NCT00176904?
This trial is sponsored by Masonic Cancer Center, University of Minnesota, which has 249 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT00176904 being conducted?
This trial has 1 study location across Minnesota. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
Learn More About Clinical Trials
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Where NCT00176904's enrollment target sits among peer trials
135 5th of 11 higher than 7 of 11 other Batten Disease trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other Batten Disease trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
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