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NCT00001839 · ClinicalTrials.gov registry record · Phase 2

A Randomized Trial of Antithymocyte Globulin Versus Cyclosporine to Treat the Cytopenia of Myelodysplastic Syndrome

A Phase 2 study of Myelodysplastic Syndromes and Hematologic Diseases, sponsored by National Institutes of Health Clinical Center (CC).

Completed
Registry status
Phase 2
Development phase
182
Enrollment target
1
Study location

NCT00001839 is a Phase 2 study of Myelodysplastic Syndromes and Hematologic Diseases that has completed, run by National Institutes of Health Clinical Center (CC). The registered enrollment target is 182 participants, below the 284-participant average among 173 other Myelodysplastic Syndromes trials with a reported enrollment target (36% lower). The trial reports 1 study location across 1 state.

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The verdict

NCT00001839, a Phase 2 study of Myelodysplastic Syndromes and Hematologic Diseases, has completed, sponsored by National Institutes of Health Clinical Center (CC).

COMPLETED
Registry status
Phase 2
Development phase
182 participants
Enrollment target
1
Study location

Study Summary

Approximately 40% of the patients with myelodysplastic syndrome (MDS) die as a consequence of their cytopenia. As in aplastic anemia, the cytopenia of MDS may be partly due to cytotoxic T cell activity. Immunosuppressive therapy may therefore reverse the cytopenia. In a phase II pilot study of anti-thymocyte globin (ATG) to treat myelodysplastic syndrome (MDS); 41% of patients (61% of patients with refractory anemia) have responded in terms of transfusion independence. Recently, Jonasova et al \[32\] reported a 82% substantial hematological response rate in 18 patients with MDS of the refractory anemia (RA) subtype treated with cyclosporine alone. Just over 50% of the patients in this series had MDS of the hypocellular type. Cyclosporine alone if indeed efficacious would be a powerful therapeutic option that could be readily used by hematologists in the community to treat patients with MDS. This efficacy needs to be proven in a larger study which includes patients with the other subtypes of MDS and more patients with the non-hypocellular forms of MDS (which constitute approximately 70% of the cases in the community). As MDS is a heterogeneous group of disorders, a randomized comparison with the other immunomodulating intervention of proven benefit, ATG, is appropriate. In this randomized study patients with MDS will receive either ATG alone or cyclosporine alone.

Interventions

  • DRUG Cyclosporine
  • DRUG Antithymocyte globulin

Study Locations (1)

Maryland

  • Warren G. Magnuson Clinical Center (CC) - Bethesda

Trial Details

FieldValue
Enrollment Target 182 participants
Start Date 1998-12
Est. Completion 2000-05
Phase Phase 2

What the Registry Record Tells You About NCT00001839

The ClinicalTrials.gov registry entry for NCT00001839 describes a study currently listed as completed, categorized as Phase 2. The registered enrollment target is 182 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 284-participant average among 173 other Myelodysplastic Syndromes trials with a reported enrollment target (36% lower). The listed sponsor is National Institutes of Health Clinical Center (CC), which has 338 total studies on file at ClinicalTrials.gov.

The record links to 2 conditions, with Myelodysplastic Syndromes appearing as the primary indexed condition, and to 2 interventions - of which Cyclosporine is the first listed.

NCT00001839 reports 1 study location spanning 1 distinct geographic area - top geographies include Maryland.

Frequently Asked Questions

What is clinical trial NCT00001839 about?

NCT00001839 is a clinical study titled "A Randomized Trial of Antithymocyte Globulin Versus Cyclosporine to Treat the Cytopenia of Myelodysplastic Syndrome". Approximately 40% of the patients with myelodysplastic syndrome (MDS) die as a consequence of their cytopenia. As in aplastic anemia, the cytopenia of MDS may be partly due to cytotoxic T cell activity. Immunosuppressive therapy may therefore reverse the cytopenia. In a phase II pilot study of anti-...

What is the current status of trial NCT00001839?

This trial is currently completed. It is a Phase 2 study. The enrollment target is 182 participants. The study started on 1998-12. Estimated completion is 2000-05.

What conditions does trial NCT00001839 study?

This clinical trial studies the following conditions: Myelodysplastic Syndromes, Hematologic Diseases.

What interventions are being tested in trial NCT00001839?

The interventions under investigation include: Cyclosporine (DRUG), Antithymocyte globulin (DRUG).

Who is sponsoring clinical trial NCT00001839?

This trial is sponsored by National Institutes of Health Clinical Center (CC), which has 338 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT00001839 being conducted?

This trial has 1 study location across Maryland. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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