Rhythm Pharmaceuticals

Open enrollment with an early-phase pipeline tilt

According to ClinicalTrials.gov-derived indexes, Rhythm Pharmaceuticals sits in the top decile of US sponsors by registered trial count (#668 of 15,742 sponsors by registered trial count).

23 total trials 2 currently recruiting 18 completed early-phase tilt top decile by trial count

Rhythm Pharmaceuticals: 23 sponsored US clinical trials, 2 recruiting.

Rhythm Pharmaceuticals sponsors 23 registered US clinical trials on ClinicalTrials.gov, 2 of them currently recruiting, and 18 completed. 8 of these trials are in Phase 3-4 (later-stage) and 13 in Phase 1-2 (earlier-stage). The most-studied condition in this pipeline is Hypothalamic Obesity, with 3 trials.

Top-decile sponsor footprint

Rhythm Pharmaceuticals ranks in the top decile of sponsors by registered trial count (#668 of 15,742 sponsors by registered trial count). Volume at this scale usually reflects a long institutional pipeline, read phase tilt and therapeutic areas below before treating it as current-year activity.

Trial completion reliability score

A 90/100

18 of 18 decided trials (Completed vs. Terminated on ClinicalTrials.gov) reached their planned completion (100.0%), vs. national p10 68.4% / p90 100% among 1,234 sponsors with at least 10 decided trials. Still-open trials (Recruiting, Active-not-recruiting, Not-yet-recruiting) are excluded since they have not reached an outcome yet.

Open and recent trials

23 total, page 1 of 1

RECRUITING Phase 3

A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)

NCT06760546

RECRUITING Phase 1

A Study of RM-718 in Healthy Subjects and Patients With MC4R Pathway Impairment

NCT06239116

ACTIVE NOT RECRUITING Phase 2

A Study of Setmelanotide in Patients With Prader-Willi Syndrome

NCT06772597

ACTIVE NOT RECRUITING Phase 3

A Trial of Setmelanotide in Acquired Hypothalamic Obesity

NCT05774756

ACTIVE NOT RECRUITING Phase 3

EMANATE: A Study of Setmelanotide in Patients With Specific Gene Variants in the MC4R Pathway

NCT05093634

COMPLETED Phase 2

A Study to Assess Efficacy and Safety of LB54640 in Patients With Hypothalamic Obesity

NCT06046443

COMPLETED Phase 3

Setmelanotide in Pediatric Participants With Rare Genetic Diseases of Obesity

NCT04966741

COMPLETED Phase 3

Phase 3 Crossover Trial of Two Formulations of Setmelanotide in Participants With Specific Gene Defects in the MC4R Pathway

NCT05194124

COMPLETED Phase 2

DAYBREAK: A Study of Setmelanotide in Participants With Specific Gene Variants in the Melanocortin-4 Receptor (MC4R) Pathway

NCT04963231

COMPLETED Phase 4

Study of Setmelanotide Effects on QTc (Corrected QT) Interval in Healthy Participants

NCT05046132

COMPLETED Phase 2

Open-Label Study of Setmelanotide in Hypothalamic Obesity

NCT04725240

COMPLETED Phase 1

A Phase 1 Study to Evaluate the Pharmacokinetics of Setmelanotide in Subjects With Varying Degrees of Renal Impairment

NCT04348175

COMPLETED Phase 3

Setmelanotide (RM-493), Melanocortin-4 Receptor (MC4R) Agonist, in Bardet-Biedl Syndrome (BBS) and Alström Syndrome (AS) Participants With Moderate to Severe Obesity

NCT03746522

COMPLETED Phase 2

Long Term Extension Trial of Setmelanotide

NCT03651765

COMPLETED

The TEMPO (Tracing the Effect of the MC4 Pathway in Obesity) Registry

NCT03479437

COMPLETED Phase 2

Setmelanotide in a Single Patient With Partial Lipodystrophy

NCT03262610

COMPLETED Phase 3

Setmelanotide for the Treatment of Early-Onset Pro-Opiomelanocortin (POMC) Deficiency Obesity

NCT02896192

COMPLETED Phase 2

Setmelanotide Phase 2 Treatment Trial in Participants With Rare Genetic Disorders of Obesity

NCT03013543

COMPLETED

Genetic Testing and Phenotypic Characterization of Severely Obese Pediatric and Adult Volunteers

NCT02849977

COMPLETED Phase 2

Phase 2 Trial to Evaluate Safety and Efficacy of Setmelanotide (RM-493) in Obese Participants With Prader-Willi Syndrome

NCT02311673

COMPLETED Phase 1

Phase 1b/2a Study to Evaluate Safety and Efficacy of Setmelanotide in Obese Patients

NCT02041195

COMPLETED Phase 1

Effects of RM-493 on Energy Expenditure in Obese Individuals

NCT01867437

COMPLETED Phase 2

Phase 2 Study to Evaluate Safety and Efficacy of RM-493 in Obese Participants

NCT01749137

What is open in the Rhythm Pharmaceuticals pipeline

2 recruiting of 23 indexed (9% open); 18 completed (78%).

Phase mix: 8 late (III/IV) vs 13 early (I/II) (early-phase heavy).

Top condition: Hypothalamic Obesity (3 trials), 9 others listed.

How open-pipeline share is computed

Recruiting share is recruiting_count divided by trial_count for this sponsor in the public registry export. Status can change between pulls; treat the figure as a research-attention snapshot, not product availability.

Rhythm Pharmaceuticals: open-pipeline peers nationwide

Peers matched on 23 registered trials and 9% open enrollment, not the therapeutic-area sidebar.

Rhythm Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot). 2×2 strategic matrix plotting 9 entities by Total trials (X) and Recruiting share (Y), with a crosshair dividing the plot into four quadrants. Higher volume & more openFocused & more openHigher volume, mostly closedSmaller & mostly closed 22.922.92323.1 0%5%10%15%20%25% Total trials Recruiting share Rhythm PharmaceuticalsAMAG PharmaceuticalsAtriCureCara TherapeuticsCraig L Slingluff, JrIowa State UniversityNew Approaches to Neuroblastoma Therapy ConsortiumSwedish Orphan BiovitrumUniversity of Nevada, Reno
Rhythm Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot).

Rhythm Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together.

Sponsors near 23 trials (± recruiting share)

Sponsors near 9% open enrollment (± trial volume)

What to do with this Rhythm Pharmaceuticals page

23 registered trials is a research-attention snapshot, not an endorsement of Rhythm Pharmaceuticals or any single study.

  • 2 of Rhythm Pharmaceuticals's trials are currently recruiting, check each one's own eligibility criteria before contacting a site. Browse recruiting trials
  • Hypothalamic Obesity is the condition Rhythm Pharmaceuticals studies most, compare against other sponsors active in the same condition before evaluating a specific study. See Hypothalamic Obesity trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Rhythm Pharmaceuticals pipeline card: 23 registered trials from official public datasets.Report a data error.