Ionis Pharmaceuticals

Open enrollment with an early-phase pipeline tilt

According to ClinicalTrials.gov-derived indexes, Ionis Pharmaceuticals sits in the top decile of US sponsors by registered trial count (#286 of 15,742 sponsors by registered trial count).

76 total trials 9 currently recruiting 52 completed early-phase tilt top decile by trial count

Ionis Pharmaceuticals: 76 sponsored US clinical trials, 9 recruiting.

Ionis Pharmaceuticals sponsors 76 registered US clinical trials on ClinicalTrials.gov, 9 of them currently recruiting, and 52 completed. 21 of these trials are in Phase 3-4 (later-stage) and 48 in Phase 1-2 (earlier-stage). The most-studied condition in this pipeline is Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM), with 3 trials.

Top-decile sponsor footprint

Ionis Pharmaceuticals ranks in the top decile of sponsors by registered trial count (#286 of 15,742 sponsors by registered trial count). Volume at this scale usually reflects a long institutional pipeline, read phase tilt and therapeutic areas below before treating it as current-year activity.

Trial completion reliability score

C 76/100

52 of 55 decided trials (Completed vs. Terminated on ClinicalTrials.gov) reached their planned completion (94.5%), vs. national p10 68.4% / p90 100% among 1,234 sponsors with at least 10 decided trials. Still-open trials (Recruiting, Active-not-recruiting, Not-yet-recruiting) are excluded since they have not reached an outcome yet.

Open and recent trials

76 total, page 2 of 2

COMPLETED Phase 2

A Safety, Tolerability, PK, and PD Study of Once Weekly ISIS-FGFR4RX SC in Obese Patients

NCT02476019

COMPLETED Phase 3

The COMPASS Study: A Study of Volanesorsen (Formally ISIS-APOCIIIRx) in Patients With Hypertriglyceridemia

NCT02300233

COMPLETED Phase 3

The APPROACH Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Patients With Familial Chylomicronemia Syndrome

NCT02211209

COMPLETED Phase 1

A Safety andTolerability Study of Multiple Doses of ISIS-DMPKRx in Adults With Myotonic Dystrophy Type 1

NCT02312011

COMPLETED Phase 3

Extension Study Assessing Long Term Safety and Efficacy of IONIS-TTR Rx in Familial Amyloid Polyneuropathy (FAP)

NCT02175004

COMPLETED Phase 2

Safety, Tolerability and Efficacy of ISIS-GCGRRx in Type 2 Diabetes

NCT01885260

COMPLETED Phase 2

Efficacy and Safety of Inotersen in Familial Amyloid Polyneuropathy

NCT01737398

TERMINATED Phase 2

Mechanistic Study of ISIS ISIS-APOCIIIRX in Type 2 Diabetes

NCT01647308

COMPLETED Phase 1

Phase 1/2, Open-label, Dose-escalation Study of IONIS-STAT3Rx, Administered to Patients With Advanced Cancers

NCT01563302

COMPLETED Phase 2

Safety, Tolerability, and Pharmacokinetic Study of ISIS ApoC-III Rx in Hypertriglyceridemia

NCT01529424

COMPLETED Phase 1

Safety and Tolerability Study of ISIS EIF4E Rx in Combination With Carboplatin and Paclitaxel

NCT01234038

COMPLETED Phase 1

Safety and Tolerability Study of ISIS EIF4E Rx in Combination With Docetaxel and Prednisone (CRPC)

NCT01234025

COMPLETED Phase 1

Safety, Tolerability, and Activity Study of ISIS SOD1Rx to Treat Familial Amyotrophic Lateral Sclerosis (ALS) Caused by SOD1 Gene Mutations

NCT01041222

COMPLETED Phase 1

Examination of Dermatologic Effects From Subcutaneous Injections of ISIS 113715

NCT00365781

TERMINATED Phase 2

Effects of ISIS 113715 on Insulin Sensitivity, Glucose, and Lipid Metabolism and Energy Expenditure in Type 2 Diabetics

NCT00330200

COMPLETED Phase 1

Addition of ISIS 14803 to Therapy With Peginterferon and Ribavirin for Chronic Hepatitis C (HCV) Patients Not Responding Adequately to the Two Drugs

NCT00062816

COMPLETED Phase 2

ISIS 2302-CS27, A 6-Week, Placebo-Controlled Clinical Study to Evaluate the Effectiveness of Alicaforsen (ISIS 2302) in Patients With Mild to Moderate Active Ulcerative Colitis.

NCT00063830

COMPLETED Phase 2

ISIS 2302-CS22, A 6-Week, Active-Controlled Clinical Study to Evaluate the Effectiveness of Alicaforsen (ISIS 2302) in Patients With Mild to Moderate Active Ulcerative Colitis

NCT00063414

COMPLETED Phase 2

ISIS 104838, an Inhibitor of Tumor Necrosis Factor, for Active Rheumatoid Arthritis

NCT00048321

COMPLETED Phase 2

ISIS 14803-CS2, Treatment With ISIS 14803, Administered IV in Patients With Chronic Hepatitis C Virus Infections

NCT00035945

COMPLETED Phase 3

Alicaforsen (ISIS 2302) in Patients With Active Crohn's Disease

NCT00048113

COMPLETED Phase 3

Carboplatin and Paclitaxel With or Without ISIS 3521 in Treating Patients With Non-Small Cell Lung Cancer

NCT00017407

COMPLETED Phase 2

The Safety and Effectiveness of ISIS 2922 in Patients With AIDS Who Have Cytomegalovirus (CMV) of the Eyes

NCT00002356

COMPLETED NA

A Study of ISIS 2922 in the Treatment of Advanced Cytomegalovirus Retinitis

NCT00002187

COMPLETED NA

A Comparison of ISIS 2922 Used Immediately or Later in Patients With Cytomegalovirus (CMV) of the Eyes

NCT00002355

COMPLETED Phase 2

A Randomized Comparison of Intravitreal ISIS 2922 Plus Ganciclovir Versus Ganciclovir as Treatment for Patients With Cytomegalovirus Retinitis ( CMVR )

NCT00002156

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What is open in the Ionis Pharmaceuticals pipeline

9 recruiting of 76 indexed (12% open); 52 completed (68%).

Phase mix: 21 late (III/IV) vs 48 early (I/II) (early-phase heavy).

Top condition: Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM) (3 trials), 9 others listed.

How open-pipeline share is computed

Recruiting share is recruiting_count divided by trial_count for this sponsor in the public registry export. Status can change between pulls; treat the figure as a research-attention snapshot, not product availability.

Ionis Pharmaceuticals: open-pipeline peers nationwide

Peers matched on 76 registered trials and 12% open enrollment, not the therapeutic-area sidebar.

Ionis Pharmaceuticals sits at or above the median trial volume and below the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot). 2×2 strategic matrix plotting 9 entities by Total trials (X) and Recruiting share (Y), with a crosshair dividing the plot into four quadrants. Higher volume & more openFocused & more openHigher volume, mostly closedSmaller & mostly closed 0100200300400500600 10%15%20%25%30%35% Total trials Recruiting share Ionis PharmaceuticalsMetroHealth Medical CenterTexas Tech University Health Sciences CenterUniversity of New MexiUniversity of HawaiiUnited States Army Research Institute of Environmental MedicineFred Hutchinson Cancer CenterCochlearErchonia Corporation
Ionis Pharmaceuticals sits at or above the median trial volume and below the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot).

Ionis Pharmaceuticals sits at or above the median trial volume and below the median recruiting share among these 9 nationwide peers -- the two do not always move together.

Sponsors near 76 trials (± recruiting share)

Sponsors near 12% open enrollment (± trial volume)

What to do with this Ionis Pharmaceuticals page

76 registered trials is a research-attention snapshot, not an endorsement of Ionis Pharmaceuticals or any single study.

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Ionis Pharmaceuticals pipeline card: 76 registered trials from official public datasets.Report a data error.