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ClinicalTrials.gov 2 recruiting now full pipeline small index

Hereditary Angioedema: full-pipeline trial registry

2 of 15 indexed Hereditary Angioedema trials are currently recruiting.

Corpus placement: #1,140 of 28,707 conditions by registered trial count.

15 US clinical trials · 2 currently recruiting · #1,140 of 28,707 conditions by registered trial count

Hereditary Angioedema: 15 US clinical trials tracked, 2 recruiting.

Hereditary Angioedema is the subject of 15 registered US clinical trials on ClinicalTrials.gov, 2 of them currently open to new participants. 9 are in Phase 3-4 (later-stage) and 6 in Phase 1-2 (earlier-stage). The most active sponsor is Shire, running 4 of these trials.

Enrollment posture brief

Registry condition hereditary-angioedema

OPEN 2 | RECR 13% | LATE 9 | EARLY 6 | RANK #1140 | SPON 4

Nearest open-share peer: Drug Addiction (13% recruiting · 15 trials)

Advanced Lung Non-Small Cell53.3%AIDS26.7%Hereditary Angioedema (this)13%Adult Acute Myeloid Leukemia0%Adult Glioblastoma0%
Open-enrollment share among volume-matched conditions near Hereditary Angioedema

Hereditary Angioedema lists 2 open slots (13% of 15 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →

Key findings

What ClinicalTrials.gov does not surface for Hereditary Angioedema on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.

  1. Hereditary Angioedema is recruiting below its size-band peers.

    2 of 15 indexed trials (13.3%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.

  2. One sponsor concentrates Hereditary Angioedema research.

    Shire accounts for 4 of 15 trials (26.7%). 8 distinct sponsors appear on at least one study for this condition label.

  3. Most Hereditary Angioedema trials plan to enrol fewer than 100 people.

    Median target enrolment is 60 among the 15 trials that report a genuine target (sentinel values excluded). 12 of those (80%) plan for fewer than 100 participants.

  4. Hereditary Angioedema research is mostly interventional.

    15 interventional and 0 observational studies make up this index (100% interventional). Study type is sponsor-reported on ClinicalTrials.gov.

Phase 12Phase 24Phase 38Phase 41

Open and recent trials

15 total, page 1 of 1

RECRUITING Phase 3 90 participants

STOP-HAE: A Phase 3 Study of ADX-324 in HAE

ADARx Pharmaceuticals

NCT06960213

RECRUITING Phase 4 30 participants

Safety Study in Subjects ≥ 12 Years of Age With Hereditary Angioedema Switching to Garadacimab

CSL Behring

NCT06806657

ACTIVE NOT RECRUITING Phase 3 154 participants

A Study to Assess the Long-Term Safety and Efficacy of Donidalorsen in the Prophylactic Treatment of Hereditary Angioedema (HAE)

Ionis Pharmaceuticals

NCT05392114

ACTIVE NOT RECRUITING Phase 3 145 participants

An Open-label Extension Trial to Evaluate the Long-term Safety of KVD900 (Sebetralstat) for On-Demand Treatment of Angioedema Attacks in Adolescent and Adult Patients With Hereditary Angioedema (HAE)

KalVista Pharmaceuticals

NCT05505916

ACTIVE NOT RECRUITING Phase 3 60 participants

HAELO: A Phase 3 Study to Evaluate NTLA-2002 in Participants With Hereditary Angioedema (HAE)

Intellia Therapeutics

NCT06634420

ACTIVE NOT RECRUITING Phase 2 56 participants

A Long-term Study of STAR-0215 in Participants With Hereditary Angioedema

Astria Therapeutics

NCT06007677

ACTIVE NOT RECRUITING Phase 1 44 participants

A Gene Therapy Study of BMN 331 in Subjects With Hereditary Angioedema

BioMarin Pharmaceutical

NCT05121376

ACTIVE NOT RECRUITING Phase 3 11 participants

PK Subtrial in Adolescent Patients With HAE Type I or II Participating in the KVD900-302 Trial

KalVista Pharmaceuticals

NCT05511922

COMPLETED Phase 3 146 participants

Open-Label C1 Esterase Inhibitor (C1INH-nf) for the Prevention of Acute Hereditary Angioedema (HAE) Attacks

Shire

NCT00462709

COMPLETED Phase 3 91 participants

OASIS-HAE: A Study to Evaluate the Safety and Efficacy of Donidalorsen (ISIS 721744 or IONIS-PKK-LRx) in Participants With Hereditary Angioedema (HAE)

Ionis Pharmaceuticals

NCT05139810

COMPLETED Phase 2 84 participants

A Phase II, Cross-over Clinical Trial Evaluating the Efficacy and Safety of KVD900 (Sebetralstat) in the On-demand Treatment of Angioedema Attacks in Adult Subjects With Hereditary Angioedema Type I or II

KalVista Pharmaceuticals

NCT04208412

COMPLETED Phase 3 83 participants

C1 Esterase Inhibitor (C1INH-nf) for the Treatment of Acute Hereditary Angioedema (HAE) Attacks

Shire

NCT00289211

COMPLETED Phase 1 29 participants

A Study of STAR-0215 in Participants With Hereditary Angioedema

Astria Therapeutics

NCT05695248

COMPLETED Phase 2 26 participants

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Subcutaneous CINRYZE Administration

Shire

NCT01095497

COMPLETED Phase 2 12 participants

A Study to Evaluate the Safety and Pharmacology of Subcutaneous Administration of CINRYZE With Recombinant Human Hyaluronidase

Shire

NCT01426763

Phase Distribution

PhaseTrial count
Phase 1 2
Phase 2 4
Phase 3 8
Phase 4 1

Named interventions

Most-linked intervention names on Hereditary Angioedema records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.

C1 esterase inhibitor [human] (C1INH-nf) Biological
2 trials
STAR-0215 Drug
2 trials
KVD900 600 mg Drug
2 trials
Donidalorsen Drug
2 trials
Placebo Drug
2 trials
CINRYZE Biological
1 trials
CINRYZE with rHuPH20 Biological
1 trials
Placebo (saline) Drug
1 trials

US sites by state

Facility locations filed on Hereditary Angioedema trials. A trial with sites in several states counts in each.

California 14 trials
Arizona 14 trials
Texas 11 trials
Ohio 11 trials
Missouri 10 trials
Maryland 10 trials
Pennsylvania 8 trials
Arkansas 7 trials

Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.

What to do with this Hereditary Angioedema page

15 registered trials, 2 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.

  • 2 Hereditary Angioedema trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
  • Shire sponsors the most Hereditary Angioedema trials on record, review their full trial history before evaluating a specific study. See Shire's trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Hereditary Angioedema condition card totals 15 registered trials; most-linked intervention C1 esterase inhibitor [human] (C1INH-nf); top US site state California. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.