Alexion Pharmaceuticals

Open enrollment with an early-phase pipeline tilt

According to ClinicalTrials.gov-derived indexes, Alexion Pharmaceuticals sits in the top decile of US sponsors by registered trial count (#183 of 15,742 sponsors by registered trial count).

162 total trials 17 currently recruiting 93 completed early-phase tilt top decile by trial count

Alexion Pharmaceuticals: 162 sponsored US clinical trials, 17 recruiting.

Alexion Pharmaceuticals sponsors 162 registered US clinical trials on ClinicalTrials.gov, 17 of them currently recruiting, and 93 completed. 45 of these trials are in Phase 3-4 (later-stage) and 90 in Phase 1-2 (earlier-stage). The most-studied condition in this pipeline is Paroxysmal Nocturnal Hemoglobinuria, with 5 trials.

Top-decile sponsor footprint

Alexion Pharmaceuticals ranks in the top decile of sponsors by registered trial count (#183 of 15,742 sponsors by registered trial count). Volume at this scale usually reflects a long institutional pipeline, read phase tilt and therapeutic areas below before treating it as current-year activity.

Trial completion reliability score

F 19/100

93 of 129 decided trials (Completed vs. Terminated on ClinicalTrials.gov) reached their planned completion (72.1%), vs. national p10 68.4% / p90 100% among 1,234 sponsors with at least 10 decided trials. Still-open trials (Recruiting, Active-not-recruiting, Not-yet-recruiting) are excluded since they have not reached an outcome yet.

Open and recent trials

162 total, page 2 of 4

COMPLETED Phase 1

Study of Radiolabeled ALXN2050 in Healthy Adult Males

NCT04609670

TERMINATED Phase 2

Study of Ravulizumab in Proliferative Lupus Nephritis (LN) or Immunoglobulin A Nephropathy (IgAN)

NCT04564339

COMPLETED Phase 3

Danicopan as Add-on Therapy to a C5 Inhibitor in Paroxysmal Nocturnal Hemoglobinuria (PNH) Participants Who Have Clinically Evident Extravascular Hemolysis (EVH)(ALPHA)

NCT04469465

COMPLETED Phase 1

A Study of the Cardiac Effects of ALXN2050 in Healthy Adults

NCT04660890

COMPLETED Phase 3

Study of Ravulizumab in Pediatric Participants With HSCT-TMA

NCT04557735

COMPLETED Phase 2

Copper Concentration & Histopathologic Changes in Liver Biopsy in Participants With Wilson Disease Treated With ALXN1840

NCT04422431

COMPLETED Phase 1

Study of ALXN1840 on the Metabolism of a CYP2B6 Substrate in Healthy Participants

NCT04526210

COMPLETED Phase 1

Study of the Metabolism of Danicopan in Healthy Adults

NCT04609696

COMPLETED Phase 2

Copper and Molybdenum Balance in Participants With Wilson Disease Treated With ALXN1840

NCT04573309

COMPLETED Phase 1

A Study of the Cardiac Effects of ALXN1840 in Healthy Adults

NCT04560816

COMPLETED Phase 1

Phase 1 Study of ALXN1840 on the Metabolism of a CYP2C9 Substrate in Healthy Participants.

NCT04526197

COMPLETED Phase 1

A Study to Assess ACH-0145228 When Administered as Immediate Release Tablet Versus Powder-In-Capsule in Healthy Adult Participants

NCT04551586

TERMINATED Phase 3

Efficacy and Safety Study of IV Ravulizumab in Patients With COVID-19 Severe Pneumonia

NCT04369469

TERMINATED Phase 3

An Efficacy and Safety Study of Ravulizumab in ALS Participants

NCT04248465

COMPLETED Phase 2

A Study to Evaluate the Safety and Tolerability of CAEL-101 in Patients With AL Amyloidosis

NCT04304144

COMPLETED Phase 1

A Study of the Effects of Food and Age on Danicopan

NCT04551599

TERMINATED Phase 2

A Study of the Safety and Activity of Eculizumab in Pediatric Participants With Relapsing Neuromyelitis Optica Spectrum Disorder

NCT04155424

COMPLETED Phase 1

A Drug Interaction Study of ACH-0145228

NCT04709081

COMPLETED Phase 3

An Efficacy and Safety Study of Ravulizumab in Adult Participants With NMOSD

NCT04201262

COMPLETED

Patient Reported Outcomes in Adults With Pediatric-onset Hypophosphatasia Treated With Strensiq® (Asfotase Alfa)

NCT04195763

COMPLETED Phase 1

A Drug Interaction Study of Danicopan

NCT04709094

COMPLETED Phase 4

Trial of Andexanet Alfa in ICrH Patients Receiving an Oral FXa Inhibitor

NCT03661528

COMPLETED Phase 3

Safety and Efficacy Study of Ravulizumab in Adults With Generalized Myasthenia Gravis

NCT03920293

COMPLETED Phase 3

Ravulizumab Subcutaneous (SC) Versus Ravulizumab Intravenous (IV) in Adults With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Eculizumab

NCT03748823

TERMINATED

US Selumetinib Registry

NCT05683678

COMPLETED Phase 3

A Phase 3 Open-Label Study of Eculizumab in Pediatric Participants With Refractory Generalized Myasthenia Gravis (gMG)

NCT03759366

COMPLETED Phase 1

A Study of the Drug Interactions Between Danicopan and Cyclosporine, Tacrolimus, Antacids, and Omeprazole in Healthy Adults

NCT05109390

COMPLETED Phase 1

A Study of the Cardiac Effects of Danicopan in Healthy Adults

NCT05016206

TERMINATED Phase 1

Study Evaluating Betrixaban in Pediatric Participants

NCT03346083

TERMINATED Phase 2

A Proof of Concept Study for a 12 Month Treatment in Patients With C3G or IC-MPGN Treated With ACH-0144471

NCT03459443

COMPLETED Phase 2

A Proof-of-Concept Study of Danicopan for 6 Months of Treatment in Participants With C3 Glomerulopathy (C3G)

NCT03369236

COMPLETED Phase 2

Study of Danicopan in Participants With Paroxysmal Nocturnal Hemoglobinuria With Inadequate Response to Eculizumab

NCT03472885

COMPLETED Phase 1

Study of Danicopan in Participants With Hepatic Impairment

NCT03555539

COMPLETED Phase 3

A Study of Ravulizumab (ALXN1210) in Children and Adolescents With Paroxysmal Nocturnal Hemoglobinuria

NCT03406507

TERMINATED Phase 3

Efficacy and Safety of ALXN1840 Administered for 48 Weeks Versus Standard of Care in Participants With Wilson Disease

NCT03403205

COMPLETED Phase 1

Study of Danicopan in Participants With Normal Kidney Function and Participants With Kidney Dysfunction

NCT04935294

TERMINATED Phase 1

A Safety Study of SYNT001 in Participants With Warm Autoimmune Hemolytic Anemia (WAIHA)

NCT03075878

COMPLETED Phase 3

Study of Ravulizumab in Children and Adolescents With Atypical Hemolytic Uremic Syndrome (aHUS)

NCT03131219

TERMINATED Phase 1

A Safety and Dose-Finding Study of SYNT001 in Subjects With Pemphigus (Vulgaris or Foliaceus)

NCT03075904

COMPLETED Phase 3

ALXN1210 Versus Eculizumab in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Eculizumab

NCT03056040

COMPLETED Phase 3

Study of ALXN1210 in Complement Inhibitor Treatment-Naïve Adult and Adolescent Participants With Atypical Hemolytic Uremic Syndrome (aHUS)

NCT02949128

COMPLETED Phase 3

ALXN1210 (Ravulizumab) Versus Eculizumab in Complement Inhibitor Treatment-Naïve Adult Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)

NCT02946463

TERMINATED Phase 1

Study of Samalizumab in Patients With Advanced Cancer

NCT02987504

TERMINATED

Screening for Lysosomal Acid Lipase Deficiency

NCT02926872

COMPLETED Phase 2

Pharmacokinetic and Dose Response Study of Asfotase Alfa in Adult Patients With Pediatric-Onset Hypophosphatasia (HPP)

NCT02797821

COMPLETED

The Assessment of Copper Parameters in Wilson Disease Participants on Standard of Care Treatment

NCT02763215

COMPLETED Phase 2

Evaluation of Safety, Efficacy and Pharmacodynamic Effect of Bertilimumab in Patients With Bullous Pemphigoid

NCT02226146

TERMINATED

Evaluation of Potential Predictors of Disease Progression in Participants With Atypical Hemolytic Uremic Syndrome (aHUS) Including Genetics, Biomarkers, and Treatment

NCT02614898

COMPLETED Phase 3

A Study in Participants With Acute Major Bleeding to Evaluate the Ability of Andexanet Alfa to Reverse the Anticoagulation Effect of Direct and Indirect Oral Anticoagulants (Extension Study)

NCT02329327

COMPLETED Phase 1

Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB)

NCT02324049

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What is open in the Alexion Pharmaceuticals pipeline

17 recruiting of 162 indexed (10% open); 93 completed (57%).

Phase mix: 45 late (III/IV) vs 90 early (I/II) (early-phase heavy).

Top condition: Paroxysmal Nocturnal Hemoglobinuria (5 trials), 9 others listed.

How open-pipeline share is computed

Recruiting share is recruiting_count divided by trial_count for this sponsor in the public registry export. Status can change between pulls; treat the figure as a research-attention snapshot, not product availability.

Alexion Pharmaceuticals: open-pipeline peers nationwide

Peers matched on 162 registered trials and 10% open enrollment, not the therapeutic-area sidebar.

Alexion Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot). 2×2 strategic matrix plotting 9 entities by Total trials (X) and Recruiting share (Y), with a crosshair dividing the plot into four quadrants. Higher volume & more openFocused & more openHigher volume, mostly closedSmaller & mostly closed 050100150200 4%6%8%10%12%14% Total trials Recruiting share Alexion PharmaceuticalsUniversity of VermontTemple UniversityTufts UniversityWayne State UniversityVertex Pharmaceuticals IncorporatedBastyr UniversityCorewell Health WestEthicon
Alexion Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together. Source: ClinicalTrials.gov (2026-08-08 snapshot).

Alexion Pharmaceuticals sits at or above the median trial volume and at or above the median recruiting share among these 9 nationwide peers -- the two do not always move together.

Sponsors near 162 trials (± recruiting share)

Sponsors near 10% open enrollment (± trial volume)

What to do with this Alexion Pharmaceuticals page

162 registered trials is a research-attention snapshot, not an endorsement of Alexion Pharmaceuticals or any single study.

  • 17 of Alexion Pharmaceuticals's trials are currently recruiting, check each one's own eligibility criteria before contacting a site. Browse recruiting trials
  • Paroxysmal Nocturnal Hemoglobinuria is the condition Alexion Pharmaceuticals studies most, compare against other sponsors active in the same condition before evaluating a specific study. See Paroxysmal Nocturnal Hemoglobinuria trials
  • Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide

Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.

Alexion Pharmaceuticals pipeline card: 162 registered trials from official public datasets.Report a data error.