Medical Information Only. Consult your healthcare provider before considering clinical trial enrollment.
Congenital Bone Marrow Failure Syndromes: early-phase trial registry
2 of 2 indexed Congenital Bone Marrow Failure Syndromes trials are currently recruiting, with more weight in Phase 1-2.
Corpus placement: #7,188 of 28,707 conditions by registered trial count.
2 US clinical trials · 2 currently recruiting · #7,188 of 28,707 conditions by registered trial count
Congenital Bone Marrow Failure Syndromes: 2 US clinical trials tracked, 2 recruiting.
Congenital Bone Marrow Failure Syndromes is the subject of 2 registered US clinical trials on ClinicalTrials.gov, 2 of them currently open to new participants. 0 are in Phase 3-4 (later-stage) and 1 in Phase 1-2 (earlier-stage). The most active sponsor is Paul Szabolcs, running 2 of these trials.
Enrollment posture brief
Registry condition congenital-bone-marrow-failure-syndromes
OPEN 2 | RECR 100% | LATE 0 | EARLY 1 | RANK #7188 | SPON 2
Volume-matched condition peers
Nearest open-share peer: Aortic Arch Aneurysm (100% recruiting · 5 trials)
Congenital Bone Marrow Failure Syndromes lists 2 open slots (100% of 2 indexed trials). Peers are matched on registered volume, not therapeutic-area browse lists. How peer matching works →
Key findings
What ClinicalTrials.gov does not surface for Congenital Bone Marrow Failure Syndromes on its own pages , computed from the registry mirror as of 2026-08-08. Each line carries its own denominator so it can be quoted as it stands.
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Congenital Bone Marrow Failure Syndromes is recruiting above its size-band peers.
2 of 2 indexed trials (100%) are open to enrollment, against a 46.5% average across 27,806 conditions with fewer than 20 trials. The peer set uses the same ClinicalTrials.gov-derived counts as this page.
Open and recent trials
2 total, page 1 of 1
Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
Paul Szabolcs
NCT01962415
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Paul Szabolcs
NCT04528355
Phase Distribution
| Phase | Trial count |
|---|---|
| Phase 2 | 1 |
Top Sponsors
Named interventions
Most-linked intervention names on Congenital Bone Marrow Failure Syndromes records (sponsor-reported on ClinicalTrials.gov). Counts are trial links, not unique products.
US sites by state
Facility locations filed on Congenital Bone Marrow Failure Syndromes trials. A trial with sites in several states counts in each.
Source: ClinicalTrials.gov, National Library of Medicine. Data is informational only.
Related
What to do with this Congenital Bone Marrow Failure Syndromes page
2 registered trials, 2 currently recruiting, is a starting point for a conversation, not a diagnosis or a recommendation.
- 2 Congenital Bone Marrow Failure Syndromes trials are currently recruiting, check eligibility criteria before contacting a site. Browse recruiting trials
- Paul Szabolcs sponsors the most Congenital Bone Marrow Failure Syndromes trials on record, review their full trial history before evaluating a specific study. See Paul Szabolcs's trials
- Bring the specific trial ID (NCT number) to your own doctor before enrolling, this page is a directory, not medical guidance. Read the trial-finding guide
Trial and recruiting counts reflect ClinicalTrials.gov registry status as of the data vintage above; individual trial eligibility and enrollment status can change.
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This Congenital Bone Marrow Failure Syndromes condition card totals 2 registered trials; most-linked intervention data collection; top US site state Pennsylvania. See our editorial standards & corrections policy, the methodology behind these numbers, the data changelog, or report a data error.