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NCT04528355 · ClinicalTrials.gov registry record
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
A clinical trial of Primary Immunodeficiency (PID) and Congenital Bone Marrow Failure Syndromes, sponsored by Paul Szabolcs.
- Recruiting
- Registry status
- 50
- Enrollment target
- 1
- Study location
NCT04528355: Recruiting study of Primary Immunodeficiency (PID) and Congenital Bone Marrow Failure Syndromes, sponsored by Paul Szabolcs.
NCT04528355 is a study of Primary Immunodeficiency (PID) and Congenital Bone Marrow Failure Syndromes that is actively recruiting participants, run by Paul Szabolcs. The registered enrollment target is 50 participants. The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04528355, a study of Primary Immunodeficiency (PID) and Congenital Bone Marrow Failure Syndromes, is actively recruiting participants, sponsored by Paul Szabolcs.
- RECRUITING
- Registry status
- 50 participants
- Enrollment target
- 1
- Study location
Study Summary
This is a data collection study that will examine the general diagnostic and treatment data associated with the reduced-intensity chemotherapy-based regimen paired with simple alemtuzumab dosing strata designed to prevented graft failure and to aid in immune reconstitution following hematopoietic stem cell transplantation.
Primary Outcome
grades 3-4, chronic extensive GVHD
Conditions Studied
Interventions
- DRUG data collection
Study Locations (1)
Pennsylvania
- UPMC Children's Hospital of Pittsburgh - Pittsburgh
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 50 participants |
| Start Date | 2020-08-20 |
| Est. Completion | 2028-06-30 |
What NCT04528355 shows while recruiting
NCT04528355 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 50 participants, a relatively small participant target.
The record links to 5 conditions, with Primary Immunodeficiency (PID) appearing as the primary indexed condition, and to 1 intervention - of which data collection is the first listed.
NCT04528355 reports a single indexed study location in Pennsylvania.
Frequently Asked Questions
What is clinical trial NCT04528355 about?
NCT04528355 is a clinical study titled "Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC". This is a data collection study that will examine the general diagnostic and treatment data associated with the reduced-intensity chemotherapy-based regimen paired with simple alemtuzumab dosing strata designed to prevented graft failure and to aid in immune reconstitution following hematopoietic st...
What is the current status of trial NCT04528355?
This trial is currently recruiting. The enrollment target is 50 participants. The study started on 2020-08-20. Estimated completion is 2028-06-30.
What conditions does trial NCT04528355 study?
This clinical trial studies the following conditions: Primary Immunodeficiency (PID), Congenital Bone Marrow Failure Syndromes, Inherited Metabolic Disorders (IMD), Hereditary Anemias, Inflammatory Conditions.
What interventions are being tested in trial NCT04528355?
The interventions under investigation include: data collection (DRUG).
Who is sponsoring clinical trial NCT04528355?
This trial is sponsored by Paul Szabolcs, which has 7 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT04528355 being conducted?
This trial has 1 study location across Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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